163 related articles for article (PubMed ID: 32313251)
1. Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook.
Hechtelt Jonker A; Hivert V; Gabaldo M; Batista L; O'Connor D; Aartsma-Rus A; Day S; Sakushima K; Ardigo D
Nat Rev Drug Discov; 2020 Aug; 19(8):495-496. PubMed ID: 32313251
[No Abstract] [Full Text] [Related]
2. A Global Approach to Rare Diseases Research and Orphan Products Development: The International Rare Diseases Research Consortium (IRDiRC).
Cutillo CM; Austin CP; Groft SC
Adv Exp Med Biol; 2017; 1031():349-369. PubMed ID: 29214582
[TBL] [Abstract][Full Text] [Related]
3. The Food and Drug Administration's Office of Orphan Products Development: incentives, grants, and special designations speed therapies for orphan diseases.
Haffner ME
Retina; 2005 Dec; 25(8 Suppl):S89-S90. PubMed ID: 16374359
[No Abstract] [Full Text] [Related]
4. An Orphan Drug Framework (ODF) for Canada.
Lee DK; Wong B
J Popul Ther Clin Pharmacol; 2014; 21(1):e42-6. PubMed ID: 24671833
[TBL] [Abstract][Full Text] [Related]
5. Translation of rare disease research into orphan drug development: disease matters.
Heemstra HE; van Weely S; Büller HA; Leufkens HG; de Vrueh RL
Drug Discov Today; 2009 Dec; 14(23-24):1166-73. PubMed ID: 19818412
[TBL] [Abstract][Full Text] [Related]
6. Ethical dilemmas about orphan drugs for orphan diseases.
Gunasekera H
J Paediatr Child Health; 2014 Aug; 50(8):656. PubMed ID: 25080986
[No Abstract] [Full Text] [Related]
7. Ethical dilemmas about orphan drugs for orphan diseases.
Isaacs D
J Paediatr Child Health; 2014 Apr; 50(4):249-50. PubMed ID: 24698059
[No Abstract] [Full Text] [Related]
8. Orphan Drugs in Oncology.
Korchagina D; Jaroslawski S; Jadot G; Toumi M
Recent Results Cancer Res; 2019; 213():109-142. PubMed ID: 30543010
[TBL] [Abstract][Full Text] [Related]
9. IRDiRC Drug Repurposing Guidebook: making better use of existing drugs to tackle rare diseases.
Hechtelt Jonker A; Day S; Gabaldo M; Stone H; de Kort M; O'Connor DJ; Pasmooij AMG
Nat Rev Drug Discov; 2023 Dec; 22(12):937-938. PubMed ID: 37872324
[No Abstract] [Full Text] [Related]
10. Orphan drugs and orphan tests in the USA.
Thoene JG
Community Genet; 2004; 7(4):169-72. PubMed ID: 15692190
[No Abstract] [Full Text] [Related]
11. Awareness of orphan therapies offer opportunities for pharmacists.
Traynor K
Am J Health Syst Pharm; 2013 Sep; 70(18):1564, 1566. PubMed ID: 23988596
[No Abstract] [Full Text] [Related]
12. [Orphan drugs. Drugs for treatment of rare diseases].
Hennemann A
Med Monatsschr Pharm; 2004 Aug; 27(8):256-9. PubMed ID: 15382448
[No Abstract] [Full Text] [Related]
13. Orphan drug development in China: progress and challenges.
Zhang S; Chen L; Zhang Z; Zhao Y
Lancet; 2019 Sep; 394(10204):1127-1128. PubMed ID: 31571591
[No Abstract] [Full Text] [Related]
14. When everyone is an orphan: against adopting a U.S.-styled orphan drug policy in Canada.
Herder M
Account Res; 2013; 20(4):227-69. PubMed ID: 23805831
[TBL] [Abstract][Full Text] [Related]
15. [Orphan diseases, rare diseases, time to get mobilised].
Cordier JF
Rev Prat; 2006 Jan; 56(2):123-4. PubMed ID: 16584035
[No Abstract] [Full Text] [Related]
16. Is it time to revisit orphan drug policies?
McCabe C; Stafinski T; Menon D
BMJ; 2010 Sep; 341():c4777. PubMed ID: 20861098
[No Abstract] [Full Text] [Related]
17. Orphan products: hope for people with rare diseases.
Rados C
FDA Consum; 2003; 37(6):10-5. PubMed ID: 14986582
[No Abstract] [Full Text] [Related]
18. A personal perspective of orphan drug development for rare diseases: A golden opportunity or an unsustainable future?
Oo C; Rusch LM
J Clin Pharmacol; 2016 Mar; 56(3):257-9. PubMed ID: 26211513
[No Abstract] [Full Text] [Related]
19. Novel Treatments for Rare Cancers: The U.S. Orphan Drug Act Is Delivering-A Cross-Sectional Analysis.
Stockklausner C; Lampert A; Hoffmann GF; Ries M
Oncologist; 2016 Apr; 21(4):487-93. PubMed ID: 27022038
[TBL] [Abstract][Full Text] [Related]
20. Orphan Drug Act passes quarter-century milestone in fight against rare diseases.
Lavine G
Am J Health Syst Pharm; 2008 Jul; 65(13):1205, 1210. PubMed ID: 18574005
[No Abstract] [Full Text] [Related]
[Next] [New Search]
