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9. Autologous intramuscular transplantation of engineered satellite cells induces exosome-mediated systemic expression of Fukutin-related protein and rescues disease phenotype in a murine model of limb-girdle muscular dystrophy type 2I. Frattini P; Villa C; De Santis F; Meregalli M; Belicchi M; Erratico S; Bella P; Raimondi MT; Lu Q; Torrente Y Hum Mol Genet; 2017 Oct; 26(19):3682-3698. PubMed ID: 28666318 [TBL] [Abstract][Full Text] [Related]
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