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8. Cellular function reinstitution of offspring red blood cells cloned from the sickle cell disease patient blood post CRISPR genome editing. Wen J; Tao W; Hao S; Zu Y J Hematol Oncol; 2017 Jun; 10(1):119. PubMed ID: 28610635 [TBL] [Abstract][Full Text] [Related]
9. Drug pipeline 3Q23 - ERT, bispecifics and CRISPR in sickle cell disease. Hodgson J Nat Biotechnol; 2023 Nov; 41(11):1498-1500. PubMed ID: 37950006 [No Abstract] [Full Text] [Related]
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13. CRISPR in personalized medicine: Industry perspectives in gene editing. Hong A Semin Perinatol; 2018 Dec; 42(8):501-507. PubMed ID: 30376985 [TBL] [Abstract][Full Text] [Related]
14. Treatment by CRISPR-Cas9 Gene Editing - A Proof of Principle. Malech HL N Engl J Med; 2021 Jan; 384(3):286-287. PubMed ID: 33471982 [No Abstract] [Full Text] [Related]
15. The promise and challenge of therapeutic genome editing. Doudna JA Nature; 2020 Feb; 578(7794):229-236. PubMed ID: 32051598 [TBL] [Abstract][Full Text] [Related]
16. [CRISPR-Cas system as molecular scissors for gene therapy]. Heinz GA; Mashreghi MF Z Rheumatol; 2017 Feb; 76(1):46-49. PubMed ID: 28124743 [TBL] [Abstract][Full Text] [Related]
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18. [Advances in application of clustered regularly interspaced short palindromic repeats (CRISPR)/CRISPR-associated 9 system in stem cells research]. Sun SJ; Huo JH; Geng ZJ; Sun XY; Fu XB Zhonghua Shao Shang Za Zhi; 2018 Apr; 34(4):253-256. PubMed ID: 29690746 [TBL] [Abstract][Full Text] [Related]
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