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22. Development of a Screening Platform to Identify Small Molecules That Modify ELP1 Pre-mRNA Splicing in Familial Dysautonomia. Salani M; Urbina F; Brenner A; Morini E; Shetty R; Gallagher CS; Law EA; Sunshine S; Finneran DJ; Johnson G; Minor L; Slaugenhaupt SA SLAS Discov; 2019 Jan; 24(1):57-67. PubMed ID: 30085848 [TBL] [Abstract][Full Text] [Related]
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