162 related articles for article (PubMed ID: 37978816)
1. Valoctocogene Roxaparvovec and Etranacogene Dezaparavovec: Novel Gene Therapies for Hemophilia A and B.
Dougherty JA; Dougherty KM
Ann Pharmacother; 2023 Nov; ():10600280231202247. PubMed ID: 37978816
[TBL] [Abstract][Full Text] [Related]
2. Comparative Effectiveness of Valoctocogene Roxaparvovec and Prophylactic Factor VIII Replacement in Severe Hemophilia A.
Oldenburg J; Chambost H; Liu H; Hawes C; You X; Yang X; Newman V; Robinson TM; Hatswell AJ; Hinds D; Santos S; Ozelo M
Adv Ther; 2024 Jun; 41(6):2267-2281. PubMed ID: 38616241
[TBL] [Abstract][Full Text] [Related]
3. Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A.
Mahlangu J; Kaczmarek R; von Drygalski A; Shapiro S; Chou SC; Ozelo MC; Kenet G; Peyvandi F; Wang M; Madan B; Key NS; Laffan M; Dunn AL; Mason J; Quon DV; Symington E; Leavitt AD; Oldenburg J; Chambost H; Reding MT; Jayaram K; Yu H; Mahajan R; Chavele KM; Reddy DB; Henshaw J; Robinson TM; Wong WY; Pipe SW;
N Engl J Med; 2023 Feb; 388(8):694-705. PubMed ID: 36812433
[TBL] [Abstract][Full Text] [Related]
4. Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A.
Ozelo MC; Mahlangu J; Pasi KJ; Giermasz A; Leavitt AD; Laffan M; Symington E; Quon DV; Wang JD; Peerlinck K; Pipe SW; Madan B; Key NS; Pierce GF; O'Mahony B; Kaczmarek R; Henshaw J; Lawal A; Jayaram K; Huang M; Yang X; Wong WY; Kim B;
N Engl J Med; 2022 Mar; 386(11):1013-1025. PubMed ID: 35294811
[TBL] [Abstract][Full Text] [Related]
5. Etranacogene dezaparvovec for hemophilia B gene therapy.
Thornburg CD
Ther Adv Rare Dis; 2021; 2():26330040211058896. PubMed ID: 37181105
[TBL] [Abstract][Full Text] [Related]
6. Comprehensive analysis and prediction of long-term durability of factor IX activity following etranacogene dezaparvovec gene therapy in the treatment of hemophilia B.
Shah J; Kim H; Sivamurthy K; Monahan PE; Fries M
Curr Med Res Opin; 2023 Feb; 39(2):227-237. PubMed ID: 36285399
[TBL] [Abstract][Full Text] [Related]
7. Matching-adjusted indirect comparison of bleeding outcomes in severe haemophilia A: Comparing valoctocogene roxaparvovec gene therapy, emicizumab prophylaxis, and FVIII replacement prophylaxis.
Astermark J; Buckner TW; Frenzel L; Hatswell AJ; You X; Liu H; Goodman E; Santos S; Hawes C; Hinds D; Klamroth R
Haemophilia; 2023 Jul; 29(4):1087-1094. PubMed ID: 37347645
[TBL] [Abstract][Full Text] [Related]
8. Hemophilia Gene Therapy: The End of the Beginning?
De Wolf D; Singh K; Chuah MK; VandenDriessche T
Hum Gene Ther; 2023 Sep; 34(17-18):782-792. PubMed ID: 37672530
[TBL] [Abstract][Full Text] [Related]
9. Assessing the potential cost-effectiveness of a gene therapy for the treatment of hemophilia A.
Cook K; Forbes SP; Adamski K; Ma JJ; Chawla A; Garrison LP
J Med Econ; 2020 May; 23(5):501-512. PubMed ID: 31971453
[No Abstract] [Full Text] [Related]
10. Long-term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post-treatment.
Symington E; Rangarajan S; Lester W; Madan B; Pierce GF; Raheja P; Robinson TM; Osmond D; Russell CB; Vettermann C; Agarwal SK; Li M; Wong WY; Laffan M
Haemophilia; 2024 Mar; 30(2):320-330. PubMed ID: 38317480
[TBL] [Abstract][Full Text] [Related]
11. Etranacogene dezaparvovec-drlb gene therapy for patients with hemophilia B (congenital factor IX deficiency).
Sekayan T; Simmons DH; von Drygalski A
Expert Opin Biol Ther; 2023; 23(12):1173-1184. PubMed ID: 37962325
[TBL] [Abstract][Full Text] [Related]
12. Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1.
O'Mahony B; Dunn AL; Leavitt AD; Peyvandi F; Ozelo MC; Mahlangu J; Peerlinck K; Wang JD; Lowe GC; Tan CW; Giermasz A; Tran H; Khoo TL; Cockrell E; Pepperell D; Chambost H; López Fernández MF; Kazmi R; Majerus E; Skinner MW; Klamroth R; Quinn J; Yu H; Wong WY; Robinson TM; Pipe SW
J Thromb Haemost; 2023 Dec; 21(12):3450-3462. PubMed ID: 37678546
[TBL] [Abstract][Full Text] [Related]
13. Using Real-World Data to Inform Value-Based Contracts for Cell and Gene Therapies in Medicaid.
Zemplenyi A; Leonard J; DiStefano MJ; Anderson KE; Wright GC; Mendola ND; Nair K; McQueen RB
Pharmacoeconomics; 2024 Mar; 42(3):319-328. PubMed ID: 37989969
[TBL] [Abstract][Full Text] [Related]
14. Clinical immunogenicity outcomes from GENEr8-1, a phase 3 study of valoctocogene roxaparvovec, an AAV5-vectored gene therapy for hemophilia A.
Long BR; Robinson TM; Day JRS; Yu H; Lau K; Imtiaz U; Patton KS; de Hart G; Henshaw J; Agarwal S; Vettermann C; Zoog SJ; Gupta S
Mol Ther; 2024 May; ():. PubMed ID: 38796703
[TBL] [Abstract][Full Text] [Related]
15. Valoctocogene Roxaparvovec: First Approval.
Blair HA
Drugs; 2022 Sep; 82(14):1505-1510. PubMed ID: 36214970
[TBL] [Abstract][Full Text] [Related]
16. Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B.
Pipe SW; Leebeek FWG; Recht M; Key NS; Castaman G; Miesbach W; Lattimore S; Peerlinck K; Van der Valk P; Coppens M; Kampmann P; Meijer K; O'Connell N; Pasi KJ; Hart DP; Kazmi R; Astermark J; Hermans CRJR; Klamroth R; Lemons R; Visweshwar N; von Drygalski A; Young G; Crary SE; Escobar M; Gomez E; Kruse-Jarres R; Quon DV; Symington E; Wang M; Wheeler AP; Gut R; Liu YP; Dolmetsch RE; Cooper DL; Li Y; Goldstein B; Monahan PE
N Engl J Med; 2023 Feb; 388(8):706-718. PubMed ID: 36812434
[TBL] [Abstract][Full Text] [Related]
17. Evaluating Gene Therapy as a Potential Paradigm Shift in Treating Severe Hemophilia.
Thornburg CD; Simmons DH; von Drygalski A
BioDrugs; 2023 Sep; 37(5):595-606. PubMed ID: 37490225
[TBL] [Abstract][Full Text] [Related]
18. Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial.
Coppens M; Pipe SW; Miesbach W; Astermark J; Recht M; van der Valk P; Ewenstein B; Pinachyan K; Galante N; Le Quellec S; Monahan PE; Leebeek FWG;
Lancet Haematol; 2024 Apr; 11(4):e265-e275. PubMed ID: 38437857
[TBL] [Abstract][Full Text] [Related]
19. Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A.
Pasi KJ; Laffan M; Rangarajan S; Robinson TM; Mitchell N; Lester W; Symington E; Madan B; Yang X; Kim B; Pierce GF; Wong WY
Haemophilia; 2021 Nov; 27(6):947-956. PubMed ID: 34378280
[TBL] [Abstract][Full Text] [Related]
20. Valoctocogene roxaparvovec (Roctavian) - a gene therapy for severe hemophilia A.
Med Lett Drugs Ther; 2023 Oct; 65(1686):157-158. PubMed ID: 37755692
[No Abstract] [Full Text] [Related]
[Next] [New Search]