BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

270 related articles for article (PubMed ID: 33398131)

  • 1. Lentiviral delivery of co-packaged Cas9 mRNA and a Vegfa-targeting guide RNA prevents wet age-related macular degeneration in mice.
    Ling S; Yang S; Hu X; Yin D; Dai Y; Qian X; Wang D; Pan X; Hong J; Sun X; Yang H; Paludan SR; Cai Y
    Nat Biomed Eng; 2021 Feb; 5(2):144-156. PubMed ID: 33398131
    [TBL] [Abstract][Full Text] [Related]  

  • 2. CRISPR-LbCpf1 prevents choroidal neovascularization in a mouse model of age-related macular degeneration.
    Koo T; Park SW; Jo DH; Kim D; Kim JH; Cho HY; Kim J; Kim JH; Kim JS
    Nat Commun; 2018 May; 9(1):1855. PubMed ID: 29748595
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Genome surgery using Cas9 ribonucleoproteins for the treatment of age-related macular degeneration.
    Kim K; Park SW; Kim JH; Lee SH; Kim D; Koo T; Kim KE; Kim JH; Kim JS
    Genome Res; 2017 Mar; 27(3):419-426. PubMed ID: 28209587
    [TBL] [Abstract][Full Text] [Related]  

  • 4. CRISPR/Cas9 mediated specific ablation of vegfa in retinal pigment epithelium efficiently regresses choroidal neovascularization.
    Park J; Cui G; Lee H; Jeong H; Kwak JJ; Lee J; Byeon SH
    Sci Rep; 2023 Mar; 13(1):3715. PubMed ID: 36878916
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Nme
    Hu S; Chen Y; Xie D; Xu K; Fu Y; Chi W; Liu H; Huang J
    Clin Transl Med; 2023 Aug; 13(8):e1383. PubMed ID: 37598400
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Targeted Knockout of the Vegfa Gene in the Retina by Subretinal Injection of RNP Complexes Containing Cas9 Protein and Modified sgRNAs.
    Holmgaard AB; Askou AL; Jensen EG; Alsing S; Bak RO; Mikkelsen JG; Corydon TJ
    Mol Ther; 2021 Jan; 29(1):191-207. PubMed ID: 33022212
    [TBL] [Abstract][Full Text] [Related]  

  • 7. CRISPR Gene Therapy of the Eye: Targeted Knockout of Vegfa in Mouse Retina by Lentiviral Delivery.
    Holmgaard A; Alsing S; Askou AL; Corydon TJ
    Methods Mol Biol; 2019; 1961():307-328. PubMed ID: 30912054
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Suppression of Choroidal Neovascularization in Mice by Subretinal Delivery of Multigenic Lentiviral Vectors Encoding Anti-Angiogenic MicroRNAs.
    Askou AL; Benckendorff JNE; Holmgaard A; Storm T; Aagaard L; Bek T; Mikkelsen JG; Corydon TJ
    Hum Gene Ther Methods; 2017 Aug; 28(4):222-233. PubMed ID: 28817343
    [TBL] [Abstract][Full Text] [Related]  

  • 9. In vivo genome editing with a small Cas9 orthologue derived from Campylobacter jejuni.
    Kim E; Koo T; Park SW; Kim D; Kim K; Cho HY; Song DW; Lee KJ; Jung MH; Kim S; Kim JH; Kim JH; Kim JS
    Nat Commun; 2017 Feb; 8():14500. PubMed ID: 28220790
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Tumor cell-targeted delivery of CRISPR/Cas9 by aptamer-functionalized lipopolymer for therapeutic genome editing of VEGFA in osteosarcoma.
    Liang C; Li F; Wang L; Zhang ZK; Wang C; He B; Li J; Chen Z; Shaikh AB; Liu J; Wu X; Peng S; Dang L; Guo B; He X; Au DWT; Lu C; Zhu H; Zhang BT; Lu A; Zhang G
    Biomaterials; 2017 Dec; 147():68-85. PubMed ID: 28938163
    [TBL] [Abstract][Full Text] [Related]  

  • 11. In Vivo Knockout of the Vegfa Gene by Lentiviral Delivery of CRISPR/Cas9 in Mouse Retinal Pigment Epithelium Cells.
    Holmgaard A; Askou AL; Benckendorff JNE; Thomsen EA; Cai Y; Bek T; Mikkelsen JG; Corydon TJ
    Mol Ther Nucleic Acids; 2017 Dec; 9():89-99. PubMed ID: 29246327
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Development of gene therapy for treatment of age-related macular degeneration.
    Askou AL
    Acta Ophthalmol; 2014 Jul; 92 Thesis3():1-38. PubMed ID: 24953666
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Delivering Cas9/sgRNA ribonucleoprotein (RNP) by lentiviral capsid-based bionanoparticles for efficient 'hit-and-run' genome editing.
    Lyu P; Javidi-Parsijani P; Atala A; Lu B
    Nucleic Acids Res; 2019 Sep; 47(17):e99. PubMed ID: 31299082
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Improved CRISPR genome editing using small highly active and specific engineered RNA-guided nucleases.
    Schmidt MJ; Gupta A; Bednarski C; Gehrig-Giannini S; Richter F; Pitzler C; Gamalinda M; Galonska C; Takeuchi R; Wang K; Reiss C; Dehne K; Lukason MJ; Noma A; Park-Windhol C; Allocca M; Kantardzhieva A; Sane S; Kosakowska K; Cafferty B; Tebbe J; Spencer SJ; Munzer S; Cheng CJ; Scaria A; Scharenberg AM; Cohnen A; Coco WM
    Nat Commun; 2021 Jul; 12(1):4219. PubMed ID: 34244505
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Efficient viral delivery of Cas9 into human safe harbor.
    Hayashi H; Kubo Y; Izumida M; Matsuyama T
    Sci Rep; 2020 Dec; 10(1):21474. PubMed ID: 33293588
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Lentiviral Vectors for Delivery of Gene-Editing Systems Based on CRISPR/Cas: Current State and Perspectives.
    Dong W; Kantor B
    Viruses; 2021 Jul; 13(7):. PubMed ID: 34372494
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Safeguarding genome integrity during gene-editing therapy in a mouse model of age-related macular degeneration.
    Yin J; Fang K; Gao Y; Ou L; Yuan S; Xin C; Wu W; Wu WW; Hong J; Yang H; Hu J
    Nat Commun; 2022 Dec; 13(1):7867. PubMed ID: 36550137
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Gene Therapy with CRISPR/Cas9 Coming to Age for HIV Cure.
    Soriano V
    AIDS Rev; 2017; 19(3):167-172. PubMed ID: 29019352
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Optical Control of a CRISPR/Cas9 System for Gene Editing by Using Photolabile crRNA.
    Zhang Y; Ling X; Su X; Zhang S; Wang J; Zhang P; Feng W; Zhu YY; Liu T; Tang X
    Angew Chem Int Ed Engl; 2020 Nov; 59(47):20895-20899. PubMed ID: 33448579
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Comparison of Zinc Finger Nucleases Versus CRISPR-Specific Nucleases for Genome Editing of the Wiskott-Aldrich Syndrome Locus.
    Gutierrez-Guerrero A; Sanchez-Hernandez S; Galvani G; Pinedo-Gomez J; Martin-Guerra R; Sanchez-Gilabert A; Aguilar-González A; Cobo M; Gregory P; Holmes M; Benabdellah K; Martin F
    Hum Gene Ther; 2018 Mar; 29(3):366-380. PubMed ID: 28922955
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 14.