BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

181 related articles for article (PubMed ID: 35889565)

  • 1. Galactomannan-Decorated Lipidic Nanocarrier for Gene Supplementation Therapy in Fabry Disease.
    Rodríguez-Castejón J; Gómez-Aguado I; Beraza-Millor M; Solinís MÁ; Del Pozo-Rodríguez A; Rodríguez-Gascón A
    Nanomaterials (Basel); 2022 Jul; 12(14):. PubMed ID: 35889565
    [TBL] [Abstract][Full Text] [Related]  

  • 2. α-Galactosidase A Augmentation by Non-Viral Gene Therapy: Evaluation in Fabry Disease Mice.
    Rodríguez-Castejón J; Alarcia-Lacalle A; Gómez-Aguado I; Vicente-Pascual M; Solinís Aspiazu MÁ; Del Pozo-Rodríguez A; Rodríguez-Gascón A
    Pharmaceutics; 2021 May; 13(6):. PubMed ID: 34064206
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Multicomponent nanoparticles as nonviral vectors for the treatment of Fabry disease by gene therapy.
    Ruiz de Garibay AP; Delgado D; Del Pozo-Rodríguez A; Solinís MÁ; Gascón AR
    Drug Des Devel Ther; 2012; 6():303-10. PubMed ID: 23118528
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Targeting strategies with lipid vectors for nucleic acid supplementation therapy in Fabry disease: a systematic review.
    Rodríguez-Castejón J; Beraza-Millor M; Solinís MÁ; Rodríguez-Gascón A; Del Pozo-Rodríguez A
    Drug Deliv Transl Res; 2024 Apr; ():. PubMed ID: 38587758
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Solid Lipid Nanoparticles as Non-Viral Vectors for Gene Transfection in a Cell Model of Fabry Disease.
    Ruiz de Garibay AP; Solinís MA; del Pozo-Rodríguez A; Apaolaza PS; Shen JS; Rodríguez-Gascón A
    J Biomed Nanotechnol; 2015 Mar; 11(3):500-11. PubMed ID: 26307832
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Dextran-protamine-solid lipid nanoparticles as a non-viral vector for gene therapy: in vitro characterization and in vivo transfection after intravenous administration to mice.
    Delgado D; Gascón AR; Del Pozo-Rodríguez A; Echevarría E; Ruiz de Garibay AP; Rodríguez JM; Solinís MÁ
    Int J Pharm; 2012 Apr; 425(1-2):35-43. PubMed ID: 22226874
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Partial correction of the alpha-galactosidase A deficiency and reduction of glycolipid storage in Fabry mice using synthetic vectors.
    Przybylska M; Wu IH; Zhao H; Ziegler RJ; Tousignant JD; Desnick RJ; Scheule RK; Cheng SH; Yew NS
    J Gene Med; 2004 Jan; 6(1):85-92. PubMed ID: 14716680
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Naked plasmid DNA-based alpha-galactosidase A gene transfer partially reduces systemic accumulation of globotriaosylceramide in Fabry mice.
    Nakamura G; Maruyama H; Ishii S; Shimotori M; Kameda S; Kono T; Miyazaki J; Kulkarni AB; Gejyo F
    Mol Biotechnol; 2008 Feb; 38(2):109-19. PubMed ID: 18219591
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Characterization of Fabry mice treated with recombinant adeno-associated virus 2/8-mediated gene transfer.
    Choi JO; Lee MH; Park HY; Jung SC
    J Biomed Sci; 2010 Apr; 17(1):26. PubMed ID: 20398385
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Adeno-associated viral vector-mediated gene transfer results in long-term enzymatic and functional correction in multiple organs of Fabry mice.
    Jung SC; Han IP; Limaye A; Xu R; Gelderman MP; Zerfas P; Tirumalai K; Murray GJ; During MJ; Brady RO; Qasba P
    Proc Natl Acad Sci U S A; 2001 Feb; 98(5):2676-81. PubMed ID: 11226298
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Long-term inhibition of glycosphingolipid accumulation in Fabry model mice by a single systemic injection of AAV1 vector in the neonatal period.
    Ogawa K; Hirai Y; Ishizaki M; Takahashi H; Hanawa H; Fukunaga Y; Shimada T
    Mol Genet Metab; 2009 Mar; 96(3):91-6. PubMed ID: 19091614
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Correction of the nonlinear dose response improves the viability of adenoviral vectors for gene therapy of Fabry disease.
    Ziegler RJ; Li C; Cherry M; Zhu Y; Hempel D; van Rooijen N; Ioannou YA; Desnick RJ; Goldberg MA; Yew NS; Cheng SH
    Hum Gene Ther; 2002 May; 13(8):935-45. PubMed ID: 12031126
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Design flexibility influencing the in vitro behavior of cationic SLN as a nonviral gene vector.
    Vighi E; Montanari M; Hanuskova M; Iannuccelli V; Coppi G; Leo E
    Int J Pharm; 2013 Jan; 440(2):161-9. PubMed ID: 22982257
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Sequencing and characterization of the porcine α-galactosidase A gene: towards the generation of a porcine model for Fabry disease.
    Yoshimitsu M; Higuchi K; Fan X; Takao S; Medin JA; Tei C; Takenaka T
    Mol Biol Rep; 2011 Jun; 38(5):3145-52. PubMed ID: 20131008
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Systemic mRNA Therapy for the Treatment of Fabry Disease: Preclinical Studies in Wild-Type Mice, Fabry Mouse Model, and Wild-Type Non-human Primates.
    Zhu X; Yin L; Theisen M; Zhuo J; Siddiqui S; Levy B; Presnyak V; Frassetto A; Milton J; Salerno T; Benenato KE; Milano J; Lynn A; Sabnis S; Burke K; Besin G; Lukacs CM; Guey LT; Finn PF; Martini PGV
    Am J Hum Genet; 2019 Apr; 104(4):625-637. PubMed ID: 30879639
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Adenovirus-transduced lung as a portal for delivering alpha-galactosidase A into systemic circulation for Fabry disease.
    Li C; Ziegler RJ; Cherry M; Lukason M; Desnick RJ; Yew NS; Cheng SH
    Mol Ther; 2002 Jun; 5(6):745-54. PubMed ID: 12027559
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Correction of enzymatic and lysosomal storage defects in Fabry mice by adenovirus-mediated gene transfer.
    Ziegler RJ; Yew NS; Li C; Cherry M; Berthelette P; Romanczuk H; Ioannou YA; Zeidner KM; Desnick RJ; Cheng SH
    Hum Gene Ther; 1999 Jul; 10(10):1667-82. PubMed ID: 10428212
    [TBL] [Abstract][Full Text] [Related]  

  • 18. pDNA condensation capacity and in vitro gene delivery properties of cationic solid lipid nanoparticles.
    Vighi E; Ruozi B; Montanari M; Battini R; Leo E
    Int J Pharm; 2010 Apr; 389(1-2):254-61. PubMed ID: 20100555
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Gene therapy for Fabry disease.
    Siatskas C; Medin JA
    J Inherit Metab Dis; 2001; 24 Suppl 2():25-41; discussion 11-2. PubMed ID: 11758676
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Long-term systemic therapy of Fabry disease in a knockout mouse by adeno-associated virus-mediated muscle-directed gene transfer.
    Takahashi H; Hirai Y; Migita M; Seino Y; Fukuda Y; Sakuraba H; Kase R; Kobayashi T; Hashimoto Y; Shimada T
    Proc Natl Acad Sci U S A; 2002 Oct; 99(21):13777-82. PubMed ID: 12370426
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 10.