128 related articles for article (PubMed ID: 38341614)
1. Ultrasound-mediated gene delivery specifically targets liver sinusoidal endothelial cells for sustained FVIII expression in hemophilia A mice.
Lawton SM; Manson MA; Fan MN; Chao TY; Chen CY; Kim P; Campbell C; Cai X; Vander Kooi A; Miao CH
Mol Ther; 2024 Apr; 32(4):969-981. PubMed ID: 38341614
[TBL] [Abstract][Full Text] [Related]
2. Ultrasound-mediated gene delivery of factor VIII plasmids for hemophilia A gene therapy in mice.
Song S; Lyle MJ; Noble-Vranish ML; Min-Tran DM; Harrang J; Xiao W; Unger EC; Miao CH
Mol Ther Nucleic Acids; 2022 Mar; 27():916-926. PubMed ID: 35141050
[TBL] [Abstract][Full Text] [Related]
3. Factor VIII can be synthesized in hemophilia A mice liver by bone marrow progenitor cell-derived hepatocytes and sinusoidal endothelial cells.
Yadav N; Kanjirakkuzhiyil S; Ramakrishnan M; Das TK; Mukhopadhyay A
Stem Cells Dev; 2012 Jan; 21(1):110-20. PubMed ID: 21480781
[TBL] [Abstract][Full Text] [Related]
4. Production of factor VIII by human liver sinusoidal endothelial cells transplanted in immunodeficient uPA mice.
Fomin ME; Zhou Y; Beyer AI; Publicover J; Baron JL; Muench MO
PLoS One; 2013; 8(10):e77255. PubMed ID: 24167566
[TBL] [Abstract][Full Text] [Related]
5. Nanocapsule-delivered Sleeping Beauty mediates therapeutic Factor VIII expression in liver sinusoidal endothelial cells of hemophilia A mice.
Kren BT; Unger GM; Sjeklocha L; Trossen AA; Korman V; Diethelm-Okita BM; Reding MT; Steer CJ
J Clin Invest; 2009 Jul; 119(7):2086-99. PubMed ID: 19509468
[TBL] [Abstract][Full Text] [Related]
6. Human liver sinusoidal endothelial cells but not hepatocytes contain factor VIII.
Shahani T; Covens K; Lavend'homme R; Jazouli N; Sokal E; Peerlinck K; Jacquemin M
J Thromb Haemost; 2014 Jan; 12(1):36-42. PubMed ID: 24118899
[TBL] [Abstract][Full Text] [Related]
7. Transplantation of endothelial cells corrects the phenotype in hemophilia A mice.
Kumaran V; Benten D; Follenzi A; Joseph B; Sarkar R; Gupta S
J Thromb Haemost; 2005 Sep; 3(9):2022-31. PubMed ID: 16102109
[TBL] [Abstract][Full Text] [Related]
8. Transcutaneous ultrasound-mediated gene delivery into canine livers achieves therapeutic levels of factor VIII expression.
Manson MA; Zhang F; Novokhodko A; Chen CY; Parker M; Loeb KR; Kajimoto M; Campbell C; Storb RF; Miao CH
Blood Adv; 2022 Jun; 6(12):3557-3568. PubMed ID: 35427415
[TBL] [Abstract][Full Text] [Related]
9. GP64-pseudotyped lentiviral vectors target liver endothelial cells and correct hemophilia A mice.
Milani M; Canepari C; Assanelli S; Merlin S; Borroni E; Starinieri F; Biffi M; Russo F; Fabiano A; Zambroni D; Annoni A; Naldini L; Follenzi A; Cantore A
EMBO Mol Med; 2024 Jun; 16(6):1427-1450. PubMed ID: 38684862
[TBL] [Abstract][Full Text] [Related]
10. A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice.
Merlin S; Cannizzo ES; Borroni E; Bruscaggin V; Schinco P; Tulalamba W; Chuah MK; Arruda VR; VandenDriessche T; Prat M; Valente G; Follenzi A
Mol Ther; 2017 Aug; 25(8):1815-1830. PubMed ID: 28552407
[TBL] [Abstract][Full Text] [Related]
11. High-affinity von Willebrand factor binding does not affect the anatomical or hepatocellular distribution of factor VIII in rats.
Øie CI; Roepstorff K; Behrens C; Bøggild Kristensen J; Karpf DM; Bolt G; Gudme CN; Kjalke M; Smedsrød B; Appa RS
J Thromb Haemost; 2016 Sep; 14(9):1803-13. PubMed ID: 27378673
[TBL] [Abstract][Full Text] [Related]
12. Expression of factor VIII by murine liver sinusoidal endothelial cells.
Do H; Healey JF; Waller EK; Lollar P
J Biol Chem; 1999 Jul; 274(28):19587-92. PubMed ID: 10391893
[TBL] [Abstract][Full Text] [Related]
13. Molecular Profiling of Liver Sinusoidal Endothelial Cells in Comparison to Hepatocytes: Reflection on Which Cell Type Should Be the Target for Gene Therapy.
El-Maarri O; Jamil MA; Oldenburg J
Hamostaseologie; 2020 Nov; 40(S 01):S26-S31. PubMed ID: 33187005
[TBL] [Abstract][Full Text] [Related]
14. FVIII expression by its native promoter sustains long-term correction avoiding immune response in hemophilic mice.
Merlin S; Famà R; Borroni E; Zanolini D; Bruscaggin V; Zucchelli S; Follenzi A
Blood Adv; 2019 Mar; 3(5):825-838. PubMed ID: 30862611
[TBL] [Abstract][Full Text] [Related]
15. Ex vivo gene therapy for hemophilia A that enhances safe delivery and sustained in vivo factor VIII expression from lentivirally engineered endothelial progenitors.
Matsui H; Shibata M; Brown B; Labelle A; Hegadorn C; Andrews C; Hebbel RP; Galipeau J; Hough C; Lillicrap D
Stem Cells; 2007 Oct; 25(10):2660-9. PubMed ID: 17615271
[TBL] [Abstract][Full Text] [Related]
16. Extrahepatic sources of factor VIII potentially contribute to the coagulation cascade correcting the bleeding phenotype of mice with hemophilia A.
Zanolini D; Merlin S; Feola M; Ranaldo G; Amoruso A; Gaidano G; Zaffaroni M; Ferrero A; Brunelleschi S; Valente G; Gupta S; Prat M; Follenzi A
Haematologica; 2015 Jul; 100(7):881-92. PubMed ID: 25911555
[TBL] [Abstract][Full Text] [Related]
17. A novel cell-sheet technology that achieves durable factor VIII delivery in a mouse model of hemophilia A.
Tatsumi K; Sugimoto M; Lillicrap D; Shima M; Ohashi K; Okano T; Matsui H
PLoS One; 2013; 8(12):e83280. PubMed ID: 24358271
[TBL] [Abstract][Full Text] [Related]
18. Adenovirus-mediated factor VIII gene expression results in attenuated anti-factor VIII-specific immunity in hemophilia A mice compared with factor VIII protein infusion.
Bristol JA; Gallo-Penn A; Andrews J; Idamakanti N; Kaleko M; Connelly S
Hum Gene Ther; 2001 Sep; 12(13):1651-61. PubMed ID: 11535168
[TBL] [Abstract][Full Text] [Related]
19. Sustained FVIII expression and phenotypic correction of hemophilia A in neonatal mice using an endothelial-targeted sleeping beauty transposon.
Liu L; Mah C; Fletcher BS
Mol Ther; 2006 May; 13(5):1006-15. PubMed ID: 16464640
[TBL] [Abstract][Full Text] [Related]
20. Comparison of different gene addition strategies to modify placental derived-mesenchymal stromal cells to produce FVIII.
Ramamurthy RM; Rodriguez M; Ainsworth HC; Shields J; Meares D; Bishop C; Farland A; Langefeld CD; Atala A; Doering CB; Spencer HT; Porada CD; Almeida-Porada G
Front Immunol; 2022; 13():954984. PubMed ID: 36591257
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
