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6. Leber congenital amaurosis/early-onset severe retinal dystrophy: current management and clinical trials. Daich Varela M; Cabral de Guimaraes TA; Georgiou M; Michaelides M Br J Ophthalmol; 2022 Apr; 106(4):445-451. PubMed ID: 33712480 [TBL] [Abstract][Full Text] [Related]
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8. Gene therapy for inherited retinal diseases: progress and possibilities. Hu ML; Edwards TL; O'Hare F; Hickey DG; Wang JH; Liu Z; Ayton LN Clin Exp Optom; 2021 May; 104(4):444-454. PubMed ID: 33689657 [TBL] [Abstract][Full Text] [Related]
9. Inherited retinal diseases: Therapeutics, clinical trials and end points-A review. Georgiou M; Fujinami K; Michaelides M Clin Exp Ophthalmol; 2021 Apr; 49(3):270-288. PubMed ID: 33686777 [TBL] [Abstract][Full Text] [Related]
10. Advances in the molecular understanding of canine retinal diseases. Petersen-Jones S J Small Anim Pract; 2005 Aug; 46(8):371-80. PubMed ID: 16119056 [TBL] [Abstract][Full Text] [Related]
11. Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement. Cideciyan AV; Jacobson SG; Beltran WA; Sumaroka A; Swider M; Iwabe S; Roman AJ; Olivares MB; Schwartz SB; Komáromy AM; Hauswirth WW; Aguirre GD Proc Natl Acad Sci U S A; 2013 Feb; 110(6):E517-25. PubMed ID: 23341635 [TBL] [Abstract][Full Text] [Related]
12. Leber's Congenital Amaurosis: Current Concepts of Genotype-Phenotype Correlations. Huang CH; Yang CM; Yang CH; Hou YC; Chen TC Genes (Basel); 2021 Aug; 12(8):. PubMed ID: 34440435 [TBL] [Abstract][Full Text] [Related]
13. Leber congenital amaurosis: Current genetic basis, scope for genetic testing and personalized medicine. Kondkar AA; Abu-Amero KK Exp Eye Res; 2019 Dec; 189():107834. PubMed ID: 31639339 [TBL] [Abstract][Full Text] [Related]
14. Leber's Congenital Amaurosis and Gene Therapy. Takkar B; Bansal P; Venkatesh P Indian J Pediatr; 2018 Mar; 85(3):237-242. PubMed ID: 28685406 [TBL] [Abstract][Full Text] [Related]
15. Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients. Colella P; Auricchio A Hum Gene Ther; 2012 Aug; 23(8):796-807. PubMed ID: 22734691 [TBL] [Abstract][Full Text] [Related]
16. Leber congenital amaurosis/early-onset severe retinal dystrophy: clinical features, molecular genetics and therapeutic interventions. Kumaran N; Moore AT; Weleber RG; Michaelides M Br J Ophthalmol; 2017 Sep; 101(9):1147-1154. PubMed ID: 28689169 [TBL] [Abstract][Full Text] [Related]
17. Gene therapy for the eye focus on mutation-independent approaches. Dalkara D; Duebel J; Sahel JA Curr Opin Neurol; 2015 Feb; 28(1):51-60. PubMed ID: 25545056 [TBL] [Abstract][Full Text] [Related]
18. The Italian Job: An Interview with Federico Mingozzi. Davies K Hum Gene Ther; 2020 Oct; 31(19-20):1027-1030. PubMed ID: 33074024 [No Abstract] [Full Text] [Related]
19. Available Evidence on Leber Congenital Amaurosis and Gene Therapy. Alkharashi M; Fulton AB Semin Ophthalmol; 2017; 32(1):14-21. PubMed ID: 27686653 [TBL] [Abstract][Full Text] [Related]
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