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2. Correction of metabolic, craniofacial, and neurologic abnormalities in MPS I mice treated at birth with adeno-associated virus vector transducing the human alpha-L-iduronidase gene. Hartung SD; Frandsen JL; Pan D; Koniar BL; Graupman P; Gunther R; Low WC; Whitley CB; McIvor RS Mol Ther; 2004 Jun; 9(6):866-75. PubMed ID: 15194053 [TBL] [Abstract][Full Text] [Related]
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