280 related articles for article (PubMed ID: 34047257)
21. Sickle Cell Disease: From Genetics to Curative Approaches.
Hardouin G; Magrin E; Corsia A; Cavazzana M; Miccio A; Semeraro M
Annu Rev Genomics Hum Genet; 2023 Aug; 24():255-275. PubMed ID: 37624668
[TBL] [Abstract][Full Text] [Related]
22. Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells.
Hoban MD; Cost GJ; Mendel MC; Romero Z; Kaufman ML; Joglekar AV; Ho M; Lumaquin D; Gray D; Lill GR; Cooper AR; Urbinati F; Senadheera S; Zhu A; Liu PQ; Paschon DE; Zhang L; Rebar EJ; Wilber A; Wang X; Gregory PD; Holmes MC; Reik A; Hollis RP; Kohn DB
Blood; 2015 Apr; 125(17):2597-604. PubMed ID: 25733580
[TBL] [Abstract][Full Text] [Related]
23. Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia.
Dong AC; Rivella S
Adv Exp Med Biol; 2017; 1013():155-176. PubMed ID: 29127680
[TBL] [Abstract][Full Text] [Related]
24. Curative Therapies for Sickle Cell Disease.
Kaviany S; Barnawi Z; LaBelle J
Pediatr Ann; 2024 Feb; 53(2):e56-e61. PubMed ID: 38302122
[TBL] [Abstract][Full Text] [Related]
25. In vivo HSC prime editing rescues sickle cell disease in a mouse model.
Li C; Georgakopoulou A; Newby GA; Chen PJ; Everette KA; Paschoudi K; Vlachaki E; Gil S; Anderson AK; Koob T; Huang L; Wang H; Kiem HP; Liu DR; Yannaki E; Lieber A
Blood; 2023 Apr; 141(17):2085-2099. PubMed ID: 36800642
[TBL] [Abstract][Full Text] [Related]
26. Effective therapies for sickle cell disease: are we there yet?
Crossley M; Christakopoulos GE; Weiss MJ
Trends Genet; 2022 Dec; 38(12):1284-1298. PubMed ID: 35934593
[TBL] [Abstract][Full Text] [Related]
27. Editing outside the body: Ex vivo gene-modification for β-hemoglobinopathy cellular therapy.
Rosanwo TO; Bauer DE
Mol Ther; 2021 Nov; 29(11):3163-3178. PubMed ID: 34628053
[TBL] [Abstract][Full Text] [Related]
28. Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells.
DeWitt MA; Magis W; Bray NL; Wang T; Berman JR; Urbinati F; Heo SJ; Mitros T; Muñoz DP; Boffelli D; Kohn DB; Walters MC; Carroll D; Martin DI; Corn JE
Sci Transl Med; 2016 Oct; 8(360):360ra134. PubMed ID: 27733558
[TBL] [Abstract][Full Text] [Related]
29. A New Era for Hemoglobinopathies: More Than One Curative Option.
Psatha N; Papayanni PG; Yannaki E
Curr Gene Ther; 2017; 17(5):364-378. PubMed ID: 29357790
[TBL] [Abstract][Full Text] [Related]
30. Curative approaches for sickle cell disease: A review of allogeneic and autologous strategies.
Bauer DE; Brendel C; Fitzhugh CD
Blood Cells Mol Dis; 2017 Sep; 67():155-168. PubMed ID: 28893518
[TBL] [Abstract][Full Text] [Related]
31. Under the hood: The molecular biology driving gene therapy for the treatment of sickle cell disease.
Waldron E; Tanhehco YC
Transfus Apher Sci; 2022 Oct; 61(5):103566. PubMed ID: 36115765
[TBL] [Abstract][Full Text] [Related]
32. Emerging Genetic Therapy for Sickle Cell Disease.
Orkin SH; Bauer DE
Annu Rev Med; 2019 Jan; 70():257-271. PubMed ID: 30355263
[TBL] [Abstract][Full Text] [Related]
33. Investigational curative gene therapy approaches to sickle cell disease.
Williams DA; Esrick E
Blood Adv; 2021 Dec; 5(23):5452. PubMed ID: 34905048
[TBL] [Abstract][Full Text] [Related]
34. Genome Editing for the β-Hemoglobinopathies.
Porteus MH
Adv Exp Med Biol; 2017; 1013():203-217. PubMed ID: 29127682
[TBL] [Abstract][Full Text] [Related]
35. Gene editing for sickle cell disease and transfusion dependent thalassemias- A cure within reach.
Eckrich MJ; Frangoul H
Semin Hematol; 2023 Jan; 60(1):3-9. PubMed ID: 37080708
[TBL] [Abstract][Full Text] [Related]
36. Correction of murine sickle cell disease using gamma-globin lentiviral vectors to mediate high-level expression of fetal hemoglobin.
Pestina TI; Hargrove PW; Jay D; Gray JT; Boyd KM; Persons DA
Mol Ther; 2009 Feb; 17(2):245-52. PubMed ID: 19050697
[TBL] [Abstract][Full Text] [Related]
37. Hematopoietic stem cell transplantation and cellular therapy in sickle cell disease: where are we now?
Tanhehco YC; Bhatia M
Curr Opin Hematol; 2019 Nov; 26(6):448-452. PubMed ID: 31483336
[TBL] [Abstract][Full Text] [Related]
38. Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders.
Persons DA
Hematology Am Soc Hematol Educ Program; 2009; ():690-7. PubMed ID: 20008255
[TBL] [Abstract][Full Text] [Related]
39. Gene therapy for sickle cell disease: An update.
Demirci S; Uchida N; Tisdale JF
Cytotherapy; 2018 Jul; 20(7):899-910. PubMed ID: 29859773
[TBL] [Abstract][Full Text] [Related]
40. Stem cell transplantation in sickle cell disease: therapeutic potential and challenges faced.
Leonard A; Tisdale JF
Expert Rev Hematol; 2018 Jul; 11(7):547-565. PubMed ID: 29883237
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]