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5. Delivery of AAV2/9-microdystrophin genes incorporating helix 1 of the coiled-coil motif in the C-terminal domain of dystrophin improves muscle pathology and restores the level of α1-syntrophin and α-dystrobrevin in skeletal muscles of mdx mice. Koo T; Malerba A; Athanasopoulos T; Trollet C; Boldrin L; Ferry A; Popplewell L; Foster H; Foster K; Dickson G Hum Gene Ther; 2011 Nov; 22(11):1379-88. PubMed ID: 21453126 [TBL] [Abstract][Full Text] [Related]
6. AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype. Yoshimura M; Sakamoto M; Ikemoto M; Mochizuki Y; Yuasa K; Miyagoe-Suzuki Y; Takeda S Mol Ther; 2004 Nov; 10(5):821-8. PubMed ID: 15509500 [TBL] [Abstract][Full Text] [Related]
7. Engineered DNA plasmid reduces immunity to dystrophin while improving muscle force in a model of gene therapy of Duchenne dystrophy. Ho PP; Lahey LJ; Mourkioti F; Kraft PE; Filareto A; Brandt M; Magnusson KEG; Finn EE; Chamberlain JS; Robinson WH; Blau HM; Steinman L Proc Natl Acad Sci U S A; 2018 Sep; 115(39):E9182-E9191. PubMed ID: 30181272 [TBL] [Abstract][Full Text] [Related]
16. Codon optimization of the microdystrophin gene for Duchene muscular dystrophy gene therapy. Athanasopoulos T; Foster H; Foster K; Dickson G Methods Mol Biol; 2011; 709():21-37. PubMed ID: 21194019 [TBL] [Abstract][Full Text] [Related]
17. C-terminal-truncated microdystrophin recruits dystrobrevin and syntrophin to the dystrophin-associated glycoprotein complex and reduces muscular dystrophy in symptomatic utrophin/dystrophin double-knockout mice. Yue Y; Liu M; Duan D Mol Ther; 2006 Jul; 14(1):79-87. PubMed ID: 16563874 [TBL] [Abstract][Full Text] [Related]
18. Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury. Liu M; Yue Y; Harper SQ; Grange RW; Chamberlain JS; Duan D Mol Ther; 2005 Feb; 11(2):245-56. PubMed ID: 15668136 [TBL] [Abstract][Full Text] [Related]
19. Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD). Athanasopoulos T; Graham IR; Foster H; Dickson G Gene Ther; 2004 Oct; 11 Suppl 1():S109-21. PubMed ID: 15454965 [TBL] [Abstract][Full Text] [Related]
20. Dual AAV therapy ameliorates exercise-induced muscle injury and functional ischemia in murine models of Duchenne muscular dystrophy. Zhang Y; Yue Y; Li L; Hakim CH; Zhang K; Thomas GD; Duan D Hum Mol Genet; 2013 Sep; 22(18):3720-9. PubMed ID: 23681067 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]