BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

164 related articles for article (PubMed ID: 36362492)

  • 1. Real-Life Experience with Oral Eliglustat in Patients with Gaucher Disease Previously Treated with Enzyme Replacement Therapy.
    Istaiti M; Becker-Cohen M; Dinur T; Revel-Vilk S; Zimran A
    J Clin Med; 2022 Oct; 11(21):. PubMed ID: 36362492
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Incremental biomarker and clinical outcomes after switch from enzyme therapy to eliglustat substrate reduction therapy in Gaucher disease.
    Kleytman N; Ruan J; Ruan A; Zhang B; Murugesan V; Lin H; Guo L; Klinger K; Mistry PK
    Mol Genet Metab Rep; 2021 Dec; 29():100798. PubMed ID: 34485083
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Patient reported outcomes of patients with Gaucher disease type 1 treated with eliglustat in real-world settings: The ELIPRO study.
    Camou F; Lagadec A; Coutinho A; Berger MG; Cador-Rousseau B; Gaches F; Belmatoug N
    Mol Genet Metab; 2023 Nov; 140(3):107667. PubMed ID: 37597334
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Eliglustat: A Review in Gaucher Disease Type 1.
    Scott LJ
    Drugs; 2015 Sep; 75(14):1669-78. PubMed ID: 26384672
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Budget Impact Analysis of Eliglustat for the Treatment of Gaucher Disease Type 1 in the United States.
    Nalysnyk L; Sugarman R; Cele C; Uyei J; Ward A
    J Manag Care Spec Pharm; 2018 Oct; 24(10):1002-1008. PubMed ID: 30247105
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Real-world effectiveness of eliglustat in treatment-naïve and switch patients enrolled in the International Collaborative Gaucher Group Gaucher Registry.
    Mistry PK; Balwani M; Charrow J; Kishnani P; Niederau C; Underhill LH; McClain MR
    Am J Hematol; 2020 Sep; 95(9):1038-1046. PubMed ID: 32438452
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Safety and efficacy of eliglustat combined to enzyme replacement therapy for lymphadenopathy in patients with Gaucher disease type 3.
    Lee NC; Chien YH; Wang CH; Wong SL; Peng SS; Tsai FJ; Hwu WL
    Mol Genet Metab Rep; 2022 Jun; 31():100867. PubMed ID: 35782609
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Biochemical response to substrate reduction therapy versus enzyme replacement therapy in Gaucher disease type 1 patients.
    Smid BE; Ferraz MJ; Verhoek M; Mirzaian M; Wisse P; Overkleeft HS; Hollak CE; Aerts JM
    Orphanet J Rare Dis; 2016 Mar; 11():28. PubMed ID: 27008851
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Long-term adverse event profile from four completed trials of oral eliglustat in adults with Gaucher disease type 1.
    Peterschmitt MJ; Freisens S; Underhill LH; Foster MC; Lewis G; Gaemers SJM
    Orphanet J Rare Dis; 2019 Jun; 14(1):128. PubMed ID: 31174576
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Recommendations for oral treatment for adult patients with type 1 Gaucher disease.
    Torralba-Cabeza MÁ; Morado-Arias M; Pijierro-Amador A; Fernández-Canal MC; Villarrubia-Espinosa J
    Rev Clin Esp (Barc); 2022 Jun; ():. PubMed ID: 35676195
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Long-term effects of eliglustat on skeletal manifestations in clinical trials of patients with Gaucher disease type 1.
    Cox TM; Charrow J; Lukina E; Mistry PK; Foster MC; Peterschmitt MJ
    Genet Med; 2023 Feb; 25(2):100329. PubMed ID: 36469032
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Stability is maintained in adults with Gaucher disease type 1 switched from velaglucerase alfa to eliglustat or imiglucerase: A sub-analysis of the eliglustat ENCORE trial.
    Pleat R; Cox TM; Burrow TA; Giraldo P; Goker-Alpan O; Rosenbloom BE; Croal LR; Underhill LH; Gaemers SJ; Peterschmitt MJ
    Mol Genet Metab Rep; 2016 Dec; 9():25-28. PubMed ID: 27722092
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Effectiveness and Safety of Eliglustat Treatment in Gaucher Disease: Real-life Unicentric Experience.
    Duminuco A; Fazio M; Grasso S; Gullo L; Riccobene C; Calafiore V; Markovic U; Di Raimondo F; Giuffrida G
    Clin Ther; 2023 Nov; 45(11):1105-1110. PubMed ID: 37722956
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Switching between Enzyme Replacement Therapies and Substrate Reduction Therapies in Patients with Gaucher Disease: Data from the Gaucher Outcome Survey (GOS).
    Hughes DA; Deegan P; Giraldo P; Göker-Alpan Ö; Lau H; Lukina E; Revel-Vilk S; Scarpa M; Botha J; Gadir N; Zimran A;
    J Clin Med; 2022 Aug; 11(17):. PubMed ID: 36079085
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Impact on bone microarchitecture and failure load in a patient with type I Gaucher disease who switched from Imiglucerase to Eliglustat.
    Sidhu K; Boyd SK; Khan A
    Mol Genet Metab Rep; 2020 Sep; 24():100606. PubMed ID: 32509532
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Real life data: follow-up assessment on Spanish Gaucher disease patients treated with eliglustat. TRAZELGA project.
    Serrano-Gonzalo I; de Frutos LL; Lahoz-Gil C; Delgado-Mateos F; Fernández-Galán MÁ; Morales-Conejo M; Calle-Gordo MV; Ibarretxe-Gerediaga D; Madinaveitia-Ochoa A; Albarracin-Arraigosa A; Balanzat-Muñoz J; Correcher-Medina P; García-Frade LJ; Hernández-Rivas JM; Labbadia F; López-Dupla JM; Lozano-Almela ML; Mora-Casterá E; Noya-Pereira MS; Ruíz-Guinaldo MÁ; Del Mar Tormo-Díaz M; Vitoria-Miñana I; Arévalo-Vargas I; Andrade-Campos M; Giraldo P
    Orphanet J Rare Dis; 2023 Dec; 18(1):390. PubMed ID: 38102667
    [TBL] [Abstract][Full Text] [Related]  

  • 17. A pooled analysis of adverse events in 393 adults with Gaucher disease type 1 from four clinical trials of oral eliglustat: Evaluation of frequency, timing, and duration.
    Peterschmitt MJ; Cox GF; Ibrahim J; MacDougall J; Underhill LH; Patel P; Gaemers SJM
    Blood Cells Mol Dis; 2018 Feb; 68():185-191. PubMed ID: 28126395
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Management and monitoring recommendations for the use of eliglustat in adults with type 1 Gaucher disease in Europe.
    Belmatoug N; Di Rocco M; Fraga C; Giraldo P; Hughes D; Lukina E; Maison-Blanche P; Merkel M; Niederau C; Plӧckinger U; Richter J; Stulnig TM; Vom Dahl S; Cox TM
    Eur J Intern Med; 2017 Jan; 37():25-32. PubMed ID: 27522145
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials.
    Lukina E; Balwani M; Belmatoug N; Watman N; Hughes D; Gaemers SJM; Foster MC; Lewis G; Peterschmitt MJ
    JIMD Rep; 2021 Jan; 57(1):76-84. PubMed ID: 33473343
    [TBL] [Abstract][Full Text] [Related]  

  • 20.
    ; ; . PubMed ID:
    [No Abstract]   [Full Text] [Related]  

    [Next]    [New Search]
    of 9.