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3. Outcomes of early-treated infants with spinal muscular atrophy: A multicenter, retrospective cohort study. Goedeker NL; Rogers A; Fisher M; Arya K; Brandsema JF; Farah H; Farrar MA; Felker MV; Gibbons M; Hamid OA; Harmelink M; Herbert K; Kichula E; King K; Lakhotia A; Lee BH; Kuntz NL; Parsons J; Rehborg R; Veerapaniyan A; Zaidman CM Muscle Nerve; 2024 Dec; 70(6):1247-1256. PubMed ID: 39370660 [TBL] [Abstract][Full Text] [Related]
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