These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

170 related articles for article (PubMed ID: 35402069)

  • 1. Long-term maintenance of dystrophin expression and resistance to injury of skeletal muscle in gene edited DMD mice.
    Karri DR; Zhang Y; Chemello F; Min YL; Huang J; Kim J; Mammen PPA; Xu L; Liu N; Bassel-Duby R; Olson EN
    Mol Ther Nucleic Acids; 2022 Jun; 28():154-167. PubMed ID: 35402069
    [TBL] [Abstract][Full Text] [Related]  

  • 2. In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers.
    Chen M; Shi H; Gou S; Wang X; Li L; Jin Q; Wu H; Zhang H; Li Y; Wang L; Li H; Lin J; Guo W; Jiang Z; Yang X; Xu A; Zhu Y; Zhang C; Lai L; Li X
    Genome Med; 2021 Apr; 13(1):57. PubMed ID: 33845891
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Dystrophin Gene-Editing Stability Is Dependent on Dystrophin Levels in Skeletal but Not Cardiac Muscles.
    Bengtsson NE; Tasfaout H; Hauschka SD; Chamberlain JS
    Mol Ther; 2021 Mar; 29(3):1070-1085. PubMed ID: 33160075
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Restoration of dystrophin expression and correction of Duchenne muscular dystrophy by genome editing.
    Aslesh T; Erkut E; Yokota T
    Expert Opin Biol Ther; 2021 Aug; 21(8):1049-1061. PubMed ID: 33401973
    [No Abstract]   [Full Text] [Related]  

  • 5. CRISPR-Cas9 Correction of Duchenne Muscular Dystrophy in Mice by a Self-Complementary AAV Delivery System.
    Zhang Y; Bassel-Duby R; Olson EN
    Methods Mol Biol; 2023; 2587():411-425. PubMed ID: 36401041
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Molecular correction of Duchenne muscular dystrophy by splice modulation and gene editing.
    Hanson B; Wood MJA; Roberts TC
    RNA Biol; 2021 Jul; 18(7):1048-1062. PubMed ID: 33472516
    [TBL] [Abstract][Full Text] [Related]  

  • 7. A consolidated AAV system for single-cut CRISPR correction of a common Duchenne muscular dystrophy mutation.
    Zhang Y; Nishiyama T; Li H; Huang J; Atmanli A; Sanchez-Ortiz E; Wang Z; Mireault AA; Mammen PPA; Bassel-Duby R; Olson EN
    Mol Ther Methods Clin Dev; 2021 Sep; 22():122-132. PubMed ID: 34485599
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Gene editing of Duchenne muscular dystrophy using biomineralization-based spCas9 variant nanoparticles.
    Li S; Du M; Deng J; Deng G; Li J; Song Z; Han H
    Acta Biomater; 2022 Dec; 154():597-607. PubMed ID: 36243370
    [TBL] [Abstract][Full Text] [Related]  

  • 9. The AAV-mediated and RNA-guided CRISPR/Cas9 system for gene therapy of DMD and BMD.
    Wang JZ; Wu P; Shi ZM; Xu YL; Liu ZJ
    Brain Dev; 2017 Aug; 39(7):547-556. PubMed ID: 28390761
    [TBL] [Abstract][Full Text] [Related]  

  • 10. A humanized knockin mouse model of Duchenne muscular dystrophy and its correction by CRISPR-Cas9 therapeutic gene editing.
    Zhang Y; Li H; Nishiyama T; McAnally JR; Sanchez-Ortiz E; Huang J; Mammen PPA; Bassel-Duby R; Olson EN
    Mol Ther Nucleic Acids; 2022 Sep; 29():525-537. PubMed ID: 36035749
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Single-swap editing for the correction of common Duchenne muscular dystrophy mutations.
    Chai AC; Chemello F; Li H; Nishiyama T; Chen K; Zhang Y; Sánchez-Ortiz E; Alomar A; Xu L; Liu N; Bassel-Duby R; Olson EN
    Mol Ther Nucleic Acids; 2023 Jun; 32():522-535. PubMed ID: 37215149
    [TBL] [Abstract][Full Text] [Related]  

  • 12. CRISPR-Editing Therapy for Duchenne Muscular Dystrophy.
    Chemello F; Olson EN; Bassel-Duby R
    Hum Gene Ther; 2023 May; 34(9-10):379-387. PubMed ID: 37060194
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Applications of CRISPR/Cas9 for the Treatment of Duchenne Muscular Dystrophy.
    Lim KRQ; Yoon C; Yokota T
    J Pers Med; 2018 Nov; 8(4):. PubMed ID: 30477208
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Prevention of early-onset cardiomyopathy in
    Rok M; Wong TWY; Maino E; Ahmed A; Yang G; Hyatt E; Lindsay K; Fatehi S; Marks R; Delgado-Olguín P; Ivakine EA; Cohn RD
    Mol Ther Methods Clin Dev; 2023 Sep; 30():246-258. PubMed ID: 37545481
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA.
    Long C; McAnally JR; Shelton JM; Mireault AA; Bassel-Duby R; Olson EN
    Science; 2014 Sep; 345(6201):1184-1188. PubMed ID: 25123483
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Functional Rescue of Dystrophin Deficiency in Mice Caused by Frameshift Mutations Using Campylobacter jejuni Cas9.
    Koo T; Lu-Nguyen NB; Malerba A; Kim E; Kim D; Cappellari O; Cho HY; Dickson G; Popplewell L; Kim JS
    Mol Ther; 2018 Jun; 26(6):1529-1538. PubMed ID: 29730196
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Gene modification strategies using AO-mediated exon skipping and CRISPR/Cas9 as potential therapies for Duchenne muscular dystrophy patients.
    Solberg MH; Shariatzadeh M; Wilson SL
    Eng Biol; 2020 Dec; 4(3):37-42. PubMed ID: 36968157
    [TBL] [Abstract][Full Text] [Related]  

  • 18. CRISPR-Cas9 correction in the DMD mouse model is accompanied by upregulation of Dp71f protein.
    Egorova TV; Polikarpova AV; Vassilieva SG; Dzhenkova MA; Savchenko IM; Velyaev OA; Shmidt AA; Soldatov VO; Pokrovskii MV; Deykin AV; Bardina MV
    Mol Ther Methods Clin Dev; 2023 Sep; 30():161-180. PubMed ID: 37457303
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Dystrophin gene editing by CRISPR/Cas9 system in human skeletal muscle cell line (HSkMC).
    Dara M; Razban V; Mazloomrezaei M; Ranjbar M; Nourigorji M; Dianatpour M
    Iran J Basic Med Sci; 2021 Aug; 24(8):1153-1158. PubMed ID: 34804433
    [TBL] [Abstract][Full Text] [Related]  

  • 20. In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.
    Nelson CE; Hakim CH; Ousterout DG; Thakore PI; Moreb EA; Castellanos Rivera RM; Madhavan S; Pan X; Ran FA; Yan WX; Asokan A; Zhang F; Duan D; Gersbach CA
    Science; 2016 Jan; 351(6271):403-7. PubMed ID: 26721684
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 9.