284 related articles for article (PubMed ID: 33019822)
1. Genetic Rescue of X-Linked Retinoschisis Mouse (
Vijayasarathy C; Zeng Y; Brooks MJ; Fariss RN; Sieving PA
Hum Gene Ther; 2021 Jul; 32(13-14):667-681. PubMed ID: 33019822
[TBL] [Abstract][Full Text] [Related]
2. Of men and mice: Human X-linked retinoschisis and fidelity in mouse modeling.
Vijayasarathy C; Sardar Pasha SPB; Sieving PA
Prog Retin Eye Res; 2022 Mar; 87():100999. PubMed ID: 34390869
[TBL] [Abstract][Full Text] [Related]
3. Intravitreal delivery of AAV8 retinoschisin results in cell type-specific gene expression and retinal rescue in the Rs1-KO mouse.
Park TK; Wu Z; Kjellstrom S; Zeng Y; Bush RA; Sieving PA; Colosi P
Gene Ther; 2009 Jul; 16(7):916-26. PubMed ID: 19458650
[TBL] [Abstract][Full Text] [Related]
4. Preclinical Dose-Escalation Study of Intravitreal AAV-RS1 Gene Therapy in a Mouse Model of X-linked Retinoschisis: Dose-Dependent Expression and Improved Retinal Structure and Function.
Bush RA; Zeng Y; Colosi P; Kjellstrom S; Hiriyanna S; Vijayasarathy C; Santos M; Li J; Wu Z; Sieving PA
Hum Gene Ther; 2016 May; 27(5):376-89. PubMed ID: 27036983
[TBL] [Abstract][Full Text] [Related]
5. Synaptic pathology and therapeutic repair in adult retinoschisis mouse by AAV-RS1 transfer.
Ou J; Vijayasarathy C; Ziccardi L; Chen S; Zeng Y; Marangoni D; Pope JG; Bush RA; Wu Z; Li W; Sieving PA
J Clin Invest; 2015 Jul; 125(7):2891-903. PubMed ID: 26098217
[TBL] [Abstract][Full Text] [Related]
6. An ex vivo gene therapy approach in X-linked retinoschisis.
Bashar AE; Metcalfe AL; Viringipurampeer IA; Yanai A; Gregory-Evans CY; Gregory-Evans K
Mol Vis; 2016; 22():718-33. PubMed ID: 27390514
[TBL] [Abstract][Full Text] [Related]
7. Targeted Expression of Retinoschisin by Retinal Bipolar Cells in XLRS Promotes Resolution of Retinoschisis Cysts Sans RS1 From Photoreceptors.
Vijayasarathy C; Zeng Y; Marangoni D; Dong L; Pan ZH; Simpson EM; Fariss RN; Sieving PA
Invest Ophthalmol Vis Sci; 2022 Oct; 63(11):8. PubMed ID: 36227606
[TBL] [Abstract][Full Text] [Related]
8. Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery.
Cukras C; Wiley HE; Jeffrey BG; Sen HN; Turriff A; Zeng Y; Vijayasarathy C; Marangoni D; Ziccardi L; Kjellstrom S; Park TK; Hiriyanna S; Wright JF; Colosi P; Wu Z; Bush RA; Wei LL; Sieving PA
Mol Ther; 2018 Sep; 26(9):2282-2294. PubMed ID: 30196853
[TBL] [Abstract][Full Text] [Related]
9. Retinal Structure and Gene Therapy Outcome in Retinoschisin-Deficient Mice Assessed by Spectral-Domain Optical Coherence Tomography.
Zeng Y; Petralia RS; Vijayasarathy C; Wu Z; Hiriyanna S; Song H; Wang YX; Sieving PA; Bush RA
Invest Ophthalmol Vis Sci; 2016 Jul; 57(9):OCT277-87. PubMed ID: 27409484
[TBL] [Abstract][Full Text] [Related]
10. Synaptic pathology in retinoschisis knockout (Rs1-/y) mouse retina and modification by rAAV-Rs1 gene delivery.
Takada Y; Vijayasarathy C; Zeng Y; Kjellstrom S; Bush RA; Sieving PA
Invest Ophthalmol Vis Sci; 2008 Aug; 49(8):3677-86. PubMed ID: 18660429
[TBL] [Abstract][Full Text] [Related]
11. Immune function in X-linked retinoschisis subjects in an AAV8-RS1 phase I/IIa gene therapy trial.
Mishra A; Vijayasarathy C; Cukras CA; Wiley HE; Sen HN; Zeng Y; Wei LL; Sieving PA
Mol Ther; 2021 Jun; 29(6):2030-2040. PubMed ID: 33601057
[TBL] [Abstract][Full Text] [Related]
12. The Road towards Gene Therapy for X-Linked Juvenile Retinoschisis: A Systematic Review of Preclinical Gene Therapy in Cell-Based and Rodent Models of XLRS.
van der Veen I; Heredero Berzal A; Koster C; Ten Asbroek ALMA; Bergen AA; Boon CJF
Int J Mol Sci; 2024 Jan; 25(2):. PubMed ID: 38279267
[TBL] [Abstract][Full Text] [Related]
13. Preclinical safety evaluation of a recombinant AAV8 vector for X-linked retinoschisis after intravitreal administration in rabbits.
Marangoni D; Wu Z; Wiley HE; Zeiss CJ; Vijayasarathy C; Zeng Y; Hiriyanna S; Bush RA; Wei LL; Colosi P; Sieving PA
Hum Gene Ther Clin Dev; 2014 Dec; 25(4):202-11. PubMed ID: 25211193
[TBL] [Abstract][Full Text] [Related]
14. Retinoschisin gene therapy and natural history in the Rs1h-KO mouse: long-term rescue from retinal degeneration.
Kjellstrom S; Bush RA; Zeng Y; Takada Y; Sieving PA
Invest Ophthalmol Vis Sci; 2007 Aug; 48(8):3837-45. PubMed ID: 17652759
[TBL] [Abstract][Full Text] [Related]
15. Rs1h
Zeng Y; Qian H; Campos MM; Li Y; Vijayasarathy C; Sieving PA
Gene Ther; 2022 Aug; 29(7-8):431-440. PubMed ID: 34548657
[TBL] [Abstract][Full Text] [Related]
16. Molecular mechanisms leading to null-protein product from retinoschisin (RS1) signal-sequence mutants in X-linked retinoschisis (XLRS) disease.
Vijayasarathy C; Sui R; Zeng Y; Yang G; Xu F; Caruso RC; Lewis RA; Ziccardi L; Sieving PA
Hum Mutat; 2010 Nov; 31(11):1251-60. PubMed ID: 20809529
[TBL] [Abstract][Full Text] [Related]
17. Advances in understanding the molecular structure of retinoschisin while questions remain of biological function.
Heymann JB; Vijayasarathy C; Fariss RN; Sieving PA
Prog Retin Eye Res; 2023 Jul; 95():101147. PubMed ID: 36402656
[TBL] [Abstract][Full Text] [Related]
18. Genetic modification of the schisis phenotype in a mouse model of X-linked retinoschisis.
Johnson BA; Aoyama N; Friedell NH; Ikeda S; Ikeda A
Genetics; 2008 Mar; 178(3):1785-94. PubMed ID: 18245825
[TBL] [Abstract][Full Text] [Related]
19. Photoreceptor deficits appear at eye opening in Rs1 mutant mouse models of X-linked retinoschisis.
Tarchick MJ; Beight C; Bonezzi PB; Peachey NS; Renna JM
Exp Eye Res; 2024 May; 242():109872. PubMed ID: 38514024
[TBL] [Abstract][Full Text] [Related]
20. XLRS Rat with Rs1
Ye EA; Zeng Y; Thomas S; Sun N; Smit-McBride Z; Sieving PA
Genes (Basel); 2022 Oct; 13(11):. PubMed ID: 36360232
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]