BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

204 related articles for article (PubMed ID: 37675899)

  • 1. Gene Therapy for Hemoglobinopathies.
    Lidonnici MR; Scaramuzza S; Ferrari G
    Hum Gene Ther; 2023 Sep; 34(17-18):793-807. PubMed ID: 37675899
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Precision Editing as a Therapeutic Approach for β-Hemoglobinopathies.
    Paschoudi K; Yannaki E; Psatha N
    Int J Mol Sci; 2023 May; 24(11):. PubMed ID: 37298481
    [TBL] [Abstract][Full Text] [Related]  

  • 3. A New Era for Hemoglobinopathies: More Than One Curative Option.
    Psatha N; Papayanni PG; Yannaki E
    Curr Gene Ther; 2017; 17(5):364-378. PubMed ID: 29357790
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Gene Therapy for Hemoglobinopathies: Beta-Thalassemia, Sickle Cell Disease.
    Leonard A; Tisdale JF; Bonner M
    Hematol Oncol Clin North Am; 2022 Aug; 36(4):769-795. PubMed ID: 35773052
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Gene Therapy Approaches to Hemoglobinopathies.
    Ferrari G; Cavazzana M; Mavilio F
    Hematol Oncol Clin North Am; 2017 Oct; 31(5):835-852. PubMed ID: 28895851
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Gene Therapy for β-Hemoglobinopathies: From Discovery to Clinical Trials.
    Segura EER; Ayoub PG; Hart KL; Kohn DB
    Viruses; 2023 Mar; 15(3):. PubMed ID: 36992422
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Extending Gene Medicines to All in Need.
    McCune JM; Kiem HP
    N Engl J Med; 2024 May; 390(18):1721-1722. PubMed ID: 38657269
    [No Abstract]   [Full Text] [Related]  

  • 8. Editing outside the body: Ex vivo gene-modification for β-hemoglobinopathy cellular therapy.
    Rosanwo TO; Bauer DE
    Mol Ther; 2021 Nov; 29(11):3163-3178. PubMed ID: 34628053
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Hemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practice.
    Sii-Felice K; Giorgi M; Leboulch P; Payen E
    Exp Hematol; 2018 Aug; 64():12-32. PubMed ID: 29807062
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Gene therapy and gene editing strategies for hemoglobinopathies.
    Lidonnici MR; Ferrari G
    Blood Cells Mol Dis; 2018 May; 70():87-101. PubMed ID: 29336892
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Curative therapy for hemoglobinopathies: an International Society for Cell & Gene Therapy Stem Cell Engineering Committee review comparing outcomes, accessibility and cost of ex vivo stem cell gene therapy versus allogeneic hematopoietic stem cell transplantation.
    Leonard A; Bertaina A; Bonfim C; Cohen S; Prockop S; Purtill D; Russell A; Boelens JJ; Wynn R; Ruggeri A; Abraham A
    Cytotherapy; 2022 Mar; 24(3):249-261. PubMed ID: 34879990
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Genome Editing for the β-Hemoglobinopathies.
    Porteus MH
    Adv Exp Med Biol; 2017; 1013():203-217. PubMed ID: 29127682
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Genome-based therapeutic interventions for β-type hemoglobinopathies.
    Karamperis K; Tsoumpeli MT; Kounelis F; Koromina M; Mitropoulou C; Moutinho C; Patrinos GP
    Hum Genomics; 2021 Jun; 15(1):32. PubMed ID: 34090531
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders.
    Persons DA
    Hematology Am Soc Hematol Educ Program; 2009; ():690-7. PubMed ID: 20008255
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Lentiviral and genome-editing strategies for the treatment of β-hemoglobinopathies.
    Magrin E; Miccio A; Cavazzana M
    Blood; 2019 Oct; 134(15):1203-1213. PubMed ID: 31467062
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Gene Therapy for β-Hemoglobinopathies.
    Cavazzana M; Antoniani C; Miccio A
    Mol Ther; 2017 May; 25(5):1142-1154. PubMed ID: 28377044
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Genome editing approaches to β-hemoglobinopathies.
    Brusson M; Miccio A
    Prog Mol Biol Transl Sci; 2021; 182():153-183. PubMed ID: 34175041
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Autologous gene therapy for hemoglobinopathies: From bench to patient's bedside.
    Locatelli F; Cavazzana M; Frangoul H; Fuente J; Algeri M; Meisel R
    Mol Ther; 2024 May; 32(5):1202-1218. PubMed ID: 38454604
    [TBL] [Abstract][Full Text] [Related]  

  • 19. In vivo base editing by a single i.v. vector injection for treatment of hemoglobinopathies.
    Li C; Georgakopoulou A; Newby GA; Everette KA; Nizamis E; Paschoudi K; Vlachaki E; Gil S; Anderson AK; Koob T; Huang L; Wang H; Kiem HP; Liu DR; Yannaki E; Lieber A
    JCI Insight; 2022 Oct; 7(19):. PubMed ID: 36006707
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.
    Payen E; Leboulch P
    Hematology Am Soc Hematol Educ Program; 2012; 2012():276-83. PubMed ID: 23233592
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 11.