199 related articles for article (PubMed ID: 33102618)
1.
Wada M; Shimada Y; Iizuka S; Ishii N; Hiraki H; Tachibana T; Maeda K; Saito M; Arakawa S; Ishimoto T; Nakano T; Ida H; Ohashi T; Kobayashi H
Mol Ther Methods Clin Dev; 2020 Dec; 19():261-274. PubMed ID: 33102618
[TBL] [Abstract][Full Text] [Related]
2. Prevention of Neurocognitive Deficiency in Mucopolysaccharidosis Type II Mice by Central Nervous System-Directed, AAV9-Mediated Iduronate Sulfatase Gene Transfer.
Laoharawee K; Podetz-Pedersen KM; Nguyen TT; Evenstar LB; Kitto KF; Nan Z; Fairbanks CA; Low WC; Kozarsky KF; McIvor RS
Hum Gene Ther; 2017 Aug; 28(8):626-638. PubMed ID: 28478695
[TBL] [Abstract][Full Text] [Related]
3. Hematopoietic Stem Cell Gene Therapy Corrects Neuropathic Phenotype in Murine Model of Mucopolysaccharidosis Type II.
Wakabayashi T; Shimada Y; Akiyama K; Higuchi T; Fukuda T; Kobayashi H; Eto Y; Ida H; Ohashi T
Hum Gene Ther; 2015 Jun; 26(6):357-66. PubMed ID: 25761450
[TBL] [Abstract][Full Text] [Related]
4. Enzyme replacement therapy in mucopolysaccharidosis type II (Hunter syndrome): a preliminary report.
Muenzer J; Lamsa JC; Garcia A; Dacosta J; Garcia J; Treco DA
Acta Paediatr Suppl; 2002; 91(439):98-9. PubMed ID: 12572850
[TBL] [Abstract][Full Text] [Related]
5. Genetics and Gene Therapy in Hunter Disease.
Sestito S; Falvo F; Scozzafava C; Apa R; Pensabene L; Bonapace G; Moricca MT; Concolino D
Curr Gene Ther; 2018; 18(2):90-95. PubMed ID: 29618310
[TBL] [Abstract][Full Text] [Related]
6. Enzyme augmentation therapy enhances the therapeutic efficacy of bone marrow transplantation in mucopolysaccharidosis type II mice.
Akiyama K; Shimada Y; Higuchi T; Ohtsu M; Nakauchi H; Kobayashi H; Fukuda T; Ida H; Eto Y; Crawford BE; Brown JR; Ohashi T
Mol Genet Metab; 2014 Feb; 111(2):139-46. PubMed ID: 24100247
[TBL] [Abstract][Full Text] [Related]
7. Enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II (Hunter syndrome).
da Silva EM; Strufaldi MW; Andriolo RB; Silva LA
Cochrane Database Syst Rev; 2014 Jan; (1):CD008185. PubMed ID: 24399699
[TBL] [Abstract][Full Text] [Related]
8. Enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II (Hunter syndrome).
da Silva EM; Strufaldi MW; Andriolo RB; Silva LA
Cochrane Database Syst Rev; 2011 Nov; (11):CD008185. PubMed ID: 22071845
[TBL] [Abstract][Full Text] [Related]
9. Effect of donor chimerism to reduce the level of glycosaminoglycans following bone marrow transplantation in a murine model of mucopolysaccharidosis type II.
Yokoi K; Akiyama K; Kaneshiro E; Higuchi T; Shimada Y; Kobayashi H; Akiyama M; Otsu M; Nakauchi H; Ohashi T; Ida H
J Inherit Metab Dis; 2015 Mar; 38(2):333-40. PubMed ID: 25503568
[TBL] [Abstract][Full Text] [Related]
10. Enzyme replacement therapy (ERT) procedure for mucopolysaccharidosis type II (MPS II) by intraventricular administration (IVA) in murine MPS II.
Higuchi T; Shimizu H; Fukuda T; Kawagoe S; Matsumoto J; Shimada Y; Kobayashi H; Ida H; Ohashi T; Morimoto H; Hirato T; Nishino K; Eto Y
Mol Genet Metab; 2012 Sep; 107(1-2):122-8. PubMed ID: 22704483
[TBL] [Abstract][Full Text] [Related]
11. Enzyme replacement therapy with idursulfase in patients with mucopolysaccharidosis type II.
Wraith JE
Acta Paediatr; 2008 Apr; 97(457):76-8. PubMed ID: 18339193
[TBL] [Abstract][Full Text] [Related]
12. Evaluation of cerebrospinal fluid heparan sulfate as a biomarker of neuropathology in a murine model of mucopolysaccharidosis type II using high-sensitivity LC/MS/MS.
Tanaka N; Kida S; Kinoshita M; Morimoto H; Shibasaki T; Tachibana K; Yamamoto R
Mol Genet Metab; 2018 Sep; 125(1-2):53-58. PubMed ID: 30064964
[TBL] [Abstract][Full Text] [Related]
13. Effectiveness of Early Hematopoietic Stem Cell Transplantation in Preventing Neurocognitive Decline in Mucopolysaccharidosis Type II: A Case Series.
Selvanathan A; Ellaway C; Wilson C; Owens P; Shaw PJ; Bhattacharya K
JIMD Rep; 2018; 41():81-89. PubMed ID: 29671225
[TBL] [Abstract][Full Text] [Related]
14. Effect of systemic high dose enzyme replacement therapy on the improvement of CNS defects in a mouse model of mucopolysaccharidosis type II.
Cho SY; Lee J; Ko AR; Kwak MJ; Kim S; Sohn YB; Park SW; Jin DK
Orphanet J Rare Dis; 2015 Oct; 10():141. PubMed ID: 26520066
[TBL] [Abstract][Full Text] [Related]
15. Impaired bone remodeling and its correction by combination therapy in a mouse model of mucopolysaccharidosis-I.
Kuehn SC; Koehne T; Cornils K; Markmann S; Riedel C; Pestka JM; Schweizer M; Baldauf C; Yorgan TA; Krause M; Keller J; Neven M; Breyer S; Stuecker R; Muschol N; Busse B; Braulke T; Fehse B; Amling M; Schinke T
Hum Mol Genet; 2015 Dec; 24(24):7075-86. PubMed ID: 26427607
[TBL] [Abstract][Full Text] [Related]
16. Distribution of heparan sulfate and dermatan sulfate in mucopolysaccharidosis type II mouse tissues pre- and post-enzyme-replacement therapy determined by UPLC-MS/MS.
Menkovic I; Lavoie P; Boutin M; Auray-Blais C
Bioanalysis; 2019 Apr; 11(8):727-740. PubMed ID: 30994022
[No Abstract] [Full Text] [Related]
17. Extension of the molecular analysis to the promoter region of the iduronate 2-sulfatase gene reveals genomic alterations in mucopolysaccharidosis type II patients with normal coding sequence.
Brusius-Facchin AC; Abrahão L; Schwartz IV; Lourenço CM; Santos ES; Zanetti A; Tomanin R; Scarpa M; Giugliani R; Leistner-Segal S
Gene; 2013 Sep; 526(2):150-4. PubMed ID: 23707223
[TBL] [Abstract][Full Text] [Related]
18. Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial.
Okuyama T; Eto Y; Sakai N; Minami K; Yamamoto T; Sonoda H; Yamaoka M; Tachibana K; Hirato T; Sato Y
Mol Ther; 2019 Feb; 27(2):456-464. PubMed ID: 30595526
[TBL] [Abstract][Full Text] [Related]
19. Brain-targeted stem cell gene therapy corrects mucopolysaccharidosis type II via multiple mechanisms.
Gleitz HF; Liao AY; Cook JR; Rowlston SF; Forte GM; D'Souza Z; O'Leary C; Holley RJ; Bigger BW
EMBO Mol Med; 2018 Jul; 10(7):. PubMed ID: 29884617
[TBL] [Abstract][Full Text] [Related]
20. Improvement of CNS defects via continuous intrathecal enzyme replacement by osmotic pump in mucopolysaccharidosis type II mice.
Sohn YB; Lee J; Cho SY; Kim SJ; Ko AR; Nam MH; Jin DK
Am J Med Genet A; 2013 May; 161A(5):1036-43. PubMed ID: 23529876
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
