These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
11. Nucleic Acid Therapeutics in Huntington's Disease. Singh K; Roy I Recent Pat Biotechnol; 2019; 13(3):187-206. PubMed ID: 30747088 [TBL] [Abstract][Full Text] [Related]
12. Preventing formation of toxic N-terminal huntingtin fragments through antisense oligonucleotide-mediated protein modification. Evers MM; Tran HD; Zalachoras I; Meijer OC; den Dunnen JT; van Ommen GJ; Aartsma-Rus A; van Roon-Mom WM Nucleic Acid Ther; 2014 Feb; 24(1):4-12. PubMed ID: 24380395 [TBL] [Abstract][Full Text] [Related]
13. Allele-selective inhibition of mutant huntingtin by peptide nucleic acid-peptide conjugates, locked nucleic acid, and small interfering RNA. Hu J; Matsui M; Corey DR Ann N Y Acad Sci; 2009 Sep; 1175():24-31. PubMed ID: 19796074 [TBL] [Abstract][Full Text] [Related]
14. Interrupting sequence variants and age of onset in Huntington's disease: clinical implications and emerging therapies. Wright GEB; Black HF; Collins JA; Gall-Duncan T; Caron NS; Pearson CE; Hayden MR Lancet Neurol; 2020 Nov; 19(11):930-939. PubMed ID: 33098802 [TBL] [Abstract][Full Text] [Related]
16. The length of uninterrupted CAG repeats in stem regions of repeat disease associated hairpins determines the amount of short CAG oligonucleotides that are toxic to cells through RNA interference. Murmann AE; Patel M; Jeong SY; Bartom ET; Jennifer Morton A; Peter ME Cell Death Dis; 2022 Dec; 13(12):1078. PubMed ID: 36585400 [TBL] [Abstract][Full Text] [Related]
17. Potent and sustained cellular inhibition of miR-122 by lysine-derivatized peptide nucleic acids (PNA) and phosphorothioate locked nucleic acid (LNA)/2'-O-methyl (OMe) mixmer anti-miRs in the absence of transfection agents. Torres AG; Threlfall RN; Gait MJ Artif DNA PNA XNA; 2011; 2(3):71-8. PubMed ID: 22567190 [TBL] [Abstract][Full Text] [Related]
18. Huntingtin Haplotypes Provide Prioritized Target Panels for Allele-specific Silencing in Huntington Disease Patients of European Ancestry. Kay C; Collins JA; Skotte NH; Southwell AL; Warby SC; Caron NS; Doty CN; Nguyen B; Griguoli A; Ross CJ; Squitieri F; Hayden MR Mol Ther; 2015 Nov; 23(11):1759-1771. PubMed ID: 26201449 [TBL] [Abstract][Full Text] [Related]
19. Biological activity and biotechnological aspects of locked nucleic acids. Lundin KE; Højland T; Hansen BR; Persson R; Bramsen JB; Kjems J; Koch T; Wengel J; Smith CI Adv Genet; 2013; 82():47-107. PubMed ID: 23721720 [TBL] [Abstract][Full Text] [Related]
20. Efficient and Precise Processing of the Optimized Primary Artificial MicroRNA in a Huntingtin-Lowering Adeno-Associated Viral Gene Therapy Wang W; Zhou P; Wang X; Chen F; Christensen E; Thompson J; Ren X; Kells A; Stanek L; Carter T; Hou J; Sah DWY Hum Gene Ther; 2022 Jan; 33(1-2):37-60. PubMed ID: 34806402 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]