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8. Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells. DeWitt MA; Magis W; Bray NL; Wang T; Berman JR; Urbinati F; Heo SJ; Mitros T; Muñoz DP; Boffelli D; Kohn DB; Walters MC; Carroll D; Martin DI; Corn JE Sci Transl Med; 2016 Oct; 8(360):360ra134. PubMed ID: 27733558 [TBL] [Abstract][Full Text] [Related]
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14. Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates. Romero Z; Lomova A; Said S; Miggelbrink A; Kuo CY; Campo-Fernandez B; Hoban MD; Masiuk KE; Clark DN; Long J; Sanchez JM; Velez M; Miyahira E; Zhang R; Brown D; Wang X; Kurmangaliyev YZ; Hollis RP; Kohn DB Mol Ther; 2019 Aug; 27(8):1389-1406. PubMed ID: 31178391 [TBL] [Abstract][Full Text] [Related]
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18. Base editing of haematopoietic stem cells rescues sickle cell disease in mice. Newby GA; Yen JS; Woodard KJ; Mayuranathan T; Lazzarotto CR; Li Y; Sheppard-Tillman H; Porter SN; Yao Y; Mayberry K; Everette KA; Jang Y; Podracky CJ; Thaman E; Lechauve C; Sharma A; Henderson JM; Richter MF; Zhao KT; Miller SM; Wang T; Koblan LW; McCaffrey AP; Tisdale JF; Kalfa TA; Pruett-Miller SM; Tsai SQ; Weiss MJ; Liu DR Nature; 2021 Jul; 595(7866):295-302. PubMed ID: 34079130 [TBL] [Abstract][Full Text] [Related]
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