These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

189 related articles for article (PubMed ID: 32767930)

  • 1. Gene Therapy for Hemophilia A: Where We Stand.
    Zhou M; Hu Z; Zhang C; Wu L; Li Z; Liang D
    Curr Gene Ther; 2020; 20(2):142-151. PubMed ID: 32767930
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Hemophilia Gene Therapy: Ready for Prime Time?
    VandenDriessche T; Chuah MK
    Hum Gene Ther; 2017 Nov; 28(11):1013-1023. PubMed ID: 28793786
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Hemophilia A ameliorated in mice by CRISPR-based in vivo genome editing of human Factor VIII.
    Chen H; Shi M; Gilam A; Zheng Q; Zhang Y; Afrikanova I; Li J; Gluzman Z; Jiang R; Kong LJ; Chen-Tsai RY
    Sci Rep; 2019 Nov; 9(1):16838. PubMed ID: 31727959
    [TBL] [Abstract][Full Text] [Related]  

  • 4. The Immune Response to the fVIII Gene Therapy in Preclinical Models.
    Patel SR; Lundgren TS; Spencer HT; Doering CB
    Front Immunol; 2020; 11():494. PubMed ID: 32351497
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Bioengineering hemophilia A-specific microvascular grafts for delivery of full-length factor VIII into the bloodstream.
    Neumeyer J; Lin RZ; Wang K; Hong X; Hua T; Croteau SE; Neufeld EJ; Melero-Martin JM
    Blood Adv; 2019 Dec; 3(24):4166-4176. PubMed ID: 31851760
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Development of improved factor VIII molecules and new gene transfer approaches for hemophilia A.
    Saenko EL; Ananyeva NM; Moayeri M; Ramezani A; Hawley RG
    Curr Gene Ther; 2003 Feb; 3(1):27-41. PubMed ID: 12553533
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Transduction of modified factor VIII gene improves lentiviral gene therapy efficacy for hemophilia A.
    Gong J; Chung TH; Zheng J; Zheng H; Chang LJ
    J Biol Chem; 2021 Dec; 297(6):101397. PubMed ID: 34774524
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Identification of the Efficient Enhancer Elements in FVIII-Padua for Gene Therapy Study of Hemophilia A.
    Xiao R; Chen Y; Hu Z; Tang Q; Wang P; Zhou M; Wu L; Liang D
    Int J Mol Sci; 2024 Mar; 25(7):. PubMed ID: 38612447
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Gene therapy strategies for hemophilia: benefits versus risks.
    Petrus I; Chuah M; VandenDriessche T
    J Gene Med; 2010 Oct; 12(10):797-809. PubMed ID: 20848668
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Exploring the Potential Feasibility of Intra-Articular Adeno-Associated Virus-Mediated Gene Therapy for Hemophilia Arthropathy.
    Zhang F; Yan X; Li M; Hua B; Xiao X; Monahan PE; Sun J
    Hum Gene Ther; 2020 Apr; 31(7-8):448-458. PubMed ID: 32079420
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Delivery of full-length factor VIII using a piggyBac transposon vector to correct a mouse model of hemophilia A.
    Matsui H; Fujimoto N; Sasakawa N; Ohinata Y; Shima M; Yamanaka S; Sugimoto M; Hotta A
    PLoS One; 2014; 9(8):e104957. PubMed ID: 25126862
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors.
    Chuah MK; Schiedner G; Thorrez L; Brown B; Johnston M; Gillijns V; Hertel S; Van Rooijen N; Lillicrap D; Collen D; VandenDriessche T; Kochanek S
    Blood; 2003 Mar; 101(5):1734-43. PubMed ID: 12406898
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Circumventing furin enhances factor VIII biological activity and ameliorates bleeding phenotypes in hemophilia models.
    Siner JI; Samelson-Jones BJ; Crudele JM; French RA; Lee BJ; Zhou S; Merricks E; Raymer R; Nichols TC; Camire RM; Arruda VR
    JCI Insight; 2016 Oct; 1(16):e89371. PubMed ID: 27734034
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Recent progress in gene therapy for hemophilia.
    Chuah MK; Nair N; VandenDriessche T
    Hum Gene Ther; 2012 Jun; 23(6):557-65. PubMed ID: 22671033
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Intraosseous delivery of lentiviral vectors targeting factor VIII expression in platelets corrects murine hemophilia A.
    Wang X; Shin SC; Chiang AF; Khan I; Pan D; Rawlings DJ; Miao CH
    Mol Ther; 2015 Apr; 23(4):617-26. PubMed ID: 25655313
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Long-term correction of hemophilia A mice following lentiviral mediated delivery of an optimized canine factor VIII gene.
    Staber JM; Pollpeter MJ; Anderson CG; Burrascano M; Cooney AL; Sinn PL; Rutkowski DT; Raschke WC; McCray PB
    Gene Ther; 2017 Nov; 24(11):742-748. PubMed ID: 28905885
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Translational Potential of Immune Tolerance Induction by AAV Liver-Directed Factor VIII Gene Therapy for Hemophilia A.
    Samelson-Jones BJ; Arruda VR
    Front Immunol; 2020; 11():618. PubMed ID: 32425925
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Advances in gene therapy for hemophilia: basis, current status, and future perspectives.
    Ohmori T
    Int J Hematol; 2020 Jan; 111(1):31-41. PubMed ID: 30083852
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Targeting of the human F8 at the multicopy rDNA locus in Hemophilia A patient-derived iPSCs using TALENickases.
    Pang J; Wu Y; Li Z; Hu Z; Wang X; Hu X; Wang X; Liu X; Zhou M; Liu B; Wang Y; Feng M; Liang D
    Biochem Biophys Res Commun; 2016 Mar; 472(1):144-9. PubMed ID: 26921444
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Gene Delivery of Activated Factor VII Using Alternative Adeno-Associated Virus Serotype Improves Hemostasis in Hemophiliac Mice with FVIII Inhibitors and Adeno-Associated Virus Neutralizing Antibodies.
    Sun J; Hua B; Chen X; Samulski RJ; Li C
    Hum Gene Ther; 2017 Aug; 28(8):654-666. PubMed ID: 28478688
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 10.