BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

393 related articles for article (PubMed ID: 37878144)

  • 1. CRISPR/Cas-based gene editing in therapeutic strategies for beta-thalassemia.
    Zeng S; Lei S; Qu C; Wang Y; Teng S; Huang P
    Hum Genet; 2023 Dec; 142(12):1677-1703. PubMed ID: 37878144
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Precision Editing as a Therapeutic Approach for β-Hemoglobinopathies.
    Paschoudi K; Yannaki E; Psatha N
    Int J Mol Sci; 2023 May; 24(11):. PubMed ID: 37298481
    [TBL] [Abstract][Full Text] [Related]  

  • 3. One-step genetic correction of hemoglobin E/beta-thalassemia patient-derived iPSCs by the CRISPR/Cas9 system.
    Wattanapanitch M; Damkham N; Potirat P; Trakarnsanga K; Janan M; U-Pratya Y; Kheolamai P; Klincumhom N; Issaragrisil S
    Stem Cell Res Ther; 2018 Feb; 9(1):46. PubMed ID: 29482624
    [TBL] [Abstract][Full Text] [Related]  

  • 4. The Combination of CRISPR/Cas9 and iPSC Technologies in the Gene Therapy of Human β-thalassemia in Mice.
    Ou Z; Niu X; He W; Chen Y; Song B; Xian Y; Fan D; Tang D; Sun X
    Sci Rep; 2016 Sep; 6():32463. PubMed ID: 27581487
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Advances in genome editing: the technology of choice for precise and efficient β-thalassemia treatment.
    Ali G; Tariq MA; Shahid K; Ahmad FJ; Akram J
    Gene Ther; 2021 Feb; 28(1-2):6-15. PubMed ID: 32355226
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Targeted deletion of BCL11A gene by CRISPR-Cas9 system for fetal hemoglobin reactivation: A promising approach for gene therapy of beta thalassemia disease.
    Khosravi MA; Abbasalipour M; Concordet JP; Berg JV; Zeinali S; Arashkia A; Azadmanesh K; Buch T; Karimipoor M
    Eur J Pharmacol; 2019 Jul; 854():398-405. PubMed ID: 31039344
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Correction of β-thalassemia by CRISPR/Cas9 editing of the α-globin locus in human hematopoietic stem cells.
    Pavani G; Fabiano A; Laurent M; Amor F; Cantelli E; Chalumeau A; Maule G; Tachtsidi A; Concordet JP; Cereseto A; Mavilio F; Ferrari G; Miccio A; Amendola M
    Blood Adv; 2021 Mar; 5(5):1137-1153. PubMed ID: 33635334
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Identification of novel HPFH-like mutations by CRISPR base editing that elevate the expression of fetal hemoglobin.
    Ravi NS; Wienert B; Wyman SK; Bell HW; George A; Mahalingam G; Vu JT; Prasad K; Bandlamudi BP; Devaraju N; Rajendiran V; Syedbasha N; Pai AA; Nakamura Y; Kurita R; Narayanasamy M; Balasubramanian P; Thangavel S; Marepally S; Velayudhan SR; Srivastava A; DeWitt MA; Crossley M; Corn JE; Mohankumar KM
    Elife; 2022 Feb; 11():. PubMed ID: 35147495
    [TBL] [Abstract][Full Text] [Related]  

  • 9. CRISPR/Cas9-mediated β-globin gene knockout in rabbits recapitulates human β-thalassemia.
    Yang Y; Kang X; Hu S; Chen B; Xie Y; Song B; Zhang Q; Wu H; Ou Z; Xian Y; Fan Y; Li X; Lai L; Sun X
    J Biol Chem; 2021; 296():100464. PubMed ID: 33639162
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Genetic correction of concurrent α- and β-thalassemia patient-derived pluripotent stem cells by the CRISPR-Cas9 technology.
    Li L; Yi H; Liu Z; Long P; Pan T; Huang Y; Li Y; Li Q; Ma Y
    Stem Cell Res Ther; 2022 Mar; 13(1):102. PubMed ID: 35255977
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Prime editing: A potential treatment option for β-thalassemia.
    Arif T; Farooq A; Ahmad FJ; Akhtar M; Choudhery MS
    Cell Biol Int; 2023 Apr; 47(4):699-713. PubMed ID: 36480796
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Co-Treatment of Erythroid Cells from β-Thalassemia Patients with CRISPR-Cas9-Based β
    Cosenza LC; Zuccato C; Zurlo M; Gambari R; Finotti A
    Genes (Basel); 2022 Sep; 13(10):. PubMed ID: 36292612
    [TBL] [Abstract][Full Text] [Related]  

  • 13. [Advances in gene therapy for β-thalassemia and hemophilia based on the CRISPR/Cas9 technology].
    Bao LW; Zhou YY; Zeng FY
    Yi Chuan; 2020 Oct; 42(10):949-964. PubMed ID: 33229321
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements.
    Lattanzi A; Meneghini V; Pavani G; Amor F; Ramadier S; Felix T; Antoniani C; Masson C; Alibeu O; Lee C; Porteus MH; Bao G; Amendola M; Mavilio F; Miccio A
    Mol Ther; 2019 Jan; 27(1):137-150. PubMed ID: 30424953
    [TBL] [Abstract][Full Text] [Related]  

  • 15. CRISPR-mediated gene modification of hematopoietic stem cells with beta-thalassemia IVS-1-110 mutation.
    Gabr H; El Ghamrawy MK; Almaeen AH; Abdelhafiz AS; Hassan AOS; El Sissy MH
    Stem Cell Res Ther; 2020 Sep; 11(1):390. PubMed ID: 32912325
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Genome editing using CRISPR-Cas9 to create the HPFH genotype in HSPCs: An approach for treating sickle cell disease and β-thalassemia.
    Ye L; Wang J; Tan Y; Beyer AI; Xie F; Muench MO; Kan YW
    Proc Natl Acad Sci U S A; 2016 Sep; 113(38):10661-5. PubMed ID: 27601644
    [TBL] [Abstract][Full Text] [Related]  

  • 17. CRISPR-Cas9-mediated gene editing of the BCL11A enhancer for pediatric β
    Fu B; Liao J; Chen S; Li W; Wang Q; Hu J; Yang F; Hsiao S; Jiang Y; Wang L; Chen F; Zhang Y; Wang X; Li D; Liu M; Wu Y
    Nat Med; 2022 Aug; 28(8):1573-1580. PubMed ID: 35922667
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Hurdles to the Adoption of Gene Therapy as a Curative Option for Transfusion-Dependent Thalassemia.
    Thuret I; Ruggeri A; Angelucci E; Chabannon C
    Stem Cells Transl Med; 2022 Apr; 11(4):407-414. PubMed ID: 35267028
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Gene Therapy and Genome Editing.
    Boulad F; Mansilla-Soto J; Cabriolu A; Rivière I; Sadelain M
    Hematol Oncol Clin North Am; 2018 Apr; 32(2):329-342. PubMed ID: 29458735
    [TBL] [Abstract][Full Text] [Related]  

  • 20. CRISPR-Based Gene Therapies: From Preclinical to Clinical Treatments.
    Laurent M; Geoffroy M; Pavani G; Guiraud S
    Cells; 2024 May; 13(10):. PubMed ID: 38786024
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 20.