These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
9. Four Individuals with a Homozygous Mutation in Exon 1f of the Mroczek M; Durmus H; Töpf A; Parman Y; Straub V Genes (Basel); 2020 Jun; 11(7):. PubMed ID: 32605089 [TBL] [Abstract][Full Text] [Related]
10. Recessive variants of MuSK are associated with late onset CMS and predominant limb girdle weakness. Owen D; Töpf A; Preethish-Kumar V; Lorenzoni PJ; Vroling B; Scola RH; Dias-Tosta E; Geraldo A; Polavarapu K; Nashi S; Cox D; Evangelista T; Dawson J; Thompson R; Senderek J; Laurie S; Beltran S; Gut M; Gut I; Nalini A; Lochmüller H Am J Med Genet A; 2018 Jul; 176(7):1594-1601. PubMed ID: 29704306 [TBL] [Abstract][Full Text] [Related]
11. Limb-girdle muscular dystrophy due to GMPPB mutations: A case report and comprehensive literature review. Sun L; Shen D; Xiong T; Zhou Z; Lu X; Cui F Bosn J Basic Med Sci; 2020 May; 20(2):275-280. PubMed ID: 30684953 [TBL] [Abstract][Full Text] [Related]
12. LAMA2-related myopathy: Frequency among congenital and limb-girdle muscular dystrophies. Løkken N; Born AP; Duno M; Vissing J Muscle Nerve; 2015 Oct; 52(4):547-53. PubMed ID: 25663498 [TBL] [Abstract][Full Text] [Related]
13. Clinical, pathological, imaging, and genetic characterization in a Taiwanese cohort with limb-girdle muscular dystrophy. Liang WC; Jong YJ; Wang CH; Wang CH; Tian X; Chen WZ; Kan TM; Minami N; Nishino I; Wong LC Orphanet J Rare Dis; 2020 Jun; 15(1):160. PubMed ID: 32576226 [TBL] [Abstract][Full Text] [Related]
14. Congenital myasthenic syndrome due to DOK7 mutation in a cohort of patients with 'unexplained' limb-girdle muscular weakness. Lorenzoni PJ; Kay CSK; Arndt RC; Hrysay NMC; Ducci RD; Fustes OHJ; Töpf A; Lochmüller H; Werneck LC; Scola RH J Clin Neurosci; 2020 May; 75():195-198. PubMed ID: 32238315 [TBL] [Abstract][Full Text] [Related]
15. Early and long-term effect of the treatment with pyridostigmine in patients with GMPPB-related congenital myasthenic syndrome. Bobadilla-Quesada EJ; Natera-de Benito D; Carrera-García L; Ortez C; Exposito-Escudero J; Jimenez-Mallebrera C; Jou C; Codina A; Corbera J; Moya O; Saez V; Gonzalez-Quereda L; Gallano P; Colomer J; Cuadras D; Medina J; Yoldi ME; Nascimento A Neuromuscul Disord; 2020 Sep; 30(9):719-726. PubMed ID: 32819792 [TBL] [Abstract][Full Text] [Related]
16. Expanding the phenotype of GMPPB mutations. Cabrera-Serrano M; Ghaoui R; Ravenscroft G; Johnsen RD; Davis MR; Corbett A; Reddel S; Sue CM; Liang C; Waddell LB; Kaur S; Lek M; North KN; MacArthur DG; Lamont PJ; Clarke NF; Laing NG Brain; 2015 Apr; 138(Pt 4):836-44. PubMed ID: 25681410 [TBL] [Abstract][Full Text] [Related]
17. Clinical features of the myasthenic syndrome arising from mutations in GMPPB. Rodríguez Cruz PM; Belaya K; Basiri K; Sedghi M; Farrugia ME; Holton JL; Liu WW; Maxwell S; Petty R; Walls TJ; Kennett R; Pitt M; Sarkozy A; Parton M; Lochmüller H; Muntoni F; Palace J; Beeson D J Neurol Neurosurg Psychiatry; 2016 Aug; 87(8):802-9. PubMed ID: 27147698 [TBL] [Abstract][Full Text] [Related]
18. Use of Whole-Exome Sequencing for Diagnosis of Limb-Girdle Muscular Dystrophy: Outcomes and Lessons Learned. Ghaoui R; Cooper ST; Lek M; Jones K; Corbett A; Reddel SW; Needham M; Liang C; Waddell LB; Nicholson G; O'Grady G; Kaur S; Ong R; Davis M; Sue CM; Laing NG; North KN; MacArthur DG; Clarke NF JAMA Neurol; 2015 Dec; 72(12):1424-32. PubMed ID: 26436962 [TBL] [Abstract][Full Text] [Related]
19. A founder mutation in Anoctamin 5 is a major cause of limb-girdle muscular dystrophy. Hicks D; Sarkozy A; Muelas N; Köehler K; Huebner A; Hudson G; Chinnery PF; Barresi R; Eagle M; Polvikoski T; Bailey G; Miller J; Radunovic A; Hughes PJ; Roberts R; Krause S; Walter MC; Laval SH; Straub V; Lochmüller H; Bushby K Brain; 2011 Jan; 134(Pt 1):171-182. PubMed ID: 21186264 [TBL] [Abstract][Full Text] [Related]
20. Clinical and genetic characterisation of a large Indian congenital myasthenic syndrome cohort. Polavarapu K; Sunitha B; Töpf A; Preethish-Kumar V; Thompson R; Vengalil S; Nashi S; Bardhan M; Sanka SB; Huddar A; Unnikrishnan G; Arunachal G; Girija MS; Porter A; Azuma Y; Lorenzoni PJ; Baskar D; Anjanappa RM; Keertipriya M; Padmanabh H; Harikrishna GV; Laurie S; Matalonga L; Horvath R; Nalini A; Lochmüller H Brain; 2024 Jan; 147(1):281-296. PubMed ID: 37721175 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]