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23. Gene therapy for Leber congenital amaurosis: advances and future directions. Hufnagel RB; Ahmed ZM; Corrêa ZM; Sisk RA Graefes Arch Clin Exp Ophthalmol; 2012 Aug; 250(8):1117-28. PubMed ID: 22644094 [TBL] [Abstract][Full Text] [Related]
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31. Gene therapy using self-complementary Y733F capsid mutant AAV2/8 restores vision in a model of early onset Leber congenital amaurosis. Ku CA; Chiodo VA; Boye SL; Goldberg AF; Li T; Hauswirth WW; Ramamurthy V Hum Mol Genet; 2011 Dec; 20(23):4569-81. PubMed ID: 21880665 [TBL] [Abstract][Full Text] [Related]
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33. Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration. Simonelli F; Maguire AM; Testa F; Pierce EA; Mingozzi F; Bennicelli JL; Rossi S; Marshall K; Banfi S; Surace EM; Sun J; Redmond TM; Zhu X; Shindler KS; Ying GS; Ziviello C; Acerra C; Wright JF; McDonnell JW; High KA; Bennett J; Auricchio A Mol Ther; 2010 Mar; 18(3):643-50. PubMed ID: 19953081 [TBL] [Abstract][Full Text] [Related]
34. AAV-mediated gene therapy for the treatment of retinal diseases. Rolling F Curr Gene Ther; 2010 Oct; 10(5):318. PubMed ID: 20874705 [No Abstract] [Full Text] [Related]
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