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6. Triple trans-splicing adeno-associated virus vectors capable of transferring the coding sequence for full-length dystrophin protein into dystrophic mice. Koo T; Popplewell L; Athanasopoulos T; Dickson G Hum Gene Ther; 2014 Feb; 25(2):98-108. PubMed ID: 24191945 [TBL] [Abstract][Full Text] [Related]
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12. Mdx mice inducibly expressing dystrophin provide insights into the potential of gene therapy for duchenne muscular dystrophy. Ahmad A; Brinson M; Hodges BL; Chamberlain JS; Amalfitano A Hum Mol Genet; 2000 Oct; 9(17):2507-15. PubMed ID: 11030755 [TBL] [Abstract][Full Text] [Related]
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16. Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD). Athanasopoulos T; Graham IR; Foster H; Dickson G Gene Ther; 2004 Oct; 11 Suppl 1():S109-21. PubMed ID: 15454965 [TBL] [Abstract][Full Text] [Related]
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20. [Gene therapy for muscular dystrophy]. Takeda S No To Hattatsu; 2004 Mar; 36(2):117-23. PubMed ID: 15031985 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]