212 related articles for article (PubMed ID: 37752993)
1. Hematopoietic cell transplantation and gene therapy for Diamond-Blackfan anemia: state of the art and science.
Bhoopalan SV; Suryaprakash S; Sharma A; Wlodarski MW
Front Oncol; 2023; 13():1236038. PubMed ID: 37752993
[TBL] [Abstract][Full Text] [Related]
2. Outcome of allogeneic Hematopoietic Stem Cell Transplantation on Diamond-Blackfan anemia using busulfan-based myeloablative regimen.
Behfar M; Koochakzadeh L; Yazdanian N; Salajegheh P; Rostami T; Khodayari-Namini N; Ghavamzadeh A; Hamidieh AA
Turk J Pediatr; 2019; 61(3):407-412. PubMed ID: 31916719
[TBL] [Abstract][Full Text] [Related]
3. An RPS19-edited model for Diamond-Blackfan anemia reveals TP53-dependent impairment of hematopoietic stem cell activity.
Bhoopalan SV; Yen JS; Mayuranathan T; Mayberry KD; Yao Y; Lillo Osuna MA; Jang Y; Liyanage JS; Blanc L; Ellis SR; Wlodarski MW; Weiss MJ
JCI Insight; 2023 Jan; 8(1):. PubMed ID: 36413407
[TBL] [Abstract][Full Text] [Related]
4. Recommendations on hematopoietic stem cell transplantation for patients with Diamond-Blackfan anemia. On behalf of the Pediatric Diseases and Severe Aplastic Anemia Working Parties of the EBMT.
Diaz-de-Heredia C; Bresters D; Faulkner L; Yesilipek A; Strahm B; Miano M; Dalle JH; Peffault de Latour R; Corbacioglu S
Bone Marrow Transplant; 2021 Dec; 56(12):2956-2963. PubMed ID: 34462566
[TBL] [Abstract][Full Text] [Related]
5. Perspectives of current understanding and therapeutics of Diamond-Blackfan anemia.
Liu Y; Karlsson S
Leukemia; 2024 Jan; 38(1):1-9. PubMed ID: 37973818
[TBL] [Abstract][Full Text] [Related]
6. Variable Clinical Features in a Large Family With Diamond Blackfan Anemia Caused by a Pathogenic Missense Mutation in
Cole S; Giri N; Alter BP; Gianferante DM
Front Genet; 2022; 13():914141. PubMed ID: 35923690
[No Abstract] [Full Text] [Related]
7. Toward RNA Repair of Diamond Blackfan Anemia Hematopoietic Stem Cells.
D'Allard DL; Liu JM
Hum Gene Ther; 2016 Oct; 27(10):792-801. PubMed ID: 27550323
[TBL] [Abstract][Full Text] [Related]
8. Proerythroblast Cells of Diamond-Blackfan Anemia Patients With
Karaosmanoglu B; Kursunel MA; Uckan Cetinkaya D; Gumruk F; Esendagli G; Unal S; Taskiran EZ
Front Physiol; 2021; 12():679919. PubMed ID: 34177624
[TBL] [Abstract][Full Text] [Related]
9. Towards a Cure for Diamond-Blackfan Anemia: Views on Gene Therapy.
Vale M; Prochazka J; Sedlacek R
Cells; 2024 May; 13(11):. PubMed ID: 38891052
[TBL] [Abstract][Full Text] [Related]
10. Reduced-intensity conditioning is effective for hematopoietic stem cell transplantation in young pediatric patients with Diamond-Blackfan anemia.
Koyamaishi S; Kamio T; Kobayashi A; Sato T; Kudo K; Sasaki S; Kanezaki R; Hasegawa D; Muramatsu H; Takahashi Y; Sasahara Y; Hiramatsu H; Kakuda H; Tanaka M; Ishimura M; Nishi M; Ishiguro A; Yabe H; Sarashina T; Yamamoto M; Yuza Y; Hyakuna N; Yoshida K; Kanno H; Ohga S; Ohara A; Kojima S; Miyano S; Ogawa S; Toki T; Terui K; Ito E
Bone Marrow Transplant; 2021 May; 56(5):1013-1020. PubMed ID: 32948829
[TBL] [Abstract][Full Text] [Related]
11. Proliferation deficiency of multipotent hematopoietic progenitors in ribosomal protein S19 (RPS19)-deficient diamond-Blackfan anemia improves following RPS19 gene transfer.
Hamaguchi I; Flygare J; Nishiura H; Brun AC; Ooka A; Kiefer T; Ma Z; Dahl N; Richter J; Karlsson S
Mol Ther; 2003 May; 7(5 Pt 1):613-22. PubMed ID: 12718904
[TBL] [Abstract][Full Text] [Related]
12. L-leucine improves anemia and growth in patients with transfusion-dependent Diamond-Blackfan anemia: Results from a multicenter pilot phase I/II study from the Diamond-Blackfan Anemia Registry.
Vlachos A; Atsidaftos E; Lababidi ML; Muir E; Rogers ZR; Alhushki W; Bernstein J; Glader B; Gruner B; Hartung H; Knoll C; Loew T; Nalepa G; Narla A; Panigrahi AR; Sieff CA; Walkovich K; Farrar JE; Lipton JM
Pediatr Blood Cancer; 2020 Dec; 67(12):e28748. PubMed ID: 33025707
[TBL] [Abstract][Full Text] [Related]
13. Successful gene therapy of Diamond-Blackfan anemia in a mouse model and human CD34
Liu Y; Dahl M; Debnath S; Rothe M; Smith EM; Grahn THM; Warsi S; Chen J; Flygare J; Schambach A; Karlsson S
Haematologica; 2022 Feb; 107(2):446-456. PubMed ID: 33440921
[TBL] [Abstract][Full Text] [Related]
14. How I treat Diamond-Blackfan anemia.
Vlachos A; Muir E
Blood; 2010 Nov; 116(19):3715-23. PubMed ID: 20651069
[TBL] [Abstract][Full Text] [Related]
15. Critical Issues in Diamond-Blackfan Anemia and Prospects for Novel Treatment.
Li H; Lodish HF; Sieff CA
Hematol Oncol Clin North Am; 2018 Aug; 32(4):701-712. PubMed ID: 30047421
[TBL] [Abstract][Full Text] [Related]
16. Emerging Therapeutic Approaches for Diamond Blackfan Anemia.
Aspesi A; Borsotti C; Follenzi A
Curr Gene Ther; 2018; 18(6):327-335. PubMed ID: 30411682
[TBL] [Abstract][Full Text] [Related]
17. Hematopoietic cell transplantation for Diamond Blackfan anemia: A report from the Pediatric Group of the Brazilian Bone Marrow Transplantation Society.
Darrigo LG; Loth G; Kuwahara C; Vieira A; Colturato V; Rodrigues AL; Arcuri L; Fernandes J; Macedo A; Tavares R; Gomes A; Ribeiro L; Seber A; Zecchin V; de Souza M; Calixto R; Pasquini R; Flowers M; Rocha V; Bonfim C
Eur J Haematol; 2020 Oct; 105(4):426-433. PubMed ID: 32525237
[TBL] [Abstract][Full Text] [Related]
18. Hematopoietic stem cell transplantation for Diamond Blackfan anemia: a report from the Diamond Blackfan Anemia Registry.
Vlachos A; Federman N; Reyes-Haley C; Abramson J; Lipton JM
Bone Marrow Transplant; 2001 Feb; 27(4):381-6. PubMed ID: 11313667
[TBL] [Abstract][Full Text] [Related]
19. Stem Cell Transplantation for Diamond-Blackfan Anemia. A Retrospective Study on Behalf of the Severe Aplastic Anemia Working Party of the European Blood and Marrow Transplantation Group (EBMT).
Miano M; Eikema DJ; de la Fuente J; Bosman P; Ghavamzadeh A; Smiers F; Sengeløv H; Yesilipek A; Formankova R; Bader P; Díaz Pérez MÁ; Bertrand Y; Niemeyer C; Diallo S; Ansari M; Bykova TA; Faraci M; Bonanomi S; Gozdzik J; Satti TM; Bodova I; Wölfl M; Rocha VG; Mellgren K; Rascon J; Holter W; Lange A; Meisel R; Beguin Y; Mozo Y; Kriván G; Sirvent A; Bruno B; Dalle JH; Onofrillo D; Giardino S; Risitano AM; de Latour RP; Dufour C
Transplant Cell Ther; 2021 Mar; 27(3):274.e1-274.e5. PubMed ID: 33781541
[TBL] [Abstract][Full Text] [Related]
20.
; ; . PubMed ID:
[No Abstract] [Full Text] [Related]
[Next] [New Search]