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5. Results of a two-year pilot study of clinical outcome measures in collagen VI- and laminin alpha2-related congenital muscular dystrophies. Meilleur KG; Jain MS; Hynan LS; Shieh CY; Kim E; Waite M; McGuire M; Fiorini C; Glanzman AM; Main M; Rose K; Duong T; Bendixen R; Linton MM; Arveson IC; Nichols C; Yang K; Fischbeck KH; Wagner KR; North K; Mankodi A; Grunseich C; Hartnett EJ; Smith M; Donkervoort S; Schindler A; Kokkinis A; Leach M; Foley AR; Collins J; Muntoni F; Rutkowski A; Bönnemann CG Neuromuscul Disord; 2015 Jan; 25(1):43-54. PubMed ID: 25307854 [TBL] [Abstract][Full Text] [Related]
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