240 related articles for article (PubMed ID: 32897878)
41. Expression analysis data of BCL11A and γ-globin genes in KU812 and KG-1 cell lines after CRISPR/Cas9-mediated BCL11A enhancer deletion.
Khosravi MA; Abbasalipour M; Concordet JP; Berg JV; Zeinali S; Arashkia A; Buch T; Karimipoor M
Data Brief; 2020 Feb; 28():104974. PubMed ID: 31890812
[TBL] [Abstract][Full Text] [Related]
42. Base editing of the HBG promoter induces potent fetal hemoglobin expression with no detectable off-target mutations in human HSCs.
Han W; Qiu HY; Sun S; Fu ZC; Wang GQ; Qian X; Wang L; Zhai X; Wei J; Wang Y; Guo YL; Cao GH; Ji RJ; Zhang YZ; Ma H; Wang H; Zhao M; Wu J; Bi L; Chen QB; Li Z; Yu L; Mou X; Yin H; Yang L; Chen J; Yang B; Zhang Y
Cell Stem Cell; 2023 Dec; 30(12):1624-1639.e8. PubMed ID: 37989316
[TBL] [Abstract][Full Text] [Related]
43. Impact of CRISPR/HDR editing versus lentiviral transduction on long-term engraftment and clonal dynamics of HSPCs in rhesus macaques.
Lee BC; Gin A; Wu C; Singh K; Grice M; Mortlock R; Abraham D; Fan X; Zhou Y; AlJanahi A; Choi U; DeRavin SS; Shin T; Hong S; Dunbar CE
Cell Stem Cell; 2024 Apr; 31(4):455-466.e4. PubMed ID: 38508195
[TBL] [Abstract][Full Text] [Related]
44. Strict in vivo specificity of the
Smith EC; Luc S; Croney DM; Woodworth MB; Greig LC; Fujiwara Y; Nguyen M; Sher F; Macklis JD; Bauer DE; Orkin SH
Blood; 2016 Nov; 128(19):2338-2342. PubMed ID: 27707736
[TBL] [Abstract][Full Text] [Related]
45. Efficient long-term multilineage engraftment of CD33-edited hematopoietic stem/progenitor cells in nonhuman primates.
Petty NE; Radtke S; Fields E; Humbert O; Llewellyn MJ; Laszlo GS; Zhu H; Jerome KR; Walter RB; Kiem HP
Mol Ther Methods Clin Dev; 2023 Dec; 31():101121. PubMed ID: 37868209
[TBL] [Abstract][Full Text] [Related]
46. Improved retroviral gene transfer into murine and Rhesus peripheral blood or bone marrow repopulating cells primed in vivo with stem cell factor and granulocyte colony-stimulating factor.
Dunbar CE; Seidel NE; Doren S; Sellers S; Cline AP; Metzger ME; Agricola BA; Donahue RE; Bodine DM
Proc Natl Acad Sci U S A; 1996 Oct; 93(21):11871-6. PubMed ID: 8876230
[TBL] [Abstract][Full Text] [Related]
47. Endothelial Cells Promote Expansion of Long-Term Engrafting Marrow Hematopoietic Stem and Progenitor Cells in Primates.
Gori JL; Butler JM; Kunar B; Poulos MG; Ginsberg M; Nolan DJ; Norgaard ZK; Adair JE; Rafii S; Kiem HP
Stem Cells Transl Med; 2017 Mar; 6(3):864-876. PubMed ID: 28297579
[TBL] [Abstract][Full Text] [Related]
48. Metabolic sensor O-GlcNAcylation regulates erythroid differentiation and globin production via BCL11A.
Luanpitpong S; Kang X; Janan M; Thumanu K; Li J; Kheolamai P; Issaragrisil S
Stem Cell Res Ther; 2022 Jun; 13(1):274. PubMed ID: 35739577
[TBL] [Abstract][Full Text] [Related]
49. Human fetal hemoglobin expression is regulated by the developmental stage-specific repressor BCL11A.
Sankaran VG; Menne TF; Xu J; Akie TE; Lettre G; Van Handel B; Mikkola HK; Hirschhorn JN; Cantor AB; Orkin SH
Science; 2008 Dec; 322(5909):1839-42. PubMed ID: 19056937
[TBL] [Abstract][Full Text] [Related]
50. Hemoglobin genetics: recent contributions of GWAS and gene editing.
Smith EC; Orkin SH
Hum Mol Genet; 2016 Oct; 25(R2):R99-R105. PubMed ID: 27340226
[TBL] [Abstract][Full Text] [Related]
51. Metformin induces FOXO3-dependent fetal hemoglobin production in human primary erythroid cells.
Zhang Y; Paikari A; Sumazin P; Ginter Summarell CC; Crosby JR; Boerwinkle E; Weiss MJ; Sheehan VA
Blood; 2018 Jul; 132(3):321-333. PubMed ID: 29884740
[TBL] [Abstract][Full Text] [Related]
52. Highly Efficient Gene Disruption of Murine and Human Hematopoietic Progenitor Cells by CRISPR/Cas9.
Brunetti L; Gundry MC; Kitano A; Nakada D; Goodell MA
J Vis Exp; 2018 Apr; (134):. PubMed ID: 29708546
[TBL] [Abstract][Full Text] [Related]
53. Lentiviral Transfer of γ-Globin with Fusion Gene NUP98-HOXA10HD Expands Hematopoietic Stem Cells and Ameliorates Murine β-Thalassemia.
Zhao HF; Abraham A; Kim YS; Wang YD; Pestina T; Zhan J; Humphries K; Nienhuis AW; Persons DA
Mol Ther; 2017 Mar; 25(3):593-605. PubMed ID: 28190779
[TBL] [Abstract][Full Text] [Related]
54. CRISPR-Cas9 interrogation of a putative fetal globin repressor in human erythroid cells.
Chung JE; Magis W; Vu J; Heo SJ; Wartiovaara K; Walters MC; Kurita R; Nakamura Y; Boffelli D; Martin DIK; Corn JE; DeWitt MA
PLoS One; 2019; 14(1):e0208237. PubMed ID: 30645582
[TBL] [Abstract][Full Text] [Related]
55. CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications.
Venkatesan V; Christopher AC; Karuppusamy KV; Babu P; Alagiri MKK; Thangavel S
J Vis Exp; 2022 Aug; (186):. PubMed ID: 36036597
[TBL] [Abstract][Full Text] [Related]
56. Robust erythroid differentiation system for rhesus hematopoietic progenitor cells allowing preclinical screening of genetic treatment strategies for the hemoglobinopathies.
Demirci S; Bhardwaj SK; Uchida N; Haro-Mora JJ; Ryu B; Blobel GA; Tisdale JF
Cytotherapy; 2018 Oct; 20(10):1278-1287. PubMed ID: 30249524
[TBL] [Abstract][Full Text] [Related]
57. Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins.
Pavani G; Laurent M; Fabiano A; Cantelli E; Sakkal A; Corre G; Lenting PJ; Concordet JP; Toueille M; Miccio A; Amendola M
Nat Commun; 2020 Jul; 11(1):3778. PubMed ID: 32728076
[TBL] [Abstract][Full Text] [Related]
58. Highly Efficient Genome Editing of Murine and Human Hematopoietic Progenitor Cells by CRISPR/Cas9.
Gundry MC; Brunetti L; Lin A; Mayle AE; Kitano A; Wagner D; Hsu JI; Hoegenauer KA; Rooney CM; Goodell MA; Nakada D
Cell Rep; 2016 Oct; 17(5):1453-1461. PubMed ID: 27783956
[TBL] [Abstract][Full Text] [Related]
59. Bone Marrow as a Hematopoietic Stem Cell Source for Gene Therapy in Sickle Cell Disease: Evidence from Rhesus and SCD Patients.
Uchida N; Fujita A; Hsieh MM; Bonifacino AC; Krouse AE; Metzger ME; Donahue RE; Tisdale JF
Hum Gene Ther Clin Dev; 2017 Sep; 28(3):136-144. PubMed ID: 28447889
[TBL] [Abstract][Full Text] [Related]
60. ATF4 Regulates MYB to Increase γ-Globin in Response to Loss of β-Globin.
Boontanrart MY; Schröder MS; Stehli GM; Banović M; Wyman SK; Lew RJ; Bordi M; Gowen BG; DeWitt MA; Corn JE
Cell Rep; 2020 Aug; 32(5):107993. PubMed ID: 32755585
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]
