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24. Developing DMD therapeutics: a review of the effectiveness of small molecules, stop-codon readthrough, dystrophin gene replacement, and exon-skipping therapies. Sheikh O; Yokota T Expert Opin Investig Drugs; 2021 Feb; 30(2):167-176. PubMed ID: 33393390 [TBL] [Abstract][Full Text] [Related]
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36. [Exon skipping therapy for Duchenne muscular dystrophy by using antisense Morpholino]. Takeda S Rinsho Shinkeigaku; 2009 Nov; 49(11):856-8. PubMed ID: 20030230 [TBL] [Abstract][Full Text] [Related]
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38. NS-065/NCNP-01: An Antisense Oligonucleotide for Potential Treatment of Exon 53 Skipping in Duchenne Muscular Dystrophy. Watanabe N; Nagata T; Satou Y; Masuda S; Saito T; Kitagawa H; Komaki H; Takagaki K; Takeda S Mol Ther Nucleic Acids; 2018 Dec; 13():442-449. PubMed ID: 30388618 [TBL] [Abstract][Full Text] [Related]
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