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5. Therapeutic exon skipping for dysferlinopathies? Aartsma-Rus A; Singh KH; Fokkema IF; Ginjaar IB; van Ommen GJ; den Dunnen JT; van der Maarel SM Eur J Hum Genet; 2010 Aug; 18(8):889-94. PubMed ID: 20145676 [TBL] [Abstract][Full Text] [Related]
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