276 related articles for article (PubMed ID: 37780116)
1. Current approaches and potential challenges in the delivery of gene editing cargos into hematopoietic stem and progenitor cells.
Murugesan R; Karuppusamy KV; Marepally S; Thangavel S
Front Genome Ed; 2023; 5():1148693. PubMed ID: 37780116
[TBL] [Abstract][Full Text] [Related]
2. Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1.
Schiroli G; Ferrari S; Conway A; Jacob A; Capo V; Albano L; Plati T; Castiello MC; Sanvito F; Gennery AR; Bovolenta C; Palchaudhuri R; Scadden DT; Holmes MC; Villa A; Sitia G; Lombardo A; Genovese P; Naldini L
Sci Transl Med; 2017 Oct; 9(411):. PubMed ID: 29021165
[TBL] [Abstract][Full Text] [Related]
3. Gene Editing in Hematopoietic Stem Cells.
Liao J; Wu Y
Adv Exp Med Biol; 2023; 1442():177-199. PubMed ID: 38228965
[TBL] [Abstract][Full Text] [Related]
4. Priming Human Repopulating Hematopoietic Stem and Progenitor Cells for Cas9/sgRNA Gene Targeting.
Charlesworth CT; Camarena J; Cromer MK; Vaidyanathan S; Bak RO; Carte JM; Potter J; Dever DP; Porteus MH
Mol Ther Nucleic Acids; 2018 Sep; 12():89-104. PubMed ID: 30195800
[TBL] [Abstract][Full Text] [Related]
5. Understanding and overcoming adverse consequences of genome editing on hematopoietic stem and progenitor cells.
Lee BC; Lozano RJ; Dunbar CE
Mol Ther; 2021 Nov; 29(11):3205-3218. PubMed ID: 34509667
[TBL] [Abstract][Full Text] [Related]
6. Automated Good Manufacturing Practice-Compatible CRISPR-Cas9 Editing of Hematopoietic Stem and Progenitor Cells for Clinical Treatment of β-Hemoglobinopathies.
Ureña-Bailén G; Block M; Grandi T; Aivazidou F; Quednau J; Krenz D; Daniel-Moreno A; Lamsfus-Calle A; Epting T; Handgretinger R; Wild S; Mezger M
CRISPR J; 2023 Feb; 6(1):5-16. PubMed ID: 36662546
[TBL] [Abstract][Full Text] [Related]
7. Lipid nanoparticles allow efficient and harmless ex vivo gene editing of human hematopoietic cells.
Vavassori V; Ferrari S; Beretta S; Asperti C; Albano L; Annoni A; Gaddoni C; Varesi A; Soldi M; Cuomo A; Bonaldi T; Radrizzani M; Merelli I; Naldini L
Blood; 2023 Aug; 142(9):812-826. PubMed ID: 37294917
[TBL] [Abstract][Full Text] [Related]
8. The Strategies and Challenges of CCR5 Gene Editing in Hematopoietic Stem and Progenitor Cells for the Treatment of HIV.
Karuppusamy KV; Babu P; Thangavel S
Stem Cell Rev Rep; 2021 Oct; 17(5):1607-1618. PubMed ID: 33788143
[TBL] [Abstract][Full Text] [Related]
9. An improved medium formulation for efficient
Rai R; Naseem A; Vetharoy W; Steinberg Z; Thrasher AJ; Santilli G; Cavazza A
Mol Ther Methods Clin Dev; 2023 Jun; 29():58-69. PubMed ID: 36950452
[TBL] [Abstract][Full Text] [Related]
10. Advances and Obstacles in Homology-Mediated Gene Editing of Hematopoietic Stem Cells.
Salisbury-Ruf CT; Larochelle A
J Clin Med; 2021 Feb; 10(3):. PubMed ID: 33535527
[TBL] [Abstract][Full Text] [Related]
11. PLGA-Nanoparticles for Intracellular Delivery of the CRISPR-Complex to Elevate Fetal Globin Expression in Erythroid Cells.
Cruz LJ; van Dijk T; Vepris O; Li TMWY; Schomann T; Baldazzi F; Kurita R; Nakamura Y; Grosveld F; Philipsen S; Eich C
Biomaterials; 2021 Jan; 268():120580. PubMed ID: 33321292
[TBL] [Abstract][Full Text] [Related]
12. CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications.
Venkatesan V; Christopher AC; Karuppusamy KV; Babu P; Alagiri MKK; Thangavel S
J Vis Exp; 2022 Aug; (186):. PubMed ID: 36036597
[TBL] [Abstract][Full Text] [Related]
13. Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases.
Tucci F; Scaramuzza S; Aiuti A; Mortellaro A
Mol Ther; 2021 Feb; 29(2):489-504. PubMed ID: 33221437
[TBL] [Abstract][Full Text] [Related]
14. Homology-directed gene-editing approaches for hematopoietic stem and progenitor cell gene therapy.
Azhagiri MKK; Babu P; Venkatesan V; Thangavel S
Stem Cell Res Ther; 2021 Sep; 12(1):500. PubMed ID: 34503562
[TBL] [Abstract][Full Text] [Related]
15. Efficient polymer nanoparticle-mediated delivery of gene editing reagents into human hematopoietic stem and progenitor cells.
El-Kharrag R; Berckmueller KE; Madhu R; Cui M; Campoy G; Mack HM; Wolf CB; Perez AM; Humbert O; Kiem HP; Radtke S
Mol Ther; 2022 Jun; 30(6):2186-2198. PubMed ID: 35240320
[TBL] [Abstract][Full Text] [Related]
16. Gene Editing of Human Hematopoietic Stem and Progenitor Cells: Promise and Potential Hurdles.
Yu KR; Natanson H; Dunbar CE
Hum Gene Ther; 2016 Oct; 27(10):729-740. PubMed ID: 27483988
[TBL] [Abstract][Full Text] [Related]
17. Combined lentiviral- and RNA-mediated CRISPR/Cas9 delivery for efficient and traceable gene editing in human hematopoietic stem and progenitor cells.
Yudovich D; Bäckström A; Schmiderer L; Žemaitis K; Subramaniam A; Larsson J
Sci Rep; 2020 Dec; 10(1):22393. PubMed ID: 33372184
[TBL] [Abstract][Full Text] [Related]
18. Homology-driven genome editing in hematopoietic stem and progenitor cells using ZFN mRNA and AAV6 donors.
Wang J; Exline CM; DeClercq JJ; Llewellyn GN; Hayward SB; Li PW; Shivak DA; Surosky RT; Gregory PD; Holmes MC; Cannon PM
Nat Biotechnol; 2015 Dec; 33(12):1256-1263. PubMed ID: 26551060
[TBL] [Abstract][Full Text] [Related]
19. Long-term multilineage engraftment of autologous genome-edited hematopoietic stem cells in nonhuman primates.
Peterson CW; Wang J; Norman KK; Norgaard ZK; Humbert O; Tse CK; Yan JJ; Trimble RG; Shivak DA; Rebar EJ; Gregory PD; Holmes MC; Kiem HP
Blood; 2016 May; 127(20):2416-26. PubMed ID: 26980728
[TBL] [Abstract][Full Text] [Related]
20. Megakaryocyte membrane-wrapped nanoparticles for targeted cargo delivery to hematopoietic stem and progenitor cells.
Das S; Harris JC; Winter EJ; Kao CY; Day ES; Papoutsakis ET
Bioeng Transl Med; 2023 May; 8(3):e10456. PubMed ID: 37206243
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]