BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

110 related articles for article (PubMed ID: 38134938)

  • 1. Therapeutic Effects of Hematopoietic Stem Cell Derived From Gene-Edited Mice on β654-Thalassemia.
    Lu D; Gong X; Guo X; Chen Y; Zhu Y; Fang Y; Cai Q; Xu M; Yang H; Li D; Zeng Y; Zeng F
    Stem Cells; 2024 Mar; 42(3):278-289. PubMed ID: 38134938
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Correction of RNA splicing defect in β
    Lu D; Gong X; Fang Y; Guo X; Chen Y; Yang F; Zhao G; Ma Q; Zeng Y; Zeng F
    Haematologica; 2022 Jun; 107(6):1427-1437. PubMed ID: 34706494
    [TBL] [Abstract][Full Text] [Related]  

  • 3. CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells.
    Dever DP; Bak RO; Reinisch A; Camarena J; Washington G; Nicolas CE; Pavel-Dinu M; Saxena N; Wilkens AB; Mantri S; Uchida N; Hendel A; Narla A; Majeti R; Weinberg KI; Porteus MH
    Nature; 2016 Nov; 539(7629):384-389. PubMed ID: 27820943
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Non-viral DNA delivery and TALEN editing correct the sickle cell mutation in hematopoietic stem cells.
    Moiani A; Letort G; Lizot S; Chalumeau A; Foray C; Felix T; Le Clerre D; Temburni-Blake S; Hong P; Leduc S; Pinard N; Marechal A; Seclen E; Boyne A; Mayer L; Hong R; Pulicani S; Galetto R; Gouble A; Cavazzana M; Juillerat A; Miccio A; Duclert A; Duchateau P; Valton J
    Nat Commun; 2024 Jun; 15(1):4965. PubMed ID: 38862518
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Editing an α-globin enhancer in primary human hematopoietic stem cells as a treatment for β-thalassemia.
    Mettananda S; Fisher CA; Hay D; Badat M; Quek L; Clark K; Hublitz P; Downes D; Kerry J; Gosden M; Telenius J; Sloane-Stanley JA; Faustino P; Coelho A; Doondeea J; Usukhbayar B; Sopp P; Sharpe JA; Hughes JR; Vyas P; Gibbons RJ; Higgs DR
    Nat Commun; 2017 Sep; 8(1):424. PubMed ID: 28871148
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Restoring T and B cell generation in X-linked severe combined immunodeficiency mice through hematopoietic stem cells adenine base editing.
    Zhang L; Li K; Liu Z; An L; Wei H; Pang S; Cao Z; Huang X; Jin X; Ma X
    Mol Ther; 2024 Jun; 32(6):1658-1671. PubMed ID: 38532630
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Reversal of aberrant splicing of beta-thalassaemia allele (IVS-2-654 C-->T) by antisense RNA expression vector in cultured human erythroid cells.
    Gong L; Gu XF; Chen YD; Ren ZR; Huang SZ; Zeng YT
    Br J Haematol; 2000 Oct; 111(1):351-8. PubMed ID: 11091224
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Improved hematopoietic differentiation efficiency of gene-corrected beta-thalassemia induced pluripotent stem cells by CRISPR/Cas9 system.
    Song B; Fan Y; He W; Zhu D; Niu X; Wang D; Ou Z; Luo M; Sun X
    Stem Cells Dev; 2015 May; 24(9):1053-65. PubMed ID: 25517294
    [TBL] [Abstract][Full Text] [Related]  

  • 9. The Combination of CRISPR/Cas9 and iPSC Technologies in the Gene Therapy of Human β-thalassemia in Mice.
    Ou Z; Niu X; He W; Chen Y; Song B; Xian Y; Fan D; Tang D; Sun X
    Sci Rep; 2016 Sep; 6():32463. PubMed ID: 27581487
    [TBL] [Abstract][Full Text] [Related]  

  • 10. In vivo correction of anaemia in β-thalassemic mice by γPNA-mediated gene editing with nanoparticle delivery.
    Bahal R; Ali McNeer N; Quijano E; Liu Y; Sulkowski P; Turchick A; Lu YC; Bhunia DC; Manna A; Greiner DL; Brehm MA; Cheng CJ; López-Giráldez F; Ricciardi A; Beloor J; Krause DS; Kumar P; Gallagher PG; Braddock DT; Mark Saltzman W; Ly DH; Glazer PM
    Nat Commun; 2016 Oct; 7():13304. PubMed ID: 27782131
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Reactivation of γ-globin in adult β-YAC mice after ex vivo and in vivo hematopoietic stem cell genome editing.
    Li C; Psatha N; Sova P; Gil S; Wang H; Kim J; Kulkarni C; Valensisi C; Hawkins RD; Stamatoyannopoulos G; Lieber A
    Blood; 2018 Jun; 131(26):2915-2928. PubMed ID: 29789357
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Correction of Beta-Thalassemia IVS-II-654 Mutation in a Mouse Model Using Prime Editing.
    Zhang H; Sun R; Fei J; Chen H; Lu D
    Int J Mol Sci; 2022 May; 23(11):. PubMed ID: 35682629
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Hematopoietic Stem Cell Gene-Addition/Editing Therapy in Sickle Cell Disease.
    Germino-Watnick P; Hinds M; Le A; Chu R; Liu X; Uchida N
    Cells; 2022 Jun; 11(11):. PubMed ID: 35681538
    [TBL] [Abstract][Full Text] [Related]  

  • 14. CRISPR/Cas-based gene editing in therapeutic strategies for beta-thalassemia.
    Zeng S; Lei S; Qu C; Wang Y; Teng S; Huang P
    Hum Genet; 2023 Dec; 142(12):1677-1703. PubMed ID: 37878144
    [TBL] [Abstract][Full Text] [Related]  

  • 15.
    Yang Y; He L; Xie Y; Zhu L; Wu J; Fan Y; Yang Y; Sun X
    Front Cell Dev Biol; 2023; 11():1276890. PubMed ID: 38333188
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Gene correction of HBB mutations in CD34
    Antony JS; Latifi N; Haque AKMA; Lamsfus-Calle A; Daniel-Moreno A; Graeter S; Baskaran P; Weinmann P; Mezger M; Handgretinger R; Kormann MSD
    Mol Cell Pediatr; 2018 Nov; 5(1):9. PubMed ID: 30430274
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Functional requirements for phenotypic correction of murine beta-thalassemia: implications for human gene therapy.
    Persons DA; Allay ER; Sabatino DE; Kelly P; Bodine DM; Nienhuis AW
    Blood; 2001 May; 97(10):3275-82. PubMed ID: 11342459
    [TBL] [Abstract][Full Text] [Related]  

  • 18. HDAd5/35
    Li C; Psatha N; Gil S; Wang H; Papayannopoulou T; Lieber A
    Mol Ther Methods Clin Dev; 2018 Jun; 9():390-401. PubMed ID: 30038942
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Dual α-globin and truncated EPO receptor knockin restores hemoglobin production in α-thalassemia-derived red blood cells.
    Chu SN; Soupene E; Wienert B; Yin H; Sharma D; McCreary T; Jia K; Homma S; Hampton JP; Gardner JM; Conklin BR; MacKenzie TC; Porteus MH; Cromer MK
    bioRxiv; 2024 May; ():. PubMed ID: 38766216
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Amelioration of murine beta-thalassemia through drug selection of hematopoietic stem cells transduced with a lentiviral vector encoding both gamma-globin and the MGMT drug-resistance gene.
    Zhao H; Pestina TI; Nasimuzzaman M; Mehta P; Hargrove PW; Persons DA
    Blood; 2009 Jun; 113(23):5747-56. PubMed ID: 19365082
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 6.