BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

345 related articles for article (PubMed ID: 36691324)

  • 1. Gene therapy for hemophilia: looking beyond factor expression.
    Yamaguti-Hayakawa GG; Ozelo MC
    Exp Biol Med (Maywood); 2022 Dec; 247(24):2223-2232. PubMed ID: 36691324
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Comprehensive analysis and prediction of long-term durability of factor IX activity following etranacogene dezaparvovec gene therapy in the treatment of hemophilia B.
    Shah J; Kim H; Sivamurthy K; Monahan PE; Fries M
    Curr Med Res Opin; 2023 Feb; 39(2):227-237. PubMed ID: 36285399
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Hemophilia Gene Therapy: Ready for Prime Time?
    VandenDriessche T; Chuah MK
    Hum Gene Ther; 2017 Nov; 28(11):1013-1023. PubMed ID: 28793786
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Gene Therapy for Hemophilia.
    Nienhuis AW; Nathwani AC; Davidoff AM
    Mol Ther; 2017 May; 25(5):1163-1167. PubMed ID: 28411016
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Practical Implications of Factor IX Gene Transfer for Individuals with Hemophilia B: A Clinical Perspective.
    Miesbach W; Sawyer EK
    Hum Gene Ther Clin Dev; 2018 Jun; 29(2):80-89. PubMed ID: 29624465
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Treatment patterns and bleeding outcomes in persons with severe hemophilia A and B in a real-world setting.
    Ay C; Perschy L; Rejtö J; Kaider A; Pabinger I
    Ann Hematol; 2020 Dec; 99(12):2763-2771. PubMed ID: 32918114
    [TBL] [Abstract][Full Text] [Related]  

  • 7. The evolution of recombinant factor replacement for hemophilia.
    Sankar AD; Weyand AC; Pipe SW
    Transfus Apher Sci; 2019 Oct; 58(5):596-600. PubMed ID: 31421983
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Gene therapy for hemophilia.
    Nathwani AC
    Hematology Am Soc Hematol Educ Program; 2022 Dec; 2022(1):569-578. PubMed ID: 36485127
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Progress, and prospects in the therapeutic armamentarium of persons with congenital hemophilia. Defining the place for liver-directed gene therapy.
    Di Minno G; Castaman G; De Cristofaro R; Brunetti-Pierri N; Pastore L; Castaldo G; Trama U; Di Minno M
    Blood Rev; 2023 Mar; 58():101011. PubMed ID: 36031462
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Hemophilia A/B.
    Croteau SE
    Hematol Oncol Clin North Am; 2022 Aug; 36(4):797-812. PubMed ID: 35773055
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Advances in Gene Therapy for Hemophilia.
    Nathwani AC; Davidoff AM; Tuddenham EGD
    Hum Gene Ther; 2017 Nov; 28(11):1004-1012. PubMed ID: 28835123
    [TBL] [Abstract][Full Text] [Related]  

  • 12. New and improved AAVenues: current status of hemophilia B gene therapy.
    Brimble MA; Reiss UM; Nathwani AC; Davidoff AM
    Expert Opin Biol Ther; 2016; 16(1):79-92. PubMed ID: 26524468
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Coagulation factors with improved properties for hemophilia gene therapy.
    Pipe SW
    Semin Thromb Hemost; 2004 Apr; 30(2):227-37. PubMed ID: 15118934
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
    George LA; Sullivan SK; Giermasz A; Rasko JEJ; Samelson-Jones BJ; Ducore J; Cuker A; Sullivan LM; Majumdar S; Teitel J; McGuinn CE; Ragni MV; Luk AY; Hui D; Wright JF; Chen Y; Liu Y; Wachtel K; Winters A; Tiefenbacher S; Arruda VR; van der Loo JCM; Zelenaia O; Takefman D; Carr ME; Couto LB; Anguela XM; High KA
    N Engl J Med; 2017 Dec; 377(23):2215-2227. PubMed ID: 29211678
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Advances in gene therapy for hemophilia: basis, current status, and future perspectives.
    Ohmori T
    Int J Hematol; 2020 Jan; 111(1):31-41. PubMed ID: 30083852
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Pathogenesis and treatment of osteoporosis in patients with hemophilia.
    Lin X; Gao P; Zhang Q; Jiang Y; Wang O; Xia W; Li M
    Arch Osteoporos; 2023 Jan; 18(1):17. PubMed ID: 36598583
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Engineered factor IX variants bypass FVIII and correct hemophilia A phenotype in mice.
    Milanov P; Ivanciu L; Abriss D; Quade-Lyssy P; Miesbach W; Alesci S; Tonn T; Grez M; Seifried E; Schüttrumpf J
    Blood; 2012 Jan; 119(2):602-11. PubMed ID: 22031860
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Foundations of hemophilia and epidemiology.
    Quintana Paris L
    Blood Coagul Fibrinolysis; 2023 Jun; 34(S1):S35-S36. PubMed ID: 37254731
    [TBL] [Abstract][Full Text] [Related]  

  • 19. [Diagnosis and management of hemophilia].
    Tokugawa T
    Rinsho Ketsueki; 2020; 61(9):1338-1348. PubMed ID: 33162534
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Hemophilia and von Willebrand's disease: 2. Management. Association of Hemophilia Clinic Directors of Canada.
    CMAJ; 1995 Jul; 153(2):147-57. PubMed ID: 7600466
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 18.