These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

165 related articles for article (PubMed ID: 38404504)

  • 1. Hair cell-specific Myo15 promoter-mediated gene therapy rescues hearing in DFNB9 mouse model.
    Wang H; Xun M; Tang H; Zhao J; Hu S; Zhang L; Lv J; Wang D; Chen Y; Liu J; Li GL; Wang W; Shu Y; Li H
    Mol Ther Nucleic Acids; 2024 Mar; 35(1):102135. PubMed ID: 38404504
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Engineering of the AAV-Compatible Hair Cell-Specific Small-Size Myo15 Promoter for Gene Therapy in the Inner Ear.
    Hu SW; Lv J; Wang Z; Tang H; Wang H; Wang F; Wang D; Zhang J; Zhang L; Cao Q; Chen Y; Gao Z; Han Y; Wang W; Li GL; Shu Y; Li H
    Research (Wash D C); 2024; 7():0341. PubMed ID: 38665848
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Preclinical evaluation of the efficacy and safety of AAV1-hOTOF in mice and nonhuman primates.
    Zhang L; Wang H; Xun M; Tang H; Wang J; Lv J; Zhu B; Chen Y; Wang D; Hu S; Gao Z; Liu J; Chen ZY; Chen B; Li H; Shu Y
    Mol Ther Methods Clin Dev; 2023 Dec; 31():101154. PubMed ID: 38027066
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Recovery kinetics of dual AAV-mediated human otoferlin expression.
    Sellon JB; So KS; D'Arcangelo A; Cancelarich S; Drummond MC; Slade PG; Pan N; Gibson TM; Yang T; Burns JC; Palermo AT; Becker L
    Front Mol Neurosci; 2024; 17():1376128. PubMed ID: 38952419
    [TBL] [Abstract][Full Text] [Related]  

  • 5. A dual-AAV approach restores fast exocytosis and partially rescues auditory function in deaf otoferlin knock-out mice.
    Al-Moyed H; Cepeda AP; Jung S; Moser T; Kügler S; Reisinger E
    EMBO Mol Med; 2019 Jan; 11(1):. PubMed ID: 30509897
    [TBL] [Abstract][Full Text] [Related]  

  • 6. AAV-Mediated Gene Therapy Restores Hearing in Patients with DFNB9 Deafness.
    Qi J; Tan F; Zhang L; Lu L; Zhang S; Zhai Y; Lu Y; Qian X; Dong W; Zhou Y; Zhang Z; Yang X; Jiang L; Yu C; Liu J; Chen T; Wu L; Tan C; Sun S; Song H; Shu Y; Xu L; Gao X; Li H; Chai R
    Adv Sci (Weinh); 2024 Mar; 11(11):e2306788. PubMed ID: 38189623
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Preclinical Efficacy And Safety Evaluation of AAV-OTOF in DFNB9 Mouse Model And Nonhuman Primate.
    Qi J; Zhang L; Tan F; Zhang Y; Zhou Y; Zhang Z; Wang H; Yu C; Jiang L; Liu J; Chen T; Wu L; Zhang S; Sun S; Sun S; Lu L; Wang Q; Chai R
    Adv Sci (Weinh); 2024 Jan; 11(3):e2306201. PubMed ID: 38014592
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate.
    György B; Meijer EJ; Ivanchenko MV; Tenneson K; Emond F; Hanlon KS; Indzhykulian AA; Volak A; Karavitaki KD; Tamvakologos PI; Vezina M; Berezovskii VK; Born RT; O'Brien M; Lafond JF; Arsenijevic Y; Kenna MA; Maguire CA; Corey DP
    Mol Ther Methods Clin Dev; 2019 Jun; 13():1-13. PubMed ID: 30581889
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Single and Dual Vector Gene Therapy with AAV9-PHP.B Rescues Hearing in Tmc1 Mutant Mice.
    Wu J; Solanes P; Nist-Lund C; Spataro S; Shubina-Oleinik O; Marcovich I; Goldberg H; Schneider BL; Holt JR
    Mol Ther; 2021 Mar; 29(3):973-988. PubMed ID: 33212302
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Rescue of Hearing by Gene Delivery to Inner-Ear Hair Cells Using Exosome-Associated AAV.
    György B; Sage C; Indzhykulian AA; Scheffer DI; Brisson AR; Tan S; Wu X; Volak A; Mu D; Tamvakologos PI; Li Y; Fitzpatrick Z; Ericsson M; Breakefield XO; Corey DP; Maguire CA
    Mol Ther; 2017 Feb; 25(2):379-391. PubMed ID: 28082074
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Identification of Adeno-Associated Viral Vectors That Target Neonatal and Adult Mammalian Inner Ear Cell Subtypes.
    Shu Y; Tao Y; Wang Z; Tang Y; Li H; Dai P; Gao G; Chen ZY
    Hum Gene Ther; 2016 Sep; 27(9):687-99. PubMed ID: 27342665
    [TBL] [Abstract][Full Text] [Related]  

  • 12. AAV-S: A versatile capsid variant for transduction of mouse and primate inner ear.
    Ivanchenko MV; Hanlon KS; Hathaway DM; Klein AJ; Peters CW; Li Y; Tamvakologos PI; Nammour J; Maguire CA; Corey DP
    Mol Ther Methods Clin Dev; 2021 Jun; 21():382-398. PubMed ID: 33869656
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Dual AAV-mediated gene therapy restores hearing in a DFNB9 mouse model.
    Akil O; Dyka F; Calvet C; Emptoz A; Lahlou G; Nouaille S; Boutet de Monvel J; Hardelin JP; Hauswirth WW; Avan P; Petit C; Safieddine S; Lustig LR
    Proc Natl Acad Sci U S A; 2019 Mar; 116(10):4496-4501. PubMed ID: 30782832
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Efficient Viral Transduction in Fetal and Adult Human Inner Ear Explants with AAV9-PHP.B Vectors.
    van Beelen ESA; van der Valk WH; Verhagen TO; de Groot JCMJ; Madison MA; Shadmanfar W; Hensen EF; Jansen JC; van Benthem PPG; Holt JR; Locher H
    Biomolecules; 2022 Jun; 12(6):. PubMed ID: 35740941
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Efficient viral transduction in mouse inner ear hair cells with utricle injection and AAV9-PHP.B.
    Lee J; Nist-Lund C; Solanes P; Goldberg H; Wu J; Pan B; Schneider BL; Holt JR
    Hear Res; 2020 Sep; 394():107882. PubMed ID: 31980281
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Targeted Gene Delivery into the Mammalian Inner Ear Using Synthetic Serotypes of Adeno-Associated Virus Vectors.
    Kim MA; Ryu N; Kim HM; Kim YR; Lee B; Kwon TJ; Bok J; Kim UK
    Mol Ther Methods Clin Dev; 2019 Jun; 13():197-204. PubMed ID: 30805407
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Characterization of promoters for adeno-associated virus mediated efficient Cas9 activation in adult Cas9 knock-in murine cochleae.
    Zhao X; Jin C; Dong T; Sun Z; Zheng X; Feng B; Cheng Z; Li X; Tao Y; Wu H
    Hear Res; 2020 Sep; 394():107999. PubMed ID: 32611519
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Overloaded Adeno-Associated Virus as a Novel Gene Therapeutic Tool for Otoferlin-Related Deafness.
    Rankovic V; Vogl C; Dörje NM; Bahader I; Duque-Afonso CJ; Thirumalai A; Weber T; Kusch K; Strenzke N; Moser T
    Front Mol Neurosci; 2020; 13():600051. PubMed ID: 33488357
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Hearing of Otof-deficient mice restored by trans-splicing of N- and C-terminal otoferlin.
    Tang H; Wang H; Wang S; Hu SW; Lv J; Xun M; Gao K; Wang F; Chen Y; Wang D; Wang W; Li H; Shu Y
    Hum Genet; 2023 Feb; 142(2):289-304. PubMed ID: 36383253
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Approaches and Vectors for Efficient Cochlear Gene Transfer in Adult Mouse Models.
    Zhao Y; Zhang L; Wang D; Chen B; Shu Y
    Biomolecules; 2022 Dec; 13(1):. PubMed ID: 36671423
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 9.