182 related articles for article (PubMed ID: 36401028)
1. Restoring Dystrophin Expression with Duchenne Muscular Dystrophy Exon 45 Skipping in Induced Pluripotent Stem Cell-Derived Cardiomyocytes.
Sato M; Shiba N; Miyazaki D; Shiba Y; Nakamura A
Methods Mol Biol; 2023; 2587():141-151. PubMed ID: 36401028
[TBL] [Abstract][Full Text] [Related]
2. Amelioration of intracellular Ca
Sato M; Shiba N; Miyazaki D; Shiba Y; Echigoya Y; Yokota T; Takizawa H; Aoki Y; Takeda S; Nakamura A
Biochem Biophys Res Commun; 2019 Nov; 520(1):179-185. PubMed ID: 31585729
[TBL] [Abstract][Full Text] [Related]
3. Exon skipping and gene transfer restore dystrophin expression in human induced pluripotent stem cells-cardiomyocytes harboring DMD mutations.
Dick E; Kalra S; Anderson D; George V; Ritso M; Laval SH; Barresi R; Aartsma-Rus A; Lochmüller H; Denning C
Stem Cells Dev; 2013 Oct; 22(20):2714-24. PubMed ID: 23829870
[TBL] [Abstract][Full Text] [Related]
4. Restoration of Dystrophin Protein Expression by Exon Skipping Utilizing CRISPR-Cas9 in Myoblasts Derived from DMD Patient iPS Cells.
Ifuku M; Iwabuchi KA; Tanaka M; Lung MSY; Hotta A
Methods Mol Biol; 2018; 1828():191-217. PubMed ID: 30171543
[TBL] [Abstract][Full Text] [Related]
5. Full-Length Dystrophin Restoration via Targeted Exon Addition in DMD-Patient Specific iPSCs and Cardiomyocytes.
Xiao R; Zhou M; Wang P; Zeng B; Wu L; Hu Z; Liang D
Int J Mol Sci; 2022 Aug; 23(16):. PubMed ID: 36012442
[TBL] [Abstract][Full Text] [Related]
6. Targeted addition of mini-dystrophin into rDNA locus of Duchenne muscular dystrophy patient-derived iPSCs.
Zeng B; Zhou M; Liu B; Shen F; Xiao R; Su J; Hu Z; Zhang Y; Gu A; Wu L; Liu X; Liang D
Biochem Biophys Res Commun; 2021 Mar; 545():40-45. PubMed ID: 33540285
[TBL] [Abstract][Full Text] [Related]
7. Restoring Dystrophin Expression with Exon 44 and 53 Skipping in the DMD Gene in Immortalized Myotubes.
Echigoya Y; Yokota T
Methods Mol Biol; 2023; 2587():125-139. PubMed ID: 36401027
[TBL] [Abstract][Full Text] [Related]
8. Quantitative Evaluation of Exon Skipping in Urine-Derived Cells for Duchenne Muscular Dystrophy.
Kunitake K; Sathyaprakash C; Motohashi N; Aoki Y
Methods Mol Biol; 2023; 2587():153-164. PubMed ID: 36401029
[TBL] [Abstract][Full Text] [Related]
9. CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.
Zhang Y; Long C; Li H; McAnally JR; Baskin KK; Shelton JM; Bassel-Duby R; Olson EN
Sci Adv; 2017 Apr; 3(4):e1602814. PubMed ID: 28439558
[TBL] [Abstract][Full Text] [Related]
10. Evaluation of Exon Skipping and Dystrophin Restoration in In Vitro Models of Duchenne Muscular Dystrophy.
López-Martínez A; Soblechero-Martín P; Arechavala-Gomeza V
Methods Mol Biol; 2022; 2434():217-233. PubMed ID: 35213020
[TBL] [Abstract][Full Text] [Related]
11. Electrophysiological abnormalities in induced pluripotent stem cell-derived cardiomyocytes generated from Duchenne muscular dystrophy patients.
Eisen B; Ben Jehuda R; Cuttitta AJ; Mekies LN; Shemer Y; Baskin P; Reiter I; Willi L; Freimark D; Gherghiceanu M; Monserrat L; Scherr M; Hilfiker-Kleiner D; Arad M; Michele DE; Binah O
J Cell Mol Med; 2019 Mar; 23(3):2125-2135. PubMed ID: 30618214
[TBL] [Abstract][Full Text] [Related]
12. Correction of Three Prominent Mutations in Mouse and Human Models of Duchenne Muscular Dystrophy by Single-Cut Genome Editing.
Min YL; Chemello F; Li H; Rodriguez-Caycedo C; Sanchez-Ortiz E; Mireault AA; McAnally JR; Shelton JM; Zhang Y; Bassel-Duby R; Olson EN
Mol Ther; 2020 Sep; 28(9):2044-2055. PubMed ID: 32892813
[TBL] [Abstract][Full Text] [Related]
13. Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9.
Li HL; Fujimoto N; Sasakawa N; Shirai S; Ohkame T; Sakuma T; Tanaka M; Amano N; Watanabe A; Sakurai H; Yamamoto T; Yamanaka S; Hotta A
Stem Cell Reports; 2015 Jan; 4(1):143-154. PubMed ID: 25434822
[TBL] [Abstract][Full Text] [Related]
14. In Vitro Multiexon Skipping by Antisense PMOs in Dystrophic Dog and Exon 7-Deleted DMD Patient.
Nakamura A; Aoki Y; Tsoumpra M; Yokota T; Takeda S
Methods Mol Biol; 2018; 1828():151-163. PubMed ID: 30171540
[TBL] [Abstract][Full Text] [Related]
15. Efficacy of Multi-exon Skipping Treatment in Duchenne Muscular Dystrophy Dog Model Neonates.
Lim KRQ; Echigoya Y; Nagata T; Kuraoka M; Kobayashi M; Aoki Y; Partridge T; Maruyama R; Takeda S; Yokota T
Mol Ther; 2019 Jan; 27(1):76-86. PubMed ID: 30448197
[TBL] [Abstract][Full Text] [Related]
16. Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy.
Echigoya Y; Lim KRQ; Trieu N; Bao B; Miskew Nichols B; Vila MC; Novak JS; Hara Y; Lee J; Touznik A; Mamchaoui K; Aoki Y; Takeda S; Nagaraju K; Mouly V; Maruyama R; Duddy W; Yokota T
Mol Ther; 2017 Nov; 25(11):2561-2572. PubMed ID: 28865998
[TBL] [Abstract][Full Text] [Related]
17. In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophy.
Wang Q; Yin H; Camelliti P; Betts C; Moulton H; Lee H; Saleh AF; Gait MJ; Wood MJ
J Gene Med; 2010 Apr; 12(4):354-64. PubMed ID: 20235089
[TBL] [Abstract][Full Text] [Related]
18. Precise correction of Duchenne muscular dystrophy exon deletion mutations by base and prime editing.
Chemello F; Chai AC; Li H; Rodriguez-Caycedo C; Sanchez-Ortiz E; Atmanli A; Mireault AA; Liu N; Bassel-Duby R; Olson EN
Sci Adv; 2021 Apr; 7(18):. PubMed ID: 33931459
[TBL] [Abstract][Full Text] [Related]
19. A multicenter comparison of quantification methods for antisense oligonucleotide-induced DMD exon 51 skipping in Duchenne muscular dystrophy cell cultures.
Hiller M; Falzarano MS; Garcia-Jimenez I; Sardone V; Verheul RC; Popplewell L; Anthony K; Ruiz-Del-Yerro E; Osman H; Goeman JJ; Mamchaoui K; Dickson G; Ferlini A; Muntoni F; Aartsma-Rus A; Arechavala-Gomeza V; Datson NA; Spitali P
PLoS One; 2018; 13(10):e0204485. PubMed ID: 30278058
[TBL] [Abstract][Full Text] [Related]
20. Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy.
Moretti A; Fonteyne L; Giesert F; Hoppmann P; Meier AB; Bozoglu T; Baehr A; Schneider CM; Sinnecker D; Klett K; Fröhlich T; Rahman FA; Haufe T; Sun S; Jurisch V; Kessler B; Hinkel R; Dirschinger R; Martens E; Jilek C; Graf A; Krebs S; Santamaria G; Kurome M; Zakhartchenko V; Campbell B; Voelse K; Wolf A; Ziegler T; Reichert S; Lee S; Flenkenthaler F; Dorn T; Jeremias I; Blum H; Dendorfer A; Schnieke A; Krause S; Walter MC; Klymiuk N; Laugwitz KL; Wolf E; Wurst W; Kupatt C
Nat Med; 2020 Feb; 26(2):207-214. PubMed ID: 31988462
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]