These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

240 related articles for article (PubMed ID: 34462265)

  • 1. Gene therapy for neuromuscular disorders: prospects and ethics.
    Ryan MM
    Arch Dis Child; 2022 May; 107(5):421-426. PubMed ID: 34462265
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Genome Editing of Monogenic Neuromuscular Diseases: A Systematic Review.
    Long C; Amoasii L; Bassel-Duby R; Olson EN
    JAMA Neurol; 2016 Nov; 73(11):1349-1355. PubMed ID: 27668807
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Antisense Oligonucleotide-Based Therapy for Neuromuscular Disease.
    Sardone V; Zhou H; Muntoni F; Ferlini A; Falzarano MS
    Molecules; 2017 Apr; 22(4):. PubMed ID: 28379182
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Special Issue "Genetic Advances in Neuromuscular Disorders: From Gene Identification to Gene Therapy".
    Arechavala-Gomeza V; Gonzalez-Quereda L
    Genes (Basel); 2021 Feb; 12(2):. PubMed ID: 33567614
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Newborn screening of neuromuscular diseases.
    Dangouloff T; Boemer F; Servais L
    Neuromuscul Disord; 2021 Oct; 31(10):1070-1080. PubMed ID: 34620514
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Genetic therapies and respiratory outcomes in patients with neuromuscular disease.
    Chen D; Ni J; Buu M
    Curr Opin Pediatr; 2024 Jun; 36(3):296-303. PubMed ID: 38655811
    [TBL] [Abstract][Full Text] [Related]  

  • 7. [Molecular therapies: present and future in neuromuscular diseases].
    Ziegler A; Walter MC; Schoser BE
    Nervenarzt; 2023 Jun; 94(6):473-487. PubMed ID: 37221259
    [TBL] [Abstract][Full Text] [Related]  

  • 8. The progress of AAV-mediated gene therapy in neuromuscular disorders.
    Aguti S; Malerba A; Zhou H
    Expert Opin Biol Ther; 2018 Jun; 18(6):681-693. PubMed ID: 29781327
    [TBL] [Abstract][Full Text] [Related]  

  • 9. RNA-targeted splice-correction therapy for neuromuscular disease.
    Wood MJ; Gait MJ; Yin H
    Brain; 2010 Apr; 133(Pt 4):957-72. PubMed ID: 20150322
    [TBL] [Abstract][Full Text] [Related]  

  • 10. [Innovative therapeutic approaches for hereditary neuromuscular diseases].
    Kirschner J; Schoser B
    Nervenarzt; 2018 Oct; 89(10):1115-1122. PubMed ID: 30171303
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Overview of gene therapy in spinal muscular atrophy and Duchenne muscular dystrophy.
    Abreu NJ; Waldrop MA
    Pediatr Pulmonol; 2021 Apr; 56(4):710-720. PubMed ID: 32886442
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Gene therapeutic strategies and relevant clinical trials in neuromuscular disorder in China.
    Hu C; Li X
    Gene Ther; 2020 Aug; 27(7-8):321-328. PubMed ID: 32591735
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Restoring Protein Expression in Neuromuscular Conditions: A Review Assessing the Current State of Exon Skipping/Inclusion and Gene Therapies for Duchenne Muscular Dystrophy and Spinal Muscular Atrophy.
    Sheikh O; Yokota T
    BioDrugs; 2021 Jul; 35(4):389-399. PubMed ID: 34097287
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Gene-based therapies for neuromuscular disorders.
    Zanoteli E; França MC; Marques W
    Arq Neuropsiquiatr; 2024 Jun; 82(6):1-10. PubMed ID: 38325390
    [TBL] [Abstract][Full Text] [Related]  

  • 15. New developments in exon skipping and splice modulation therapies for neuromuscular diseases.
    Touznik A; Lee JJ; Yokota T
    Expert Opin Biol Ther; 2014 Jun; 14(6):809-19. PubMed ID: 24620745
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Genome engineering: a new approach to gene therapy for neuromuscular disorders.
    Nelson CE; Robinson-Hamm JN; Gersbach CA
    Nat Rev Neurol; 2017 Nov; 13(11):647-661. PubMed ID: 28960187
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Genetic therapies for inherited neuromuscular disorders.
    Scoto M; Finkel R; Mercuri E; Muntoni F
    Lancet Child Adolesc Health; 2018 Aug; 2(8):600-609. PubMed ID: 30119719
    [TBL] [Abstract][Full Text] [Related]  

  • 18. A Historical and Current Review of Newborn Screening for Neuromuscular Disorders From Around the World: Lessons for the United States.
    Ross LF; Clarke AJ
    Pediatr Neurol; 2017 Dec; 77():12-22. PubMed ID: 29079012
    [TBL] [Abstract][Full Text] [Related]  

  • 19. On the path to evidence-based therapy in neuromuscular disorders.
    Younger DS
    Handb Clin Neurol; 2023; 195():315-358. PubMed ID: 37562877
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Progress in therapeutic antisense applications for neuromuscular disorders.
    Aartsma-Rus A; van Ommen GJ
    Eur J Hum Genet; 2010 Feb; 18(2):146-53. PubMed ID: 19809477
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 12.