These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

120 related articles for article (PubMed ID: 38218582)

  • 1. Self-complementary AAV vector therapy for treating corneal cloudiness of mucopolysaccharidosis type VII (MPS VII).
    Venkatakrishnan J; Yuan Y; Zhang J; Yu Y; Hu YC; Kao WW
    Ocul Surf; 2024 Apr; 32():39-47. PubMed ID: 38218582
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Corrective GUSB transfer to the canine mucopolysaccharidosis VII cornea using a helper-dependent canine adenovirus vector.
    Serratrice N; Cubizolle A; Ibanes S; Mestre-Francés N; Bayo-Puxan N; Creyssels S; Gennetier A; Bernex F; Verdier JM; Haskins ME; Couderc G; Malecaze F; Kalatzis V; Kremer EJ
    J Control Release; 2014 May; 181():22-31. PubMed ID: 24607662
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.
    Daly TM; Okuyama T; Vogler C; Haskins ME; Muzyczka N; Sands MS
    Hum Gene Ther; 1999 Jan; 10(1):85-94. PubMed ID: 10022533
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII.
    Gurda BL; De Guilhem De Lataillade A; Bell P; Zhu Y; Yu H; Wang P; Bagel J; Vite CH; Sikora T; Hinderer C; Calcedo R; Yox AD; Steet RA; Ruane T; O'Donnell P; Gao G; Wilson JM; Casal M; Ponder KP; Haskins ME
    Mol Ther; 2016 Feb; 24(2):206-216. PubMed ID: 26447927
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Significantly increased expression of beta-glucuronidase in the central nervous system of mucopolysaccharidosis type VII mice from the latency-associated transcript promoter in a nonpathogenic herpes simplex virus type 1 vector.
    Zhu J; Kang W; Wolfe JH; Fraser NW
    Mol Ther; 2000 Jul; 2(1):82-94. PubMed ID: 10899831
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.
    Frisella WA; O'Connor LH; Vogler CA; Roberts M; Walkley S; Levy B; Daly TM; Sands MS
    Mol Ther; 2001 Mar; 3(3):351-8. PubMed ID: 11273777
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Neonatal retroviral vector-mediated hepatic gene therapy reduces bone, joint, and cartilage disease in mucopolysaccharidosis VII mice and dogs.
    Mango RL; Xu L; Sands MS; Vogler C; Seiler G; Schwarz T; Haskins ME; Ponder KP
    Mol Genet Metab; 2004 May; 82(1):4-19. PubMed ID: 15110316
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Intrathecal AAVrh10 corrects biochemical and histological hallmarks of mucopolysaccharidosis VII mice and improves behavior and survival.
    Pagès G; Giménez-Llort L; García-Lareu B; Ariza L; Navarro M; Casas C; Chillón M; Bosch A
    Hum Mol Genet; 2019 Nov; 28(21):3610-3624. PubMed ID: 31511867
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Widespread correction of lysosomal storage in the mucopolysaccharidosis type VII mouse brain with a herpes simplex virus type 1 vector expressing beta-glucuronidase.
    Berges BK; Yellayi S; Karolewski BA; Miselis RR; Wolfe JH; Fraser NW
    Mol Ther; 2006 May; 13(5):859-69. PubMed ID: 16515890
    [TBL] [Abstract][Full Text] [Related]  

  • 10. AAV-mediated intravitreal gene therapy reduces lysosomal storage in the retinal pigmented epithelium and improves retinal function in adult MPS VII mice.
    Hennig AK; Ogilvie JM; Ohlemiller KK; Timmers AM; Hauswirth WW; Sands MS
    Mol Ther; 2004 Jul; 10(1):106-16. PubMed ID: 15233947
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Murine mucopolysaccharidosis type VII: the impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease.
    Vogler C; Sands MS; Galvin N; Levy B; Thorpe C; Barker J; Sly WS
    J Inherit Metab Dis; 1998 Aug; 21(5):575-86. PubMed ID: 9728337
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.
    Xu L; Mango RL; Sands MS; Haskins ME; Ellinwood NM; Ponder KP
    Mol Ther; 2002 Dec; 6(6):745-58. PubMed ID: 12498771
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Cross-correction of beta-glucuronidase deficiency by retroviral vector-mediated gene transfer.
    Taylor RM; Wolfe JH
    Exp Cell Res; 1994 Oct; 214(2):606-13. PubMed ID: 7925654
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs.
    Ponder KP; Melniczek JR; Xu L; Weil MA; O'Malley TM; O'Donnell PA; Knox VW; Aguirre GD; Mazrier H; Ellinwood NM; Sleeper M; Maguire AM; Volk SW; Mango RL; Zweigle J; Wolfe JH; Haskins ME
    Proc Natl Acad Sci U S A; 2002 Oct; 99(20):13102-7. PubMed ID: 12232044
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Lentiviral-mediated gene therapy results in sustained expression of β-glucuronidase for up to 12 months in the gus(mps/mps) and up to 18 months in the gus(tm(L175F)Sly) mouse models of mucopolysaccharidosis type VII.
    Derrick-Roberts AL; Pyragius CE; Kaidonis XM; Jackson MR; Anson DS; Byers S
    Hum Gene Ther; 2014 Sep; 25(9):798-810. PubMed ID: 25003807
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Clinical response to persistent, low-level beta-glucuronidase expression in the murine model of mucopolysaccharidosis type VII.
    Donsante A; Levy B; Vogler C; Sands MS
    J Inherit Metab Dis; 2007 Apr; 30(2):227-38. PubMed ID: 17308887
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Corrective GUSB transfer to the canine mucopolysaccharidosis VII brain.
    Cubizolle A; Serratrice N; Skander N; Colle MA; Ibanes S; Gennetier A; Bayo-Puxan N; Mazouni K; Mennechet F; Joussemet B; Cherel Y; Lajat Y; Vite C; Bernex F; Kalatzis V; Haskins ME; Kremer EJ
    Mol Ther; 2014 Apr; 22(4):762-73. PubMed ID: 24343103
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Transgene produces massive overexpression of human beta -glucuronidase in mice, lysosomal storage of enzyme, and strain-dependent tumors.
    Vogler C; Galvin N; Levy B; Grubb J; Jiang J; Zhou XY; Sly WS
    Proc Natl Acad Sci U S A; 2003 Mar; 100(5):2669-73. PubMed ID: 12591953
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Transplantation of human umbilical mesenchymal stem cells cures the corneal defects of mucopolysaccharidosis VII mice.
    Coulson-Thomas VJ; Caterson B; Kao WW
    Stem Cells; 2013 Oct; 31(10):2116-26. PubMed ID: 23897660
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase.
    Taylor RM; Wolfe JH
    Nat Med; 1997 Jul; 3(7):771-4. PubMed ID: 9212105
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 6.