These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
31. CRISPR-Cas9 Editing of the Sharma A; Boelens JJ; Cancio M; Hankins JS; Bhad P; Azizy M; Lewandowski A; Zhao X; Chitnis S; Peddinti R; Zheng Y; Kapoor N; Ciceri F; Maclachlan T; Yang Y; Liu Y; Yuan J; Naumann U; Yu VWC; Stevenson SC; De Vita S; LaBelle JL N Engl J Med; 2023 Aug; 389(9):820-832. PubMed ID: 37646679 [TBL] [Abstract][Full Text] [Related]
32. Dual function NFI factors control fetal hemoglobin silencing in adult erythroid cells. Qin K; Huang P; Feng R; Keller CA; Peslak SA; Khandros E; Saari MS; Lan X; Mayuranathan T; Doerfler PA; Abdulmalik O; Giardine B; Chou ST; Shi J; Hardison RC; Weiss MJ; Blobel GA Nat Genet; 2022 Jun; 54(6):874-884. PubMed ID: 35618846 [TBL] [Abstract][Full Text] [Related]
33. Induction of therapeutic levels of HbF in genome-edited primary β Mingoia M; Caria CA; Ye L; Asunis I; Marongiu MF; Manunza L; Sollaino MC; Wang J; Cabriolu A; Kurita R; Nakamura Y; Cucca F; Kan YW; Marini MG; Moi P Br J Haematol; 2021 Jan; 192(2):395-404. PubMed ID: 33216968 [TBL] [Abstract][Full Text] [Related]
34. Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus. Antoniani C; Meneghini V; Lattanzi A; Felix T; Romano O; Magrin E; Weber L; Pavani G; El Hoss S; Kurita R; Nakamura Y; Cradick TJ; Lundberg AS; Porteus M; Amendola M; El Nemer W; Cavazzana M; Mavilio F; Miccio A Blood; 2018 Apr; 131(17):1960-1973. PubMed ID: 29519807 [TBL] [Abstract][Full Text] [Related]
35. SIRT1 activates the expression of fetal hemoglobin genes. Dai Y; Chen T; Ijaz H; Cho EH; Steinberg MH Am J Hematol; 2017 Nov; 92(11):1177-1186. PubMed ID: 28776729 [TBL] [Abstract][Full Text] [Related]
36. Development of a double shmiR lentivirus effectively targeting both BCL11A and ZNF410 for enhanced induction of fetal hemoglobin to treat β-hemoglobinopathies. Liu B; Brendel C; Vinjamur DS; Zhou Y; Harris C; McGuinness M; Manis JP; Bauer DE; Xu H; Williams DA Mol Ther; 2022 Aug; 30(8):2693-2708. PubMed ID: 35526095 [TBL] [Abstract][Full Text] [Related]
37. Hemoglobin genetics: recent contributions of GWAS and gene editing. Smith EC; Orkin SH Hum Mol Genet; 2016 Oct; 25(R2):R99-R105. PubMed ID: 27340226 [TBL] [Abstract][Full Text] [Related]
38. BCL11A-targeted γ-globin gene induction by triterpenoid glycosides of Fagonia indica: A preclinical scientific validation of indigenous herb for the treatment of β-hemoglobinopathies. Iftikhar F; Khan MBN; Tehreem S; Kanwal N; Musharraf SG Bioorg Chem; 2023 Nov; 140():106768. PubMed ID: 37586133 [TBL] [Abstract][Full Text] [Related]
39. 3'HS1 CTCF binding site in human β-globin locus regulates fetal hemoglobin expression. Himadewi P; Wang XQD; Feng F; Gore H; Liu Y; Yu L; Kurita R; Nakamura Y; Pfeifer GP; Liu J; Zhang X Elife; 2021 Sep; 10():. PubMed ID: 34585664 [TBL] [Abstract][Full Text] [Related]
40. Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements. Lattanzi A; Meneghini V; Pavani G; Amor F; Ramadier S; Felix T; Antoniani C; Masson C; Alibeu O; Lee C; Porteus MH; Bao G; Amendola M; Mavilio F; Miccio A Mol Ther; 2019 Jan; 27(1):137-150. PubMed ID: 30424953 [TBL] [Abstract][Full Text] [Related] [Previous] [Next] [New Search]