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2. Severe Toxicity in Nonhuman Primates and Piglets Following High-Dose Intravenous Administration of an Adeno-Associated Virus Vector Expressing Human SMN. Hinderer C; Katz N; Buza EL; Dyer C; Goode T; Bell P; Richman LK; Wilson JM Hum Gene Ther; 2018 Mar; 29(3):285-298. PubMed ID: 29378426 [TBL] [Abstract][Full Text] [Related]
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