200 related articles for article (PubMed ID: 34931542)
1. Biodistribution and Tolerability of AAV-PHP.B-CBh-
Palazzi X; Pardo ID; Sirivelu MP; Newman L; Kumpf SW; Qian J; Franks T; Lopes S; Liu J; Monarski L; Casinghino S; Ritenour C; Ritenour H; Dubois C; Olson J; Graves J; Alexander KE; Coskran T; Lanz TA; Brady J; McCarty D; Suryanarayan S; Whiteley LO
Hum Gene Ther; 2022 Feb; 33(3-4):175-187. PubMed ID: 34931542
[TBL] [Abstract][Full Text] [Related]
2. Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN.
Hinderer C; Katz N; Buza EL; Dyer C; Goode T; Bell P; Richman LK; Wilson JM
Hum Gene Ther; 2018 Mar; 29(3):285-298. PubMed ID: 29378426
[TBL] [Abstract][Full Text] [Related]
3. Intravenous administration of the adeno-associated virus-PHP.B capsid fails to upregulate transduction efficiency in the marmoset brain.
Matsuzaki Y; Konno A; Mochizuki R; Shinohara Y; Nitta K; Okada Y; Hirai H
Neurosci Lett; 2018 Feb; 665():182-188. PubMed ID: 29175632
[TBL] [Abstract][Full Text] [Related]
4. Circulating neurofilament light chain as a promising biomarker of AAV-induced dorsal root ganglia toxicity in nonclinical toxicology species.
Fader KA; Pardo ID; Kovi RC; Somps CJ; Wang HH; Vaidya VS; Ramaiah SK; Sirivelu MP
Mol Ther Methods Clin Dev; 2022 Jun; 25():264-277. PubMed ID: 35505662
[TBL] [Abstract][Full Text] [Related]
5. AAV-PHP.B Administration Results in a Differential Pattern of CNS Biodistribution in Non-human Primates Compared with Mice.
Liguore WA; Domire JS; Button D; Wang Y; Dufour BD; Srinivasan S; McBride JL
Mol Ther; 2019 Nov; 27(11):2018-2037. PubMed ID: 31420242
[TBL] [Abstract][Full Text] [Related]
6. Liver injury in cynomolgus monkeys following intravenous and intrathecal scAAV9 gene therapy delivery.
Hudry E; Aihara F; Meseck E; Mansfield K; McElroy C; Chand D; Tukov FF; Penraat K
Mol Ther; 2023 Oct; 31(10):2999-3014. PubMed ID: 37515322
[TBL] [Abstract][Full Text] [Related]
7. Adeno-Associated Virus-Induced Dorsal Root Ganglion Pathology.
Hordeaux J; Buza EL; Dyer C; Goode T; Mitchell TW; Richman L; Denton N; Hinderer C; Katz N; Schmid R; Miller R; Choudhury GR; Horiuchi M; Nambiar K; Yan H; Li M; Wilson JM
Hum Gene Ther; 2020 Aug; 31(15-16):808-818. PubMed ID: 32845779
[TBL] [Abstract][Full Text] [Related]
8. scAAVengr, a transcriptome-based pipeline for quantitative ranking of engineered AAVs with single-cell resolution.
Öztürk BE; Johnson ME; Kleyman M; Turunç S; He J; Jabalameli S; Xi Z; Visel M; Dufour VL; Iwabe S; Pompeo Marinho LFL; Aguirre GD; Sahel JA; Schaffer DV; Pfenning AR; Flannery JG; Beltran WA; Stauffer WR; Byrne LC
Elife; 2021 Oct; 10():. PubMed ID: 34664552
[TBL] [Abstract][Full Text] [Related]
9. Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys.
Hordeaux J; Hinderer C; Buza EL; Louboutin JP; Jahan T; Bell P; Chichester JA; Tarantal AF; Wilson JM
Hum Gene Ther; 2019 Aug; 30(8):957-966. PubMed ID: 31017018
[TBL] [Abstract][Full Text] [Related]
10. Self-complementary AAV virus (scAAV) safe and long-term gene transfer in the trabecular meshwork of living rats and monkeys.
Buie LK; Rasmussen CA; Porterfield EC; Ramgolam VS; Choi VW; Markovic-Plese S; Samulski RJ; Kaufman PL; Borrás T
Invest Ophthalmol Vis Sci; 2010 Jan; 51(1):236-48. PubMed ID: 19684004
[TBL] [Abstract][Full Text] [Related]
11. Intrathecal sc-AAV9-CB-GFP: Systemic Distribution Predominates Following Single-Dose Administration in Cynomolgus Macaques.
Meseck EK; Guibinga G; Wang S; McElroy C; Hudry E; Mansfield K
Toxicol Pathol; 2022 Jun; 50(4):415-431. PubMed ID: 35658751
[TBL] [Abstract][Full Text] [Related]
12. Global CNS gene delivery and evasion of anti-AAV-neutralizing antibodies by intrathecal AAV administration in non-human primates.
Gray SJ; Nagabhushan Kalburgi S; McCown TJ; Jude Samulski R
Gene Ther; 2013 Apr; 20(4):450-9. PubMed ID: 23303281
[TBL] [Abstract][Full Text] [Related]
13. The AAV9 Variant Capsid AAV-F Mediates Widespread Transgene Expression in Nonhuman Primate Spinal Cord After Intrathecal Administration.
Beharry A; Gong Y; Kim JC; Hanlon KS; Nammour J; Hieber K; Eichler F; Cheng M; Stemmer-Rachamimov A; Stankovic KM; Welling DB; Ng C; Maguire CA
Hum Gene Ther; 2022 Jan; 33(1-2):61-75. PubMed ID: 34128391
[TBL] [Abstract][Full Text] [Related]
14. Preclinical Potency and Biodistribution Studies of an AAV 5 Vector Expressing Human Interferon-β (ART-I02) for Local Treatment of Patients with Rheumatoid Arthritis.
Aalbers CJ; Bevaart L; Loiler S; de Cortie K; Wright JF; Mingozzi F; Tak PP; Vervoordeldonk MJ
PLoS One; 2015; 10(6):e0130612. PubMed ID: 26107769
[TBL] [Abstract][Full Text] [Related]
15. More expansive gene transfer to the rat CNS: AAV PHP.EB vector dose-response and comparison to AAV PHP.B.
Dayton RD; Grames MS; Klein RL
Gene Ther; 2018 Aug; 25(5):392-400. PubMed ID: 30013186
[TBL] [Abstract][Full Text] [Related]
16. Inverse zonation of hepatocyte transduction with AAV vectors between mice and non-human primates.
Bell P; Wang L; Gao G; Haskins ME; Tarantal AF; McCarter RJ; Zhu Y; Yu H; Wilson JM
Mol Genet Metab; 2011 Nov; 104(3):395-403. PubMed ID: 21778099
[TBL] [Abstract][Full Text] [Related]
17. Safety and Biodistribution Evaluation in Cynomolgus Macaques of rAAV2tYF-CB-hRS1, a Recombinant Adeno-Associated Virus Vector Expressing Retinoschisin.
Ye GJ; Budzynski E; Sonnentag P; Miller PE; Sharma AK; Ver Hoeve JN; Howard K; Knop DR; Neuringer M; McGill T; Stoddard J; Chulay JD
Hum Gene Ther Clin Dev; 2015 Sep; 26(3):165-76. PubMed ID: 26390090
[TBL] [Abstract][Full Text] [Related]
18. Direct Intracranial Injection of AAVrh8 Encoding Monkey β-N-Acetylhexosaminidase Causes Neurotoxicity in the Primate Brain.
Golebiowski D; van der Bom IMJ; Kwon CS; Miller AD; Petrosky K; Bradbury AM; Maitland S; Kühn AL; Bishop N; Curran E; Silva N; GuhaSarkar D; Westmoreland SV; Martin DR; Gounis MJ; Asaad WF; Sena-Esteves M
Hum Gene Ther; 2017 Jun; 28(6):510-522. PubMed ID: 28132521
[TBL] [Abstract][Full Text] [Related]
19. Preclinical testing of AAV9-PHP.B for transgene expression in the non-human primate cochlea.
Ivanchenko MV; Hanlon KS; Devine MK; Tenneson K; Emond F; Lafond JF; Kenna MA; Corey DP; Maguire CA
Hear Res; 2020 Sep; 394():107930. PubMed ID: 32145977
[TBL] [Abstract][Full Text] [Related]
20. Biodistribution of a low dose of intravenously administered AAV-2, 10, and 11 vectors to cynomolgus monkeys.
Mori S; Takeuchi T; Enomoto Y; Kondo K; Sato K; Ono F; Iwata N; Sata T; Kanda T
Jpn J Infect Dis; 2006 Oct; 59(5):285-93. PubMed ID: 17060693
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
