These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

417 related articles for article (PubMed ID: 33221437)

  • 1. Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases.
    Tucci F; Scaramuzza S; Aiuti A; Mortellaro A
    Mol Ther; 2021 Feb; 29(2):489-504. PubMed ID: 33221437
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Enhanced genetic modification of adult growth factor mobilized peripheral blood hematopoietic stem and progenitor cells with rapamycin.
    Li L; Torres-Coronado M; Gu A; Rao A; Gardner AM; Epps EW; Gonzalez N; Tran CA; Wu X; Wang JH; DiGiusto DL
    Stem Cells Transl Med; 2014 Oct; 3(10):1199-208. PubMed ID: 25107584
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Assessing the Impact of Cyclosporin A on Lentiviral Transduction and Preservation of Human Hematopoietic Stem Cells in Clinically Relevant
    Petrillo C; Calabria A; Piras F; Capotondo A; Spinozzi G; Cuccovillo I; Benedicenti F; Naldini L; Montini E; Biffi A; Gentner B; Kajaste-Rudnitski A
    Hum Gene Ther; 2019 Sep; 30(9):1133-1146. PubMed ID: 31037976
    [TBL] [Abstract][Full Text] [Related]  

  • 4. A systematic review and meta-analysis of gene therapy with hematopoietic stem and progenitor cells for monogenic disorders.
    Tucci F; Galimberti S; Naldini L; Valsecchi MG; Aiuti A
    Nat Commun; 2022 Mar; 13(1):1315. PubMed ID: 35288539
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study.
    Ferrua F; Cicalese MP; Galimberti S; Giannelli S; Dionisio F; Barzaghi F; Migliavacca M; Bernardo ME; Calbi V; Assanelli AA; Facchini M; Fossati C; Albertazzi E; Scaramuzza S; Brigida I; Scala S; Basso-Ricci L; Pajno R; Casiraghi M; Canarutto D; Salerio FA; Albert MH; Bartoli A; Wolf HM; Fiori R; Silvani P; Gattillo S; Villa A; Biasco L; Dott C; Culme-Seymour EJ; van Rossem K; Atkinson G; Valsecchi MG; Roncarolo MG; Ciceri F; Naldini L; Aiuti A
    Lancet Haematol; 2019 May; 6(5):e239-e253. PubMed ID: 30981783
    [TBL] [Abstract][Full Text] [Related]  

  • 6. A Short and Efficient Transduction Protocol for Mouse Hematopoietic Stem Cells with Lentiviral Vectors.
    Fernández-García M; Mesa C; Almarza E; Bueren J; Yañez R
    Hum Gene Ther Methods; 2017 Dec; 28(6):310-317. PubMed ID: 28817977
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Stem Cell Genetic Therapy for Fanconi Anemia - A New Hope.
    Hanenberg H; Roellecke K; Wiek C
    Curr Gene Ther; 2017; 16(5):309-320. PubMed ID: 28067166
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.
    Aiuti A; Biasco L; Scaramuzza S; Ferrua F; Cicalese MP; Baricordi C; Dionisio F; Calabria A; Giannelli S; Castiello MC; Bosticardo M; Evangelio C; Assanelli A; Casiraghi M; Di Nunzio S; Callegaro L; Benati C; Rizzardi P; Pellin D; Di Serio C; Schmidt M; Von Kalle C; Gardner J; Mehta N; Neduva V; Dow DJ; Galy A; Miniero R; Finocchi A; Metin A; Banerjee PP; Orange JS; Galimberti S; Valsecchi MG; Biffi A; Montini E; Villa A; Ciceri F; Roncarolo MG; Naldini L
    Science; 2013 Aug; 341(6148):1233151. PubMed ID: 23845947
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Gene therapy using haematopoietic stem and progenitor cells.
    Ferrari G; Thrasher AJ; Aiuti A
    Nat Rev Genet; 2021 Apr; 22(4):216-234. PubMed ID: 33303992
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Lentiviral hematopoietic stem cell gene therapy in inherited metabolic disorders.
    Wagemaker G
    Hum Gene Ther; 2014 Oct; 25(10):862-5. PubMed ID: 25184354
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Promises and Challenges in Hematopoietic Stem Cell Gene Therapy.
    Kohlscheen S; Bonig H; Modlich U
    Hum Gene Ther; 2017 Oct; 28(10):782-799. PubMed ID: 28854824
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Gene transfer into hematopoietic stem cells using lentiviral vectors.
    Scherr M; Eder M
    Curr Gene Ther; 2002 Feb; 2(1):45-55. PubMed ID: 12108973
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Prostaglandin E
    Heffner GC; Bonner M; Christiansen L; Pierciey FJ; Campbell D; Smurnyy Y; Zhang W; Hamel A; Shaw S; Lewis G; Goss KA; Garijo O; Torbett BE; Horton H; Finer MH; Gregory PD; Veres G
    Mol Ther; 2018 Jan; 26(1):320-328. PubMed ID: 29102562
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Promising Results with Ex Vivo Lentiviral HSPC Gene Therapy in ADA-SCID.
    Am J Med Genet A; 2021 Aug; 185(8):2291-2292. PubMed ID: 34240545
    [No Abstract]   [Full Text] [Related]  

  • 15. Preclinical Development of a Hematopoietic Stem and Progenitor Cell Bioengineered Factor VIII Lentiviral Vector Gene Therapy for Hemophilia A.
    Doering CB; Denning G; Shields JE; Fine EJ; Parker ET; Srivastava A; Lollar P; Spencer HT
    Hum Gene Ther; 2018 Oct; 29(10):1183-1201. PubMed ID: 30160169
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Advancements in Hematopoietic Stem Cell Gene Therapy: A Journey of Progress for Viral Transduction.
    Giommetti A; Papanikolaou E
    Cells; 2024 Jun; 13(12):. PubMed ID: 38920667
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Gene Therapy in Fanconi Anemia: A Matter of Time, Safety and Gene Transfer Tool Efficiency.
    Verhoeyen E; Roman-Rodriguez FJ; Cosset FL; Levy C; Rio P
    Curr Gene Ther; 2017; 16(5):297-308. PubMed ID: 28067165
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Lentiviral vectors escape innate sensing but trigger p53 in human hematopoietic stem and progenitor cells.
    Piras F; Riba M; Petrillo C; Lazarevic D; Cuccovillo I; Bartolaccini S; Stupka E; Gentner B; Cittaro D; Naldini L; Kajaste-Rudnitski A
    EMBO Mol Med; 2017 Sep; 9(9):1198-1211. PubMed ID: 28667090
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34
    Río P; Navarro S; Guenechea G; Sánchez-Domínguez R; Lamana ML; Yañez R; Casado JA; Mehta PA; Pujol MR; Surrallés J; Charrier S; Galy A; Segovia JC; Díaz de Heredia C; Sevilla J; Bueren JA
    Blood; 2017 Sep; 130(13):1535-1542. PubMed ID: 28801449
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Lentiviral Transduction of Nonhuman Primate Hematopoietic Stem and Progenitor Cells.
    Wu C; Hong SG; Bonifacino A; Dunbar CE
    Methods Mol Biol; 2023; 2567():63-84. PubMed ID: 36255695
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 21.