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2. Therapeutic base editing and prime editing of COL7A1 mutations in recessive dystrophic epidermolysis bullosa. Hong SA; Kim SE; Lee AY; Hwang GH; Kim JH; Iwata H; Kim SC; Bae S; Lee SE Mol Ther; 2022 Aug; 30(8):2664-2679. PubMed ID: 35690907 [TBL] [Abstract][Full Text] [Related]
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