These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

161 related articles for article (PubMed ID: 37141855)

  • 1. Confronting complexity in the design and conduct of high-risk rare disease clinical trials.
    Stedman HH
    Mol Ther; 2023 May; 31(5):1191-1192. PubMed ID: 37141855
    [No Abstract]   [Full Text] [Related]  

  • 2. The promise and challenges of rare cancer research.
    Komatsubara KM; Carvajal RD
    Lancet Oncol; 2016 Feb; 17(2):136-138. PubMed ID: 26868336
    [No Abstract]   [Full Text] [Related]  

  • 3. Design of phase III clinical trials for treatments of orphan retinal diseases: an overview of considerations.
    Hyman L
    Retina; 2005 Dec; 25(8 Suppl):S69-S71. PubMed ID: 16374346
    [No Abstract]   [Full Text] [Related]  

  • 4. Clinical trial strategies for rare neurodevelopmental disorders: challenges and opportunities.
    Krishnan ML; Berry-Kravis E; Capal JK; Carpenter R; Gringras P; Hipp JF; Miller MT; Mingorance A; Philpot BD; Pletcher MT; Rotenberg A; Tjeertes J; Wang PP; Willgoss T; de Wit MC; Jeste SS
    Nat Rev Drug Discov; 2021 Sep; 20(9):653-654. PubMed ID: 34002058
    [No Abstract]   [Full Text] [Related]  

  • 5. The changing landscape of clinical trials for mitochondrial diseases: 2011 to present.
    Khayat D; Kurtz TL; Stacpoole PW
    Mitochondrion; 2020 Jan; 50():51-57. PubMed ID: 31669619
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Methodology of clinical trials for rare diseases.
    Tudur Smith C; Williamson PR; Beresford MW
    Best Pract Res Clin Rheumatol; 2014 Apr; 28(2):247-62. PubMed ID: 24974061
    [TBL] [Abstract][Full Text] [Related]  

  • 7. A patient-researcher partnership for rare cancer research.
    Staniszewka S
    Nat Med; 2020 Feb; 26(2):164-165. PubMed ID: 32042195
    [No Abstract]   [Full Text] [Related]  

  • 8. [Rare diseases as models in clinical research--from genetics to better medical care ].
    Schmidtke J; Schmidt RE
    Bundesgesundheitsblatt Gesundheitsforschung Gesundheitsschutz; 2007 Dec; 50(12):1475-6. PubMed ID: 18058147
    [No Abstract]   [Full Text] [Related]  

  • 9. Should clinical trials be approached differently for rare cancers?
    Olver I
    Future Oncol; 2016 May; 12(10):1207-9. PubMed ID: 26939845
    [No Abstract]   [Full Text] [Related]  

  • 10. Proceedings of the First International Symposium on Translational Clinical Research for Inherited and Orphan Retinal Diseases. November 5-7, 2004. Washington, DC, USA.
    Retina; 2005 Dec; 25(8 Suppl):S1-113. PubMed ID: 16509005
    [No Abstract]   [Full Text] [Related]  

  • 11. Rare diseases: what do you need to know?
    Stewart S; Peers K
    Nurs Times; 2013 Nov 13-19; 109(45):12-4. PubMed ID: 24380183
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Rare diseases. Foreword.
    Jones LH
    Future Med Chem; 2014 Jun; 6(9):969-70. PubMed ID: 25068979
    [No Abstract]   [Full Text] [Related]  

  • 13. From gene to treatment: supporting rare disease translational research through model systems.
    Hmeljak J; Justice MJ
    Dis Model Mech; 2019 Feb; 12(2):. PubMed ID: 30819728
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Alternative designs for clinical trials in rare diseases.
    Abrahamyan L; Feldman BM; Tomlinson G; Faughnan ME; Johnson SR; Diamond IR; Gupta S
    Am J Med Genet C Semin Med Genet; 2016 Dec; 172(4):313-331. PubMed ID: 27862920
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Challenges associated with clinical trials for inherited and orphan retinal diseases.
    Fishman GA
    Retina; 2005 Dec; 25(8 Suppl):S10-S12. PubMed ID: 16374308
    [No Abstract]   [Full Text] [Related]  

  • 16. Gene therapy for rare diseases: summary of a National Institutes of Health workshop, September 13, 2012.
    O'Reilly M; Kohn DB; Bartlett J; Benson J; Brooks PJ; Byrne BJ; Camozzi C; Cornetta K; Crystal RG; Fong Y; Gargiulo L; Gopal-Srivastava R; High KA; Jacobson SG; Jambou RC; Montgomery M; Rosenthal E; Samulski RJ; Skarlatos SI; Sorrentino B; Wilson JM; Xie Y; Corrigan-Curay J
    Hum Gene Ther; 2013 Apr; 24(4):355-62. PubMed ID: 23517518
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Gene therapies advance towards finish line.
    Mullard A
    Nat Rev Drug Discov; 2011 Sep; 10(10):719-20. PubMed ID: 21959273
    [No Abstract]   [Full Text] [Related]  

  • 18. Spotlight on rare diseases.
    The Lancet Diabetes Endocrinology
    Lancet Diabetes Endocrinol; 2019 Feb; 7(2):75. PubMed ID: 30683214
    [No Abstract]   [Full Text] [Related]  

  • 19. Gene therapy of inherited diseases.
    Fischer A; Cavazzana-Calvo M
    Lancet; 2008 Jun; 371(9629):2044-7. PubMed ID: 18555917
    [No Abstract]   [Full Text] [Related]  

  • 20. [Ophthalmogenetics: Rare Diseases - A Challenge for Diagnostic and Treatment].
    Rudolph G
    Klin Monbl Augenheilkd; 2016 Mar; 232(3):242. PubMed ID: 27011027
    [No Abstract]   [Full Text] [Related]  

    [Next]    [New Search]
    of 9.