These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
3. A valid mouse model of AGRIN-associated congenital myasthenic syndrome. Bogdanik LP; Burgess RW Hum Mol Genet; 2011 Dec; 20(23):4617-33. PubMed ID: 21890498 [TBL] [Abstract][Full Text] [Related]
4. Novel SEA and LG2 Agrin mutations causing congenital Myasthenic syndrome. Xi J; Yan C; Liu WW; Qiao K; Lin J; Tian X; Wu H; Lu J; Wong LJ; Beeson D; Zhao C Orphanet J Rare Dis; 2017 Dec; 12(1):182. PubMed ID: 29258548 [TBL] [Abstract][Full Text] [Related]
5. Congenital myasthenic syndrome-associated agrin variants affect clustering of acetylcholine receptors in a domain-specific manner. Ohkawara B; Shen X; Selcen D; Nazim M; Bril V; Tarnopolsky MA; Brady L; Fukami S; Amato AA; Yis U; Ohno K; Engel AG JCI Insight; 2020 Apr; 5(7):. PubMed ID: 32271162 [TBL] [Abstract][Full Text] [Related]
6. Agrin mutations lead to a congenital myasthenic syndrome with distal muscle weakness and atrophy. Nicole S; Chaouch A; Torbergsen T; Bauché S; de Bruyckere E; Fontenille MJ; Horn MA; van Ghelue M; Løseth S; Issop Y; Cox D; Müller JS; Evangelista T; Stålberg E; Ioos C; Barois A; Brochier G; Sternberg D; Fournier E; Hantaï D; Abicht A; Dusl M; Laval SH; Griffin H; Eymard B; Lochmüller H Brain; 2014 Sep; 137(Pt 9):2429-43. PubMed ID: 24951643 [TBL] [Abstract][Full Text] [Related]
7. MYO9A deficiency in motor neurons is associated with reduced neuromuscular agrin secretion. O'Connor E; Phan V; Cordts I; Cairns G; Hettwer S; Cox D; Lochmüller H; Roos A Hum Mol Genet; 2018 Apr; 27(8):1434-1446. PubMed ID: 29462312 [TBL] [Abstract][Full Text] [Related]
8. A Novel Missense Variant in the AGRN Gene; Congenital Myasthenic Syndrome Presenting With Head Drop. Karakaya M; Ceyhan-Birsoy O; Beggs AH; Topaloglu H J Clin Neuromuscul Dis; 2017 Mar; 18(3):147-151. PubMed ID: 28221305 [TBL] [Abstract][Full Text] [Related]
9. Identification of an agrin mutation that causes congenital myasthenia and affects synapse function. Huzé C; Bauché S; Richard P; Chevessier F; Goillot E; Gaudon K; Ben Ammar A; Chaboud A; Grosjean I; Lecuyer HA; Bernard V; Rouche A; Alexandri N; Kuntzer T; Fardeau M; Fournier E; Brancaccio A; Rüegg MA; Koenig J; Eymard B; Schaeffer L; Hantaï D Am J Hum Genet; 2009 Aug; 85(2):155-67. PubMed ID: 19631309 [TBL] [Abstract][Full Text] [Related]
10. New mutation in the β1 propeller domain of LRP4 responsible for congenital myasthenic syndrome associated with Cenani-Lenz syndrome. Masingue M; Cattaneo O; Wolff N; Buon C; Sternberg D; Euchparmakian M; Boex M; Behin A; Mamchaouhi K; Maisonobe T; Nougues MC; Isapof A; Fontaine B; Messéant J; Eymard B; Strochlic L; Bauché S Sci Rep; 2023 Aug; 13(1):14054. PubMed ID: 37640745 [TBL] [Abstract][Full Text] [Related]
11. Synaptic basal lamina-associated congenital myasthenic syndromes. Maselli RA; Arredondo J; Ferns MJ; Wollmann RL Ann N Y Acad Sci; 2012 Dec; 1275():36-48. PubMed ID: 23278576 [TBL] [Abstract][Full Text] [Related]
12. LRP4 third β-propeller domain mutations cause novel congenital myasthenia by compromising agrin-mediated MuSK signaling in a position-specific manner. Ohkawara B; Cabrera-Serrano M; Nakata T; Milone M; Asai N; Ito K; Ito M; Masuda A; Ito Y; Engel AG; Ohno K Hum Mol Genet; 2014 Apr; 23(7):1856-68. PubMed ID: 24234652 [TBL] [Abstract][Full Text] [Related]
14. Beta-2 Adrenergic Receptor Agonists Enhance AChR Clustering in C2C12 Myotubes: Implications for Therapy of Myasthenic Disorders. Clausen L; Cossins J; Beeson D J Neuromuscul Dis; 2018; 5(2):231-240. PubMed ID: 29865088 [TBL] [Abstract][Full Text] [Related]
15. Motoneuron-specific loss of VAChT mimics neuromuscular defects seen in congenital myasthenic syndrome. Joviano-Santos JV; Kljakic O; Magalhães-Gomes MPS; Valadão PAC; de Oliveira LR; Prado MAM; Prado VF; Guatimosim C FEBS J; 2021 Sep; 288(18):5331-5349. PubMed ID: 33730374 [TBL] [Abstract][Full Text] [Related]
16. Current status of the congenital myasthenic syndromes. Engel AG Neuromuscul Disord; 2012 Feb; 22(2):99-111. PubMed ID: 22104196 [TBL] [Abstract][Full Text] [Related]
17. CHRND mutation causes a congenital myasthenic syndrome by impairing co-clustering of the acetylcholine receptor with rapsyn. Müller JS; Baumeister SK; Schara U; Cossins J; Krause S; von der Hagen M; Huebner A; Webster R; Beeson D; Lochmüller H; Abicht A Brain; 2006 Oct; 129(Pt 10):2784-93. PubMed ID: 16916845 [TBL] [Abstract][Full Text] [Related]