264 related articles for article (PubMed ID: 34363036)
1. Non-viral delivery of CRISPR-Cas9 complexes for targeted gene editing via a polymer delivery system.
O'Keeffe Ahern J; Lara-Sáez I; Zhou D; Murillas R; Bonafont J; Mencía Á; García M; Manzanares D; Lynch J; Foley R; Xu Q; Sigen A; Larcher F; Wang W
Gene Ther; 2022 Apr; 29(3-4):157-170. PubMed ID: 34363036
[TBL] [Abstract][Full Text] [Related]
2. Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing.
Bonafont J; Mencía Á; García M; Torres R; Rodríguez S; Carretero M; Chacón-Solano E; Modamio-Høybjør S; Marinas L; León C; Escamez MJ; Hausser I; Del Río M; Murillas R; Larcher F
Mol Ther; 2019 May; 27(5):986-998. PubMed ID: 30930113
[TBL] [Abstract][Full Text] [Related]
3. Highly Efficient Ex Vivo Correction of COL7A1 through Ribonucleoprotein-Based CRISPR/Cas9 and Homology-Directed Repair to Treat Recessive Dystrophic Epidermolysis Bullosa.
Berthault C; Gaucher S; Gouin O; Schmitt A; Chen M; Woodley D; Titeux M; Hovnanian A; Izmiryan A
J Invest Dermatol; 2024 Jun; 144(6):1322-1333.e13. PubMed ID: 38043638
[TBL] [Abstract][Full Text] [Related]
4. COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa.
Hainzl S; Peking P; Kocher T; Murauer EM; Larcher F; Del Rio M; Duarte B; Steiner M; Klausegger A; Bauer JW; Reichelt J; Koller U
Mol Ther; 2017 Nov; 25(11):2573-2584. PubMed ID: 28800953
[TBL] [Abstract][Full Text] [Related]
5. Footprint-free gene mutation correction in induced pluripotent stem cell (iPSC) derived from recessive dystrophic epidermolysis bullosa (RDEB) using the CRISPR/Cas9 and piggyBac transposon system.
Itoh M; Kawagoe S; Tamai K; Nakagawa H; Asahina A; Okano HJ
J Dermatol Sci; 2020 Jun; 98(3):163-172. PubMed ID: 32376152
[TBL] [Abstract][Full Text] [Related]
6. Cyclization-enhanced poly(β-amino ester)s vectors for efficient CRISPR gene editing therapy.
Wang X; Li Y; A S; Lyu J; Wang X; He Z; Lara-Sáez I; Li M; Wang W
J Control Release; 2024 Apr; 368():444-452. PubMed ID: 38401849
[TBL] [Abstract][Full Text] [Related]
7. Correction of recessive dystrophic epidermolysis bullosa by homology-directed repair-mediated genome editing.
Bonafont J; Mencía A; Chacón-Solano E; Srifa W; Vaidyanathan S; Romano R; Garcia M; Hervás-Salcedo R; Ugalde L; Duarte B; Porteus MH; Del Rio M; Larcher F; Murillas R
Mol Ther; 2021 Jun; 29(6):2008-2018. PubMed ID: 33609734
[TBL] [Abstract][Full Text] [Related]
8. CRISPR-Cas9-based non-viral gene editing therapy for topical treatment of recessive dystrophic epidermolysis bullosa.
Wang X; Wang X; Li Y; A S; Qiu B; Bushmalyova A; He Z; Wang W; Lara-Sáez I
Mol Ther Methods Clin Dev; 2023 Dec; 31():101134. PubMed ID: 38027067
[TBL] [Abstract][Full Text] [Related]
9. Predictable CRISPR/Cas9-Mediated COL7A1 Reframing for Dystrophic Epidermolysis Bullosa.
Kocher T; March OP; Bischof J; Liemberger B; Hainzl S; Klausegger A; Hoog A; Strunk D; Bauer JW; Koller U
J Invest Dermatol; 2020 Oct; 140(10):1985-1993.e5. PubMed ID: 32142798
[TBL] [Abstract][Full Text] [Related]
10. Efficient Gene Reframing Therapy for Recessive Dystrophic Epidermolysis Bullosa with CRISPR/Cas9.
Takashima S; Shinkuma S; Fujita Y; Nomura T; Ujiie H; Natsuga K; Iwata H; Nakamura H; Vorobyev A; Abe R; Shimizu H
J Invest Dermatol; 2019 Aug; 139(8):1711-1721.e4. PubMed ID: 30831133
[TBL] [Abstract][Full Text] [Related]
11. Development of Minicircle Vectors Encoding COL7A1 Gene with Human Promoters for Non-Viral Gene Therapy for Recessive Dystrophic Epidermolysis Bullosa.
Wang X; Alshehri F; Manzanares D; Li Y; He Z; Qiu B; Zeng M; A S; Lara-Sáez I; Wang W
Int J Mol Sci; 2021 Nov; 22(23):. PubMed ID: 34884578
[TBL] [Abstract][Full Text] [Related]
12. Efficient in vivo gene editing using ribonucleoproteins in skin stem cells of recessive dystrophic epidermolysis bullosa mouse model.
Wu W; Lu Z; Li F; Wang W; Qian N; Duan J; Zhang Y; Wang F; Chen T
Proc Natl Acad Sci U S A; 2017 Feb; 114(7):1660-1665. PubMed ID: 28137859
[TBL] [Abstract][Full Text] [Related]
13. Efficient and Robust Highly Branched Poly(β-amino ester)/Minicircle
Zeng M; Alshehri F; Zhou D; Lara-Sáez I; Wang X; Li X; A S; Xu Q; Zhang J; Wang W
ACS Appl Mater Interfaces; 2019 Aug; 11(34):30661-30672. PubMed ID: 31390173
[TBL] [Abstract][Full Text] [Related]
14. A knot polymer mediated non-viral gene transfection for skin cells.
Cutlar L; Gao Y; Aied A; Greiser U; Murauer EM; Zhou D; Wang W
Biomater Sci; 2016 Jan; 4(1):92-5. PubMed ID: 26369723
[TBL] [Abstract][Full Text] [Related]
15. Targeted Exon Skipping Restores Type VII Collagen Expression and Anchoring Fibril Formation in an In Vivo RDEB Model.
Turczynski S; Titeux M; Tonasso L; Décha A; Ishida-Yamamoto A; Hovnanian A
J Invest Dermatol; 2016 Dec; 136(12):2387-2395. PubMed ID: 27498345
[TBL] [Abstract][Full Text] [Related]
16. Gene editing toward the use of autologous therapies in recessive dystrophic epidermolysis bullosa.
Perdoni C; Osborn MJ; Tolar J
Transl Res; 2016 Feb; 168():50-58. PubMed ID: 26073463
[TBL] [Abstract][Full Text] [Related]
17. Restoration of type VII collagen expression and function in dystrophic epidermolysis bullosa.
Chen M; Kasahara N; Keene DR; Chan L; Hoeffler WK; Finlay D; Barcova M; Cannon PM; Mazurek C; Woodley DT
Nat Genet; 2002 Dec; 32(4):670-5. PubMed ID: 12426566
[TBL] [Abstract][Full Text] [Related]
18. Characterization of mutations of the type VII collagen gene (COL7A1) in recessive dystrophic epidermolysis bullosa mitis (M-RDEB) from three Korean patients.
Ryoo YW; Kim BC; Lee KS
J Dermatol Sci; 2001 Jun; 26(2):125-32. PubMed ID: 11378329
[TBL] [Abstract][Full Text] [Related]
19. Base Editor Correction of COL7A1 in Recessive Dystrophic Epidermolysis Bullosa Patient-Derived Fibroblasts and iPSCs.
Osborn MJ; Newby GA; McElroy AN; Knipping F; Nielsen SC; Riddle MJ; Xia L; Chen W; Eide CR; Webber BR; Wandall HH; Dabelsteen S; Blazar BR; Liu DR; Tolar J
J Invest Dermatol; 2020 Feb; 140(2):338-347.e5. PubMed ID: 31437443
[TBL] [Abstract][Full Text] [Related]
20. Gene-Corrected Fibroblast Therapy for Recessive Dystrophic Epidermolysis Bullosa using a Self-Inactivating COL7A1 Retroviral Vector.
Jacków J; Titeux M; Portier S; Charbonnier S; Ganier C; Gaucher S; Hovnanian A
J Invest Dermatol; 2016 Jul; 136(7):1346-1354. PubMed ID: 26994967
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
