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3. Risdiplam distributes and increases SMN protein in both the central nervous system and peripheral organs. Poirier A; Weetall M; Heinig K; Bucheli F; Schoenlein K; Alsenz J; Bassett S; Ullah M; Senn C; Ratni H; Naryshkin N; Paushkin S; Mueller L Pharmacol Res Perspect; 2018 Dec; 6(6):e00447. PubMed ID: 30519476 [TBL] [Abstract][Full Text] [Related]
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