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4. Efficacy and safety of maralixibat treatment in patients with Alagille syndrome and cholestatic pruritus (ICONIC): a randomised phase 2 study. Gonzales E; Hardikar W; Stormon M; Baker A; Hierro L; Gliwicz D; Lacaille F; Lachaux A; Sturm E; Setchell KDR; Kennedy C; Dorenbaum A; Steinmetz J; Desai NK; Wardle AJ; Garner W; Vig P; Jaecklin T; Sokal EM; Jacquemin E Lancet; 2021 Oct; 398(10311):1581-1592. PubMed ID: 34755627 [TBL] [Abstract][Full Text] [Related]
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14. Clinical outcomes of surgical management for rare types of progressive familial intrahepatic cholestasis: a case series. Masahata K; Ueno T; Bessho K; Kodama T; Tsukada R; Saka R; Tazuke Y; Miyagawa S; Okuyama H Surg Case Rep; 2022 Jan; 8(1):10. PubMed ID: 35024979 [TBL] [Abstract][Full Text] [Related]
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