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9. A newly identified chromosomal microdeletion of the rapsyn gene causes a congenital myasthenic syndrome. Müller JS; Abicht A; Christen HJ; Stucka R; Schara U; Mortier W; Huebner A; Lochmüller H Neuromuscul Disord; 2004 Nov; 14(11):744-9. PubMed ID: 15482960 [TBL] [Abstract][Full Text] [Related]
10. The longest reported sibling survivors of a severe form of congenital myasthenic syndrome with the ALG14 pathogenic variant. Katata Y; Uneoka S; Saijyo N; Aihara Y; Miyazoe T; Koyamaishi S; Oikawa Y; Ito Y; Abe Y; Numata-Uematsu Y; Takayama J; Kikuchi A; Tamiya G; Uematsu M; Kure S Am J Med Genet A; 2022 Apr; 188(4):1293-1298. PubMed ID: 34971077 [TBL] [Abstract][Full Text] [Related]
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15. Decrement with high frequency repetitive nerve stimulation in a RAPSN congenital myasthenic syndrome. LoRusso SJ; Iyadurai SJ Muscle Nerve; 2018 Mar; 57(3):E106-E108. PubMed ID: 29053879 [No Abstract] [Full Text] [Related]
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