These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

205 related articles for article (PubMed ID: 38027066)

  • 1. Preclinical evaluation of the efficacy and safety of AAV1-hOTOF in mice and nonhuman primates.
    Zhang L; Wang H; Xun M; Tang H; Wang J; Lv J; Zhu B; Chen Y; Wang D; Hu S; Gao Z; Liu J; Chen ZY; Chen B; Li H; Shu Y
    Mol Ther Methods Clin Dev; 2023 Dec; 31():101154. PubMed ID: 38027066
    [TBL] [Abstract][Full Text] [Related]  

  • 2. AAV1-hOTOF gene therapy for autosomal recessive deafness 9: a single-arm trial.
    Lv J; Wang H; Cheng X; Chen Y; Wang D; Zhang L; Cao Q; Tang H; Hu S; Gao K; Xun M; Wang J; Wang Z; Zhu B; Cui C; Gao Z; Guo L; Yu S; Jiang L; Yin Y; Zhang J; Chen B; Wang W; Chai R; Chen ZY; Li H; Shu Y
    Lancet; 2024 May; 403(10441):2317-2325. PubMed ID: 38280389
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Hair cell-specific Myo15 promoter-mediated gene therapy rescues hearing in DFNB9 mouse model.
    Wang H; Xun M; Tang H; Zhao J; Hu S; Zhang L; Lv J; Wang D; Chen Y; Liu J; Li GL; Wang W; Shu Y; Li H
    Mol Ther Nucleic Acids; 2024 Mar; 35(1):102135. PubMed ID: 38404504
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Preclinical Efficacy And Safety Evaluation of AAV-OTOF in DFNB9 Mouse Model And Nonhuman Primate.
    Qi J; Zhang L; Tan F; Zhang Y; Zhou Y; Zhang Z; Wang H; Yu C; Jiang L; Liu J; Chen T; Wu L; Zhang S; Sun S; Sun S; Lu L; Wang Q; Chai R
    Adv Sci (Weinh); 2024 Jan; 11(3):e2306201. PubMed ID: 38014592
    [TBL] [Abstract][Full Text] [Related]  

  • 5. AAV-Mediated Gene Therapy Restores Hearing in Patients with DFNB9 Deafness.
    Qi J; Tan F; Zhang L; Lu L; Zhang S; Zhai Y; Lu Y; Qian X; Dong W; Zhou Y; Zhang Z; Yang X; Jiang L; Yu C; Liu J; Chen T; Wu L; Tan C; Sun S; Song H; Shu Y; Xu L; Gao X; Li H; Chai R
    Adv Sci (Weinh); 2024 Mar; 11(11):e2306788. PubMed ID: 38189623
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Bilateral gene therapy in children with autosomal recessive deafness 9: single-arm trial results.
    Wang H; Chen Y; Lv J; Cheng X; Cao Q; Wang D; Zhang L; Zhu B; Shen M; Xu C; Xun M; Wang Z; Tang H; Hu S; Cui C; Jiang L; Yin Y; Guo L; Zhou Y; Han L; Gao Z; Zhang J; Yu S; Gao K; Wang J; Chen B; Wang W; Chen ZY; Li H; Shu Y
    Nat Med; 2024 Jul; 30(7):1898-1904. PubMed ID: 38839897
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV.
    György B; Sage C; Indzhykulian AA; Scheffer DI; Brisson AR; Tan S; Wu X; Volak A; Mu D; Tamvakologos PI; Li Y; Fitzpatrick Z; Ericsson M; Breakefield XO; Corey DP; Maguire CA
    Mol Ther; 2017 Feb; 25(2):379-391. PubMed ID: 28082074
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Recovery kinetics of dual AAV-mediated human otoferlin expression.
    Sellon JB; So KS; D'Arcangelo A; Cancelarich S; Drummond MC; Slade PG; Pan N; Gibson TM; Yang T; Burns JC; Palermo AT; Becker L
    Front Mol Neurosci; 2024; 17():1376128. PubMed ID: 38952419
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Adeno-associated virus transformation into the normal miniature pig and the normal guinea pigs cochlea via scala tympani.
    Shi X; Wu N; Zhang Y; Guo W; Lin C; Yang S
    Acta Otolaryngol; 2017 Sep; 137(9):910-916. PubMed ID: 28471702
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Identification of Adeno-Associated Viral Vectors That Target Neonatal and Adult Mammalian Inner Ear Cell Subtypes.
    Shu Y; Tao Y; Wang Z; Tang Y; Li H; Dai P; Gao G; Chen ZY
    Hum Gene Ther; 2016 Sep; 27(9):687-99. PubMed ID: 27342665
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Distributional comparison of different AAV vectors after unilateral cochlear administration.
    Han S; Xu Z; Wang S; Tang H; Hu S; Wang H; Guan G; Shu Y
    Gene Ther; 2024 Mar; 31(3-4):154-164. PubMed ID: 38097651
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Choice of vector and surgical approach enables efficient cochlear gene transfer in nonhuman primate.
    Andres-Mateos E; Landegger LD; Unzu C; Phillips J; Lin BM; Dewyer NA; Sanmiguel J; Nicolaou F; Valero MD; Bourdeu KI; Sewell WF; Beiler RJ; McKenna MJ; Stankovic KM; Vandenberghe LH
    Nat Commun; 2022 Mar; 13(1):1359. PubMed ID: 35292639
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Preclinical testing of AAV9-PHP.B for transgene expression in the non-human primate cochlea.
    Ivanchenko MV; Hanlon KS; Devine MK; Tenneson K; Emond F; Lafond JF; Kenna MA; Corey DP; Maguire CA
    Hear Res; 2020 Sep; 394():107930. PubMed ID: 32145977
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Engineering of the AAV-Compatible Hair Cell-Specific Small-Size Myo15 Promoter for Gene Therapy in the Inner Ear.
    Hu SW; Lv J; Wang Z; Tang H; Wang H; Wang F; Wang D; Zhang J; Zhang L; Cao Q; Chen Y; Gao Z; Han Y; Wang W; Li GL; Shu Y; Li H
    Research (Wash D C); 2024; 7():0341. PubMed ID: 38665848
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Cochlear Synaptopathy due to Mutations in OTOF Gene May Result in Stable Mild Hearing Loss and Severe Impairment of Speech Perception.
    Santarelli R; Scimemi P; Costantini M; Domínguez-Ruiz M; Rodríguez-Ballesteros M; Del Castillo I
    Ear Hear; 2021 Nov-Dec 01; 42(6):1627-1639. PubMed ID: 33908410
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Hearing of Otof-deficient mice restored by trans-splicing of N- and C-terminal otoferlin.
    Tang H; Wang H; Wang S; Hu SW; Lv J; Xun M; Gao K; Wang F; Chen Y; Wang D; Wang W; Li H; Shu Y
    Hum Genet; 2023 Feb; 142(2):289-304. PubMed ID: 36383253
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Efficient Delivery of Adeno-Associated Virus into Inner Ear
    Wang J; Zhao L; Gu X; Xue Y; Wang S; Xiao R; Vandenberghe LH; Peng KA; Shu Y; Li H
    Hum Gene Ther; 2022 Jul; 33(13-14):719-728. PubMed ID: 35156857
    [TBL] [Abstract][Full Text] [Related]  

  • 18. A dual-AAV approach restores fast exocytosis and partially rescues auditory function in deaf otoferlin knock-out mice.
    Al-Moyed H; Cepeda AP; Jung S; Moser T; Kügler S; Reisinger E
    EMBO Mol Med; 2019 Jan; 11(1):. PubMed ID: 30509897
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Hair Cell Transduction Efficiency of Single- and Dual-AAV Serotypes in Adult Murine Cochleae.
    Omichi R; Yoshimura H; Shibata SB; Vandenberghe LH; Smith RJH
    Mol Ther Methods Clin Dev; 2020 Jun; 17():1167-1177. PubMed ID: 32518805
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Dual AAV-mediated gene therapy restores hearing in a DFNB9 mouse model.
    Akil O; Dyka F; Calvet C; Emptoz A; Lahlou G; Nouaille S; Boutet de Monvel J; Hardelin JP; Hauswirth WW; Avan P; Petit C; Safieddine S; Lustig LR
    Proc Natl Acad Sci U S A; 2019 Mar; 116(10):4496-4501. PubMed ID: 30782832
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 11.