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8. The effectiveness and cost-effectiveness of enzyme and substrate replacement therapies: a longitudinal cohort study of people with lysosomal storage disorders. Wyatt K; Henley W; Anderson L; Anderson R; Nikolaou V; Stein K; Klinger L; Hughes D; Waldek S; Lachmann R; Mehta A; Vellodi A; Logan S Health Technol Assess; 2012; 16(39):1-543. PubMed ID: 23089251 [TBL] [Abstract][Full Text] [Related]
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