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9. Treatment of lysosomal storage diseases: recent patents and future strategies. Ortolano S; Viéitez I; Navarro C; Spuch C Recent Pat Endocr Metab Immune Drug Discov; 2014 Jan; 8(1):9-25. PubMed ID: 24433521 [TBL] [Abstract][Full Text] [Related]
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13. The effectiveness and cost-effectiveness of enzyme and substrate replacement therapies: a longitudinal cohort study of people with lysosomal storage disorders. Wyatt K; Henley W; Anderson L; Anderson R; Nikolaou V; Stein K; Klinger L; Hughes D; Waldek S; Lachmann R; Mehta A; Vellodi A; Logan S Health Technol Assess; 2012; 16(39):1-543. PubMed ID: 23089251 [TBL] [Abstract][Full Text] [Related]
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